Gene correction for SCID-X1 in long-term hematopoietic stem cells
Pavel-Dinu, Mara, Wiebking, Volker, Dejene, Beruh T, Srifa, Waracharee, Mantri, Sruthi, Nicolas, Carmencita E, Lee, Ciaran, Bao, Gang, Kildebeck, Eric J, Punjya, Niraj, Sindhu, Camille, Inlay, Matthew A, Saxena, Nivedita, DeRavin, Suk See, Malech, Harry, Roncarolo, Maria Grazia, Weinberg, Kenneth I, Porteus, Matthew H
Published in Nature communications (09.04.2019)
Published in Nature communications (09.04.2019)
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Author Correction: Gene correction for SCID-X1 in long-term hematopoietic stem cells
Pavel-Dinu, Mara, Wiebking, Volker, Dejene, Beruh T, Srifa, Waracharee, Mantri, Sruthi, Nicolas, Carmencita E, Lee, Ciaran, Bao, Gang, Kildebeck, Eric J, Punjya, Niraj, Sindhu, Camille, Inlay, Matthew A, Saxena, Nivedita, DeRavin, Suk See, Malech, Harry, Roncarolo, Maria Grazia, Weinberg, Kenneth I, Porteus, Matthew H
Published in Nature communications (26.04.2019)
Published in Nature communications (26.04.2019)
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Common Severe Infections in Chronic Granulomatous Disease
Marciano, Beatriz E., Spalding, Christine, Fitzgerald, Alan, Mann, Daphne, Brown, Thomas, Osgood, Sharon, Yockey, Lynne, Darnell, Dirk N., Barnhart, Lisa, Daub, Janine, Boris, Lisa, Rump, Amy P., Anderson, Victoria L., Haney, Carissa, Kuhns, Douglas B., Rosenzweig, Sergio D., Kelly, Corin, Zelazny, Adrian, Mason, Tamika, See DeRavin, Suk, Kang, Elizabeth, Gallin, John I., Malech, Harry L., Olivier, Kenneth N., Uzel, Gulbu, Freeman, Alexandra F., Heller, Theo, Zerbe, Christa S., Holland, Steven M.
Published in Clinical infectious diseases (15.04.2015)
Published in Clinical infectious diseases (15.04.2015)
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Gene Editing Rescues In vitro T Cell Development of RAG2-Deficient Induced Pluripotent Stem Cells in an Artificial Thymic Organoid System
Gardner, Cameron L., Pavel-Dinu, Mara, Dobbs, Kerry, Bosticardo, Marita, Reardon, Paul K., Lack, Justin, DeRavin, Suk See, Le, Kent, Bello, Ezekiel, Pala, Francesca, Delmonte, Ottavia M., Malech, Harry, Montel-Hagan, Amelie, Crooks, Gay, Acuto, Oreste, Porteus, Matthew H., Notarangelo, Luigi D.
Published in Journal of clinical immunology (01.07.2021)
Published in Journal of clinical immunology (01.07.2021)
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Aberrant Clonal Hematopoiesis following Lentiviral Vector Transduction of HSPCs in a Rhesus Macaque
Espinoza, Diego A., Fan, Xing, Yang, Di, Cordes, Stefan F., Truitt, Lauren L., Calvo, Katherine R., Yabe, Idalia M., Demirci, Selami, Hope, Kristin J., Hong, So Gun, Krouse, Allen, Metzger, Mark, Bonifacino, Aylin, Lu, Rong, Uchida, Naoya, Tisdale, John F., Wu, Xiaolin, DeRavin, Suk See, Malech, Harry L., Donahue, Robert E., Wu, Chuanfeng, Dunbar, Cynthia E.
