Gene editing of hematopoietic stem cells restores T-cell response in familial hemophagocytic lymphohistiocytosis
Dettmer-Monaco, Viviane, Weißert, Kristoffer, Ammann, Sandra, Monaco, Gianni, Lei, Lei, Gräßel, Linda, Rhiel, Manuel, Rositzka, Julia, Kaufmann, Masako M, Geiger, Kerstin, Andrieux, Geoffroy, Lao, Jessica, Thoulass, Gudrun, Schell, Christoph, Boerries, Melanie, Illert, Anna L, Cornu, Tatjana I, Ehl, Stephan, Aichele, Peter, Cathomen, Toni
Published in Journal of allergy and clinical immunology (01.01.2024)
Published in Journal of allergy and clinical immunology (01.01.2024)
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Biodegradable Nanocarriers Resembling Extracellular Vesicles Deliver Genetic Material with the Highest Efficiency to Various Cell Types
Tarakanchikova, Yana, Alzubi, Jamal, Pennucci, Valentina, Follo, Marie, Kochergin, Boris, Muslimov, Albert, Skovorodkin, Ilya, Vainio, Seppo, Antipina, Maria N., Atkin, Vsevolod, Popov, Alexey, Meglinski, Igor, Cathomen, Toni, Cornu, Tatjana I., Gorin, Dmitry A., Sukhorukov, Gleb B., Nazarenko, Irina
Published in Small (Weinheim an der Bergstrasse, Germany) (01.01.2020)
Published in Small (Weinheim an der Bergstrasse, Germany) (01.01.2020)
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Epitope-engineered human hematopoietic stem cells are shielded from CD123-targeted immunotherapy
Marone, Romina, Landmann, Emmanuelle, Devaux, Anna, Lepore, Rosalba, Seyres, Denis, Zuin, Jessica, Burgold, Thomas, Engdahl, Corinne, Capoferri, Giuseppina, Dell'Aglio, Alessandro, Larrue, Clément, Simonetta, Federico, Rositzka, Julia, Rhiel, Manuel, Andrieux, Geoffroy, Gallagher, Danielle N, Schröder, Markus S, Wiederkehr, Amélie, Sinopoli, Alessandro, Do Sacramento, Valentin, Haydn, Anna, Garcia-Prat, Laura, Divsalar, Christopher, Camus, Anna, Xu, Liwen, Bordoli, Lorenza, Schwede, Torsten, Porteus, Matthew, Tamburini, Jérôme, Corn, Jacob E, Cathomen, Toni, Cornu, Tatjana I, Urlinger, Stefanie, Jeker, Lukas T
Published in The Journal of experimental medicine (04.12.2023)
Published in The Journal of experimental medicine (04.12.2023)
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Cells Expressing the RING Finger Z Protein Are Resistant to Arenavirus Infection
CORNU, Tatiana I, FELDMANN, Heinz, DE LA TORRE, Juan Carlos
Published in Journal of Virology (01.03.2004)
Published in Journal of Virology (01.03.2004)
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Disruption of HIV-1 co-receptors CCR5 and CXCR4 in primary human T cells and hematopoietic stem and progenitor cells using base editing
Knipping, Friederike, Newby, Gregory A., Eide, Cindy R., McElroy, Amber N., Nielsen, Sarah C., Smith, Kyle, Fang, Yongxing, Cornu, Tatjana I., Costa, Caroline, Gutierrez-Guerrero, Alejandra, Bingea, Samuel P., Feser, Colby J., Steinbeck, Benjamin, Hippen, Keli L., Blazar, Bruce R., McCaffrey, Anton, Mussolino, Claudio, Verhoeyen, Els, Tolar, Jakub, Liu, David R., Osborn, Mark J.
Published in Molecular therapy (05.01.2022)
Published in Molecular therapy (05.01.2022)
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Preclinical Evaluation of a Novel TALEN Targeting CCR5 Confirms Efficacy and Safety in Conferring Resistance to HIV‐1 Infection
Romito, Marianna, Juillerat, Alexandre, Kok, Yik Lim, Hildenbeutel, Markus, Rhiel, Manuel, Andrieux, Geoffroy, Geiger, Johannes, Rudolph, Carsten, Mussolino, Claudio, Duclert, Aymeric, Metzner, Karin J., Duchateau, Philippe, Cathomen, Toni, Cornu, Tatjana I.
