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Long-acting recombinant coagulation factor IX albumin fusion protein (rIX-FP) in hemophilia B: results of a phase 3 trial
Santagostino, Elena, Martinowitz, Uri, Lissitchkov, Toshko, Pan-Petesch, Brigitte, Hanabusa, Hideji, Oldenburg, Johannes, Boggio, Lisa, Negrier, Claude, Pabinger, Ingrid, von Depka Prondzinski, Mario, Altisent, Carmen, Castaman, Giancarlo, Yamamoto, Koji, Álvarez-Roman, Maria-Teresa, Voigt, Christine, Blackman, Nicole, Jacobs, Iris
Published in Blood (07.04.2016)
Published in Blood (07.04.2016)
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Safety, pharmacokinetics, and pharmacodynamics of a next‐generation subcutaneously administered coagulation factor IX variant, dalcinonacog alfa, in previously treated hemophilia B patients
You, Chur Woo, Hong, Seung‐Beom, Kim, Suyeong, Shin, Ho‐Jin, Kim, Jin Seok, Han, Jung Woo, Kim, Soo‐Jeong, Kim, Do Young, Lee, Martin, Levy, Howard
Published in Journal of thrombosis and haemostasis (01.04.2021)
Published in Journal of thrombosis and haemostasis (01.04.2021)
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IDEAL study: A real‐world assessment of pattern of use and clinical outcomes with recombinant coagulation factor IX albumin fusion protein (rIX‐FP) in patients with haemophilia B in Italy
Tagliaferri, Annarita, Molinari, Angelo Claudio, Peyvandi, Flora, Coppola, Antonio, Demartis, Francesco, Biasoli, Chiara, Borchiellini, Alessandra, Cultrera, Dorina, De Cristofaro, Raimondo, Daniele, Filomena, Giordano, Paola, Marchesini, Emanuela, Margaglione, Maurizio, Marino, Renato, Pollio, Berardino, Radossi, Paolo, Santoro, Cristina, Santoro, Rita Carlotta, Siragusa, Sergio, Sottilotta, Gianluca, Tosetto, Alberto, Piscitelli, Lydia, Villa, Maria Rosaria, Zanon, Ezio, Finardi, Adele, Schiavetti, Irene, Vaccari, Daniella, Castaman, Giancarlo
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2023)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2023)
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Safety and pharmacokinetics of a novel recombinant fusion protein linking coagulation factor IX with albumin (rIX-FP) in hemophilia B patients
Santagostino, Elena, Negrier, Claude, Klamroth, Robert, Tiede, Andreas, Pabinger-Fasching, Ingrid, Voigt, Christine, Jacobs, Iris, Morfini, Massimo
Published in Blood (20.09.2012)
Published in Blood (20.09.2012)
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Multicentre, randomized, open-label study of on-demand treatment with two prophylaxis regimens of recombinant coagulation factor IX in haemophilia B subjects
Valentino, L. A., Rusen, L., Elezovic, I., Smith, L. M., Korth-Bradley, J. M., Rendo, P.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2014)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2014)
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Results of a phase I/II open-label, safety and efficacy trial of coagulation factor IX (recombinant), albumin fusion protein in haemophilia B patients
Martinowitz, U., Lissitchkov, T., Lubetsky, A., Jotov, G., Barazani-Brutman, T., Voigt, C., Jacobs, I., Wuerfel, T., Santagostino, E.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2015)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2015)
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Long-Term Safety and Efficacy of Recombinant Coagulation Factor IX Albumin Fusion Protein (rIX-FP) in Previously Treated Pediatric Patients with Hemophilia B: Results from a Phase 3b Extension Study
Kenet, Gili, Chambost, Hervé, Male, Christoph, Halimeh, Susan, Lambert, Thierry, Li, Yanyan, Seifert, Wilfried, Santagostino, Elena
Published in Thrombosis and haemostasis (01.04.2020)
Published in Thrombosis and haemostasis (01.04.2020)
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Evolutionary insights into coagulation factor IX Padua and other high-specific-activity variants
Samelson-Jones, Benjamin J., Finn, Jonathan D., Raffini, Leslie J., Merricks, Elizabeth P., Camire, Rodney M., Nichols, Timothy C., Arruda, Valder R.