Published in Molecular therapy (05.06.2019)
Published in Molecular therapy (05.06.2019)
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Human syndromes of immunodeficiency and dysregulation are characterized by distinct defects in T-cell receptor repertoire development
Yu, Xiaomin, PhD, Almeida, Jorge R., PhD, Darko, Sam, PhD, van der Burg, Mirjam, PhD, DeRavin, Suk See, MD, PhD, Malech, Harry, MD, Gennery, Andrew, MD, Chinn, Ivan, MD, Markert, Mary Louise, MD, PhD, Douek, Daniel C., MD, PhD, Milner, Joshua D., MD
Published in Journal of allergy and clinical immunology (01.04.2014)
Published in Journal of allergy and clinical immunology (01.04.2014)
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The Changing Paradigm of Management of Liver Abscesses in Chronic Granulomatous Disease
Straughan, David M, McLoughlin, Kaitlin C, Mullinax, John E, Marciano, Beatriz E, Freeman, Alexandra F, Anderson, Victoria L, Uzel, Gulbu, Azoury, Said C, Sorber, Rebecca, Quadri, Humair S, Malech, Harry L, DeRavin, Suk See, Kamal, Natasha, Koh, Christopher, Zerbe, Christa S, Kuhns, Douglas B, Gallin, John I, Heller, Theo, Holland, Steven M, Rudloff, Udo
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Published in Clinical infectious diseases (17.04.2018)
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Bonner, Kimberly E, Sukerman, Ellie, Liko, Juventila, Lanzieri, Tatiana M, Sutton, Melissa, DeBess, Emilio, Leesman, Christopher, Icenogle, Joseph, Hao, LiJuan, Chen, Min-Hsin, Faisthalab, Raeesa, Leman, Richard F, Cieslak, Paul R, DeRavin, Suk See, Perelygina, Ludmila
Published in Frontiers in immunology (08.12.2022)
Published in Frontiers in immunology (08.12.2022)
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Correction to: Gene Editing Rescues in Vitro T Cell Development of RAG2-Deficient Induced Pluripotent Stem Cells in an Artificial Thymic Organoid System
Gardner, Cameron L., Pavel-Dinu, Mara, Dobbs, Kerry, Bosticardo, Marita, Reardon, Paul K., Lack, Justin, DeRavin, Suk See, Le, Kent, Bello, Ezekiel, Pala, Francesca, Delmonte, Ottavia M., Malech, Harry, Montel-Hagen, Amelie, Crooks, Gay, Acuto, Oreste, Porteus, Matthew H., Notarangelo, Luigi D.
Published in Journal of clinical immunology (01.07.2021)
Published in Journal of clinical immunology (01.07.2021)
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Author Correction: Gene correction for SCID-X1 in long-term hematopoietic stem cells
Pavel-Dinu, Mara, Wiebking, Volker, Dejene, Beruh T, Srifa, Waracharee, Mantri, Sruthi, Nicolas, Carmencita E, Lee, Ciaran, Bao, Gang, Kildebeck, Eric J, Punjya, Niraj, Sindhu, Camille, Inlay, Matthew A, Saxena, Nivedita, DeRavin, Suk See, Malech, Harry, Roncarolo, Maria Grazia, Weinberg, Kenneth I, Porteus, Matthew H
Published in Nature communications (04.12.2019)
Published in Nature communications (04.12.2019)
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Interleukin-27 Enhances the Potential of Reactive Oxygen Species Generation from Monocyte-derived Macrophages and Dendritic cells by Induction of p47phox
Sowrirajan, Bharatwaj, Saito, Yoshiro, Poudyal, Deepak, Chen, Qian, Sui, Hongyan, DeRavin, Suk See, Imamichi, Hiromi, Sato, Toyotaka, Kuhns, Douglas B., Noguchi, Noriko, Malech, Harry L., Lane, H. Clifford, Imamichi, Tomozumi
Published in Scientific reports (27.02.2017)
Published in Scientific reports (27.02.2017)
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Disseminated and Congenital Toxoplasmosis in a Mother and Child With Activated PI3-Kinase δ Syndrome Type 2 (APDS2): Case Report and a Literature Review of Toxoplasma Infections in Primary Immunodeficiencies
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Published in Frontiers in immunology (14.02.2019)
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Lawrence, Monica G., MD, Siegel, Andrea, PhD, DeRavin, Suk See, MD, Hanson, Eric Paul, MD, Moir, Susan, PhD, Klein, Christoph, MD, Holland, Steven M., MD, Uzel, Gulbu, MD, Milner, Joshua D., MD
Published in Journal of allergy and clinical immunology (01.02.2013)
Published in Journal of allergy and clinical immunology (01.02.2013)
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Impact of CRISPR/HDR editing versus lentiviral transduction on long-term engraftment and clonal dynamics of HSPCs in rhesus macaques
Lee, Byung-Chul, Gin, Ashley, Wu, Chuanfeng, Singh, Komudi, Grice, Max, Mortlock, Ryland, Abraham, Diana, Fan, Xing, Zhou, Yifan, AlJanahi, Aisha, Choi, Uimook, DeRavin, Suk See, Shin, Taehoon, Hong, Sogun, Dunbar, Cynthia E.
