Rationale, design, and methods of a randomized, controlled, open-label clinical trial with open-label extension to investigate the safety of vosoritide in infants, and young children with achondroplasia at risk of requiring cervicomedullary decompression surgery
Savarirayan, Ravi, Irving, Melita, Maixner, Wirginia, Thompson, Dominic, Offiah, Amaka C, Connolly, Daniel JA, Raghavan, Ashok, Powell, James, Kronhardt, Marcin, Jeha, George, Ghani, Sajda, Fisheleva, Elena, Day, Jonathan RS
Published in Science progress (1916) (01.01.2021)
Published in Science progress (1916) (01.01.2021)
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