P071 Evaluation of CFTR modulator efficacy by rectal organoid morphology analysis (ROMA) indexes
Cuyx, S., Ramalho, A.S., Proesmans, M., Boon, M., Dupont, L., De Boeck, K., Vermeulen, F.
Published in Journal of cystic fibrosis (01.06.2023)
Published in Journal of cystic fibrosis (01.06.2023)
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Journal Article
WS04.06 Validation of rectal organoid morphology analysis (ROMA) as a novel physiological CFTR assay for diagnosis of cystic fibrosis
Cuyx, S., Ramalho, A.S., Proesmans, M., Boon, M., Dupont, L., De Boeck, K., Vermeulen, F.
Published in Journal of cystic fibrosis (01.06.2023)
Published in Journal of cystic fibrosis (01.06.2023)
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Journal Article
P025 Assessment of CFTR modulator combinations in rectal organoids from F508del homozygous patients with cystic fibrosis
Cuyx, S., Ramalho, A.S., Proesmans, M., Boon, M., Ensinck, M., Carlon, M.S., Dupont, L., De Boeck, K., Vermeulen, F.
Published in Journal of cystic fibrosis (01.06.2022)
Published in Journal of cystic fibrosis (01.06.2022)
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Journal Article
WS09.02 Theratyping molecular defects of CFTR rare variants in patient derived rectal organoids
Soeffers, Y., Cuyx, S., Proesmans, M., Dupont, L., Van Hoorenbeeck, K., De Wachter, E., Van Biervliet, S., De Boeck, K., Vermeulen, F., Ramalho, A.S.
Published in Journal of cystic fibrosis (01.06.2023)
Published in Journal of cystic fibrosis (01.06.2023)
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Journal Article
692 Importance of cystic fibrosis transmembrane conductance regulator messenger ribonucleic acid testing to uncover other variants in cystic fibrosis genotype that affect cystic fibrosis transmembrane conductance regulator expression
Ramalho, A., Cuyx, S., Boon, M., Proesmans, M., Dupont, L., Van Hoorenbeeck, K., De Wachter, E., Van Biervliet, S., De Boeck, K., Vermeulen, F.
Published in Journal of cystic fibrosis (01.10.2022)
Published in Journal of cystic fibrosis (01.10.2022)
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Journal Article
WS06.03 Novel CFTR modulator combinations maximise functional rescue of G85E and N1303K in rectal organoids
Ensinck, M.M., De Keersmaecker, L., Ramalho, A.S., Cuyx, S., Van Biervliet, S., Dupont, L., Christ, F., Debyser, Z., Vermeulen, F., Carlon, M.S.
Published in Journal of cystic fibrosis (01.06.2022)
Published in Journal of cystic fibrosis (01.06.2022)
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Journal Article
WS11.1 Response to CFTR modulators in organoids from patients with cystic fibrosis as a tool to select candidates to treatment
Ramalho, A. Santo, Cuyx, S., Boon, M., Dupont, L., Proesmans, M., Sarouk, I., Cordero, C.V., Vermeulen, F., De Boeck, K.
Published in Journal of cystic fibrosis (01.06.2020)
Published in Journal of cystic fibrosis (01.06.2020)
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Journal Article
WS09.2 Elexacaftor combinations (partially) restore CFTR function to previously drug-refractory mutations G85E and N1303K
Ensinck, M., De Keersmaecker, L., Ramalho, A.S., Cuyx, S., Van Biervliet, S., De Boeck, K., Christ, F., Debyser, Z., Vermeulen, F., Carlon, M.S.
Published in Journal of cystic fibrosis (2021)
Published in Journal of cystic fibrosis (2021)
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Journal Article
ePS1.03 Investigation of in vitro treatment response to CFTR modulators in patients with cystic fibrosis in a cross-sectional intestinal organoid study
Furstova, E., Ramalho, A.S., Cuyx, S., Proesmans, M., Dupont, L., Vermeulen, F., Amelina, E.L., Kashirskaya, N.Y., Drevinek, P., De Boeck, K.
Published in Journal of cystic fibrosis (01.06.2019)
Published in Journal of cystic fibrosis (01.06.2019)
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