Published in Cell stem cell (04.04.2024)
Published in Cell stem cell (04.04.2024)
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Residual NADPH Oxidase and Survival in Chronic Granulomatous Disease
KUHNS, Douglas B, ALVORD, W. Gregory, ZAREMBER, Kol A, MALECH, Harry L, HOLLAND, Steven M, GALLIN, John I, HELLER, Theo, FELD, Jordan J, PIKE, Kristen M, MARCIANO, Beatriz E, UZEL, Gulbu, SUK SEE DERAVIN, LONG, Debra A, SOULE, Benjamin P
Published in The New England journal of medicine (30.12.2010)
Published in The New England journal of medicine (30.12.2010)
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Residual NADPH Oxidase and Survival in Chronic Granulomatous Disease
Kuhns, Douglas B, Alvord, W. Gregory, Heller, Theo, Feld, Jordan J, Pike, Kristen M, Marciano, Beatriz E, Uzel, Gulbu, DeRavin, Suk See, Priel, Debra A. Long, Soule, Benjamin P, Zarember, Kol A, Malech, Harry L, Holland, Steven M, Gallin, John I
Published in The New England journal of medicine (30.12.2010)
Published in The New England journal of medicine (30.12.2010)
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Impact of CRISPR/HDR editing versus lentiviral transduction on long-term engraftment and clonal dynamics of HSPCs in rhesus macaques
Lee, Byung-Chul, Gin, Ashley, Wu, Chuanfeng, Singh, Komudi, Grice, Max, Mortlock, Ryland, Abraham, Diana, Fan, Xing, Zhou, Yifan, AlJanahi, Aisha, Choi, Uimook, DeRavin, Suk See, Shin, Taehoon, Hong, Sogun, Dunbar, Cynthia E.
Published in Cell stem cell (02.05.2024)
Published in Cell stem cell (02.05.2024)
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P116 SMALL BOWEL INVOLVEMENT IN CHRONIC GRANULOMATOUS DISEASE COLITIS
Bhattacharya, Sumona, Taneja, Sonia, Zerbe, Christa, DeRavin, Suk See, Malech, Harry, Holland, Steven, Koh, Christopher, Heller, Theo
Published in Inflammatory bowel diseases (23.01.2020)
Published in Inflammatory bowel diseases (23.01.2020)
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Gastrointestinal Features of Chronic Granulomatous Disease Found During Endoscopy
Khangura, Sajneet K, Kamal, Natasha, Ho, Nancy, Quezado, Martha, Zhao, Xiongce, Marciano, Beatriz, Simpson, Jennifer, Zerbe, Christa, Uzel, Gulbu, Yao, Michael D, DeRavin, Suk See, Hadigan, Colleen, Kuhns, Douglas B, Gallin, John I, Malech, Harry L, Holland, Steven M, Heller, Theo
Published in Clinical gastroenterology and hepatology (01.03.2016)
Published in Clinical gastroenterology and hepatology (01.03.2016)
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