Selection-free genome editing of the sickle mutation in human adult hematopoietic stem/progenitor cells
DeWitt, Mark A, Magis, Wendy, Bray, Nicolas L, Wang, Tianjiao, Berman, Jennifer R, Urbinati, Fabrizia, Heo, Seok-Jin, Mitros, Therese, Muñoz, Denise P, Boffelli, Dario, Kohn, Donald B, Walters, Mark C, Carroll, Dana, Martin, David I K, Corn, Jacob E
Published in Science translational medicine (12.10.2016)
Published in Science translational medicine (12.10.2016)
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Synthetically modified guide RNA and donor DNA are a versatile platform for CRISPR-Cas9 engineering
Lee, Kunwoo, Mackley, Vanessa A, Rao, Anirudh, Chong, Anthony T, Dewitt, Mark A, Corn, Jacob E, Murthy, Niren
Published in eLife (02.05.2017)
Published in eLife (02.05.2017)
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Improving Gene Editing Outcomes in Human Hematopoietic Stem and Progenitor Cells by Temporal Control of DNA Repair
Lomova, Anastasia, Clark, Danielle N., Campo‐Fernandez, Beatriz, Flores‐Bjurström, Carmen, Kaufman, Michael L., Fitz‐Gibbon, Sorel, Wang, Xiaoyan, Miyahira, Eric Y., Brown, Devin, DeWitt, Mark A., Corn, Jacob E., Hollis, Roger P., Romero, Zulema, Kohn, Donald B.
Published in Stem cells (Dayton, Ohio) (01.02.2019)
Published in Stem cells (Dayton, Ohio) (01.02.2019)
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Nanoparticle delivery of Cas9 ribonucleoprotein and donor DNA in vivo induces homology-directed DNA repair
Lee, Kunwoo, Conboy, Michael, Park, Hyo Min, Jiang, Fuguo, Kim, Hyun Jin, Dewitt, Mark A., Mackley, Vanessa A., Chang, Kevin, Rao, Anirudh, Skinner, Colin, Shobha, Tamanna, Mehdipour, Melod, Liu, Hui, Huang, Wen-chin, Lan, Freeman, Bray, Nicolas L., Li, Song, Corn, Jacob E., Kataoka, Kazunori, Doudna, Jennifer A., Conboy, Irina, Murthy, Niren
Published in Nature biomedical engineering (2017)
Published in Nature biomedical engineering (2017)
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Tension on the linker gates the ATP-dependent release of dynein from microtubules
Cleary, Frank B., Dewitt, Mark A., Bilyard, Thomas, Htet, Zaw Min, Belyy, Vladislav, Chan, Danna D., Chang, Amy Y., Yildiz, Ahmet
Published in Nature communications (11.08.2014)
Published in Nature communications (11.08.2014)
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Controlled Cycling and Quiescence Enables Efficient HDR in Engraftment-Enriched Adult Hematopoietic Stem and Progenitor Cells
Shin, Jiyung J., Schröder, Markus S., Caiado, Francisco, Wyman, Stacia K., Bray, Nicolas L., Bordi, Matteo, Dewitt, Mark A., Vu, Jonathan T., Kim, Won-Tae, Hockemeyer, Dirk, Manz, Markus G., Corn, Jacob E.
Published in Cell reports (Cambridge) (01.09.2020)
Published in Cell reports (Cambridge) (01.09.2020)
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Journal Article
Genome editing via delivery of Cas9 ribonucleoprotein
DeWitt, Mark A., Corn, Jacob E., Carroll, Dana
Published in Methods (San Diego, Calif.) (15.05.2017)
Published in Methods (San Diego, Calif.) (15.05.2017)
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Identification of novel HPFH-like mutations by CRISPR base editing that elevate the expression of fetal hemoglobin
Ravi, Nithin Sam, Wienert, Beeke, Wyman, Stacia K, Bell, Henry William, George, Anila, Mahalingam, Gokulnath, Vu, Jonathan T, Prasad, Kirti, Bandlamudi, Bhanu Prasad, Devaraju, Nivedhitha, Rajendiran, Vignesh, Syedbasha, Nazar, Pai, Aswin Anand, Nakamura, Yukio, Kurita, Ryo, Narayanasamy, Muthuraman, Balasubramanian, Poonkuzhali, Thangavel, Saravanabhavan, Marepally, Srujan, Velayudhan, Shaji R, Srivastava, Alok, DeWitt, Mark A, Crossley, Merlin, Corn, Jacob E, Mohankumar, Kumarasamypet M
Published in eLife (11.02.2022)
Published in eLife (11.02.2022)
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Covalent Protein Labeling and Improved Single-Molecule Optical Properties of Aqueous CdSe/CdS Quantum Dots
Wichner, Sara M, Mann, Victor R, Powers, Alexander S, Segal, Maya A, Mir, Mustafa, Bandaria, Jigar N, DeWitt, Mark A, Darzacq, Xavier, Yildiz, Ahmet, Cohen, Bruce E
Published in ACS nano (25.07.2017)
Published in ACS nano (25.07.2017)
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Journal Article
CRISPR-Cas9 interrogation of a putative fetal globin repressor in human erythroid cells
Chung, Jennifer E, Magis, Wendy, Vu, Jonathan, Heo, Seok-Jin, Wartiovaara, Kirmo, Walters, Mark C, Kurita, Ryo, Nakamura, Yukio, Boffelli, Dario, Martin, David I K, Corn, Jacob E, DeWitt, Mark A
Published in PloS one (15.01.2019)
Published in PloS one (15.01.2019)
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ATF4 Regulates MYB to Increase γ-Globin in Response to Loss of β-Globin
Boontanrart, Mandy Y., Schröder, Markus S., Stehli, Gautier M., Banović, Marija, Wyman, Stacia K., Lew, Rachel J., Bordi, Matteo, Gowen, Benjamin G., DeWitt, Mark A., Corn, Jacob E.
Published in Cell reports (Cambridge) (04.08.2020)
Published in Cell reports (Cambridge) (04.08.2020)
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Journal Article
Monomeric Rhodopsin Is the Minimal Functional Unit Required for Arrestin Binding
Tsukamoto, Hisao, Sinha, Abhinav, DeWitt, Mark, Farrens, David L.
Published in Journal of molecular biology (11.06.2010)
Published in Journal of molecular biology (11.06.2010)
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Journal Article
High-level correction of the sickle mutation is amplified in vivo during erythroid differentiation
Magis, Wendy, DeWitt, Mark A., Wyman, Stacia K., Vu, Jonathan T., Heo, Seok-Jin, Shao, Shirley J., Hennig, Finn, Romero, Zulema G., Campo-Fernandez, Beatriz, Said, Suzanne, McNeill, Matthew S., Rettig, Garrett R., Sun, Yongming, Wang, Yu, Behlke, Mark A., Kohn, Donald B., Boffelli, Dario, Walters, Mark C., Corn, Jacob E., Martin, David I.K.
Published in iScience (17.06.2022)
Published in iScience (17.06.2022)
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