Published in Biotechnology journal (01.01.2021)
Published in Biotechnology journal (01.01.2021)
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Correction: Patients and mice with deficiency in the SNARE protein SYNTAXIN-11 have a secondary B cell defect
Kögl, Tamara, Chang, Hsin-Fang, Staniek, Julian, Chiang, Samuel C C, Thoulass, Gudrun, Lao, Jessica, Weißert, Kristoffer, Dettmer-Monaco, Viviane, Geiger, Kerstin, Manna, Paul T, Beziat, Vivien, Momenilandi, Mana, Tu, Szu-Min, Keppler, Selina J, Pattu, Varsha, Wolf, Philipp, Kupferschmid, Laurence, Tholen, Stefan, Covill, Laura E, Ebert, Karolina, Straub, Tobias, Groß, Miriam, Gather, Ruth, Engel, Helena, Salzer, Ulrich, Schell, Christoph, Maier, Sarah, Lehmberg, Kai, Cornu, Tatjana I, Pircher, Hanspeter, Shahrooei, Mohammad, Parvaneh, Nima, Elling, Roland, Rizzi, Marta, Bryceson, Yenan T, Ehl, Stephan, Aichele, Peter, Ammann, Sandra
Published in The Journal of experimental medicine (01.07.2024)
Published in The Journal of experimental medicine (01.07.2024)
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Journal Article
Patients and mice with deficiency in the SNARE protein SYNTAXIN-11 have a secondary B cell defect
Kögl, Tamara, Chang, Hsin-Fang, Staniek, Julian, Chiang, Samuel C C, Thoulass, Gudrun, Lao, Jessica, Weißert, Kristoffer, Dettmer-Monaco, Viviane, Geiger, Kerstin, Manna, Paul T, Beziat, Vivien, Momenilandi, Mana, Tu, Szu-Min, Keppler, Selina J, Pattu, Varsha, Wolf, Philipp, Kupferschmid, Laurence, Tholen, Stefan, Covill, Laura E, Ebert, Karolina, Straub, Tobias, Groß, Miriam, Gather, Ruth, Engel, Helena, Salzer, Ulrich, Schell, Christoph, Maier, Sarah, Lehmberg, Kai, Cornu, Tatjana I, Pircher, Hanspeter, Shahrooei, Mohammad, Parvaneh, Nima, Elling, Roland, Rizzi, Marta, Bryceson, Yenan T, Ehl, Stephan, Aichele, Peter, Ammann, Sandra
Published in The Journal of experimental medicine (01.07.2024)
Published in The Journal of experimental medicine (01.07.2024)
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Versatile and efficient genome editing in human cells by combining zinc-finger nucleases with adeno-associated viral vectors
Händel, Eva-Maria, Gellhaus, Katharina, Khan, Kafaitullah, Bednarski, Christien, Cornu, Tatjana I, Müller-Lerch, Felix, Kotin, Robert M, Heilbronn, Regine, Cathomen, Toni
Published in Human gene therapy (01.03.2012)
Published in Human gene therapy (01.03.2012)
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Safe and effective liver-directed AAV-mediated homology-independent targeted integration in mouse models of inherited diseases
Esposito, Federica, Dell’Aquila, Fabio, Rhiel, Manuel, Auricchio, Stefano, Chmielewski, Kay Ole, Andrieux, Geoffroy, Ferla, Rita, Horrach, Paula Sureda, Padmanabhan, Arjun, Di Cunto, Roberto, Notaro, Simone, Santeularia, Manel Llado, Boerries, Melanie, Dell’Anno, Margherita, Nusco, Edoardo, Padula, Agnese, Nutarelli, Sofia, Cornu, Tatjana I., Sorrentino, Nicolina Cristina, Piccolo, Pasquale, Trapani, Ivana, Cathomen, Toni, Auricchio, Alberto
Published in Cell reports. Medicine (16.07.2024)
Published in Cell reports. Medicine (16.07.2024)
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Editing CCR5: a novel approach to HIV gene therapy
Cornu, Tatjana I, Mussolino, Claudio, Bloom, Kristie, Cathomen, Toni
Published in Advances in experimental medicine and biology (01.01.2015)
Published in Advances in experimental medicine and biology (01.01.2015)
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Measles virus and canine distemper virus target proteins into a TAP-independent MHC class I-restricted antigen-processing pathway
Neumeister, Claudia, Nanan, Ralph, Cornu, Tatjana I, Luder, Carsten G. K, ter Meulen, Volker, Naim, Hussein, Niewiesk, Stefan
Published in Journal of general virology (01.02.2001)
Published in Journal of general virology (01.02.2001)
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Allele-Specific Disruption of a Common ISTAT3/I Autosomal Dominant Allele Is Not Sufficient to Restore Downstream Signaling in Patient-Derived T Cells
König, Saskia, Fliegauf, Manfred, Rhiel, Manuel, Grimbacher, Bodo, Cornu, Tatjana I, Cathomen, Toni, Mussolino, Claudio
Published in Genes (01.10.2022)
Published in Genes (01.10.2022)
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Function-Preserving Single Amino Acid Substitutions Shield Hematopoietic Stem and Progenitor Cells from CD117 Targeted Immunotherapy In Vivo
Marone, Romina, Lepore, Rosalba, Rositzka, Julia, Dettmer-Monaco, Viviane, dell' Aglio, Alessandro, Capoferri, Giuseppina, Brault, Julie, Ten Buren, Emiel, Burgold, Thomas, Camus, Anna, Divsalar, Christopher, Garcia Prat, Laura, Haydn, Anna, Hermann, Felix, Heugel, Marcel, Knezevic, Andreja, Lehmann, Frank Michael, Do Sacramento, Valentin, Sinopoli, Alessandro, Wellinger, Lisa C, Wiederkehr, Amélie, Yumlu, Saniye, Cathomen, Toni, Winkler, Thomas, Cornu, Tatjana I, Urlinger, Stefanie, Jeker, Lukas T
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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A Highly Efficient and GMP Compliant Protocol to Manufacture CCR5 Edited Cells to Treat HIV Infection
Romito, Marianna, Meyer, Emily, Poddar, Sushmita, Heinz, Helena, Rositzka, Julia, Hildenbeutel, Markus, Gautron, Anne-Sophie, Busser, Brian W, Kok, Yik Lim, Turchiano, Giandomenico, Haas, Simone, Schäfer, Richard, Smith, Julianne, Metzner, Karin J, Mussolino, Claudio, Duchateau, Philippe, Cathomen, Toni, Cornu, Tatjana I
Published in Blood (29.11.2018)
Published in Blood (29.11.2018)
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Gene Therapy Getting Personal: Mutation-Specific Editing and Gene Addition Strategies for β-Thalassaemia
Lederer, Carsten W., Patsali, Petros, Mussolino, Claudio, Turchiano, Giandomenico, Papasavva, Panayiota, Romito, Marianna, Stephanou, Coralea, Cornu, Tatjana I., Kolnagou, Annita, Christou, Soteroula, Sitarou, Maria, Antoniou, Mike N., Cathomen, Toni, Kleanthous, Marina
Published in Hemoglobin (02.11.2019)
Published in Hemoglobin (02.11.2019)
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Evidence That the Hypermutated M Protein of a Subacute Sclerosing Panencephalitis Measles Virus Actively Contributes to the Chronic Progressive CNS Disease
Patterson, John B., Cornu, Tatjana I., Redwine, Jeffrey, Dales, Samuel, Lewicki, Hanna, Holz, Andreas, Thomas, Diane, Billeter, Martin A., Oldstone, Michael B.A.
Published in Virology (New York, N.Y.) (20.12.2001)
Published in Virology (New York, N.Y.) (20.12.2001)
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