Published in Blood advances (09.03.2021)
Published in Blood advances (09.03.2021)
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SVA retrotransposition in exon 6 of the coagulation factor IX gene causing severe hemophilia B
Nakamura, Yuki, Murata, Moe, Takagi, Yuki, Kozuka, Toshihiro, Nakata, Yukiko, Hasebe, Ryo, Takagi, Akira, Kitazawa, Jun-ichi, Shima, Midori, Kojima, Tetsuhito
Published in International journal of hematology (01.07.2015)
Published in International journal of hematology (01.07.2015)
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Recombinant Fusion Protein Linking Coagulation Factor IX with Albumin (RIX-FP) in Previously Treated Adolescents/Adults with Hemophilia B: Long-Term Efficacy and Safety from an Ongoing Phase 3b Extension Clinical Trial
Pabinger, Ingrid, Santagostino, Elena, Brainsky, Andres, Powell, Jerry S., Li, Yanyan, Seifert, Wilfried
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Recombinant Fusion Protein Linking Coagulation Factor IX with Albumin (RIX-FP) in Previously Treated Children < 12 Years of Age with Hemophilia B: Long-Term Efficacy and Safety from an Ongoing Phase 3b Extension Clinical Trial
Kenet, Gili, Brainsky, Andres, Powell, Jerry S., Li, Yanyan, Seifert, Wilfried
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Long-Term Use of Coagulation Factor IX (Recombinant) Albumin Fusion Protein (rIX-FP) in Previously Treated Patients with Hemophilia B in the Prolong-9FP Program
Lubetsky, Aaron, Martinowitz, Uri, Lissitchkov, Toshko, Voigt, Christine, Wolko, Denise, Jacobs, Iris C., Santagostino, Elena
Published in Blood (03.12.2015)
Published in Blood (03.12.2015)
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Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector
Herzog, Roland W., Yang, Edmund Y., Couto, Linda B., Hagstrom, J. Nathan, Elwell, Dan, Fields, Paul A., Burton, Melissa, Bellinger, Dwight A., Read, Marjorie S., Brinkhous, Kenneth M., Podsakoff, Gregory M., Nichols, Timothy C., Kurtzman, Gary J., High, Katherine A.
Published in Nature medicine (01.01.1999)
Published in Nature medicine (01.01.1999)
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Efficacy and Safety Results of Prolong-9FP Clinical Program of Recombinant Fusion Protein Linking Coagulation Factor IX with Albumin (rIX-FP) in Previously Treated Patients with Hemophilia B
Santagostino, Elena, Voigt, Christine, Wolko, Denise, Cole, Grace, Li, Yanyan, Jacobs, Iris C.
Published in Blood (03.12.2015)
Published in Blood (03.12.2015)
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Efficacy and Safety of Recombinant Fusion Protein Linking Coagulation Factor IX with Albumin (rIX-FP) in Previously Treated Patients with Hemophilia B Undergoing Major Orthopedic Surgeries
Negrier, Claude, Lepatan, Lynda Mae, Karim, Faralzah, Lienhart, Anne, Wolko, Denise, Voigt, Christine, Jacobs, Iris C., Santagostino, Elena
Published in Blood (03.12.2015)
Published in Blood (03.12.2015)
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Pharmacokinetic Results of Two Phase III Clinical Studies of Coagulation Factor IX (Recombinant) Albumin Fusion Protein (rIX-FP) in Previously Treated Patients with Hemophilia B (PROLONG-9FP)
Santagostino, Elena, Jacobs, Iris C., Voigt, Christine, Feussner, Annettee, Limsakun, Tharin
Published in Blood (06.12.2014)
Published in Blood (06.12.2014)
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Efficacy, PK and Safety Results of Clinical Study Of Recombinant Fusion Protein Linking Coagulation Factor IX With Albumin (rIX-FP) In Previously Treated Patients With Hemophilia B
Lubetsky, Aaron, Lissitchkov, Toshko, Santagostino, Elena, Jotov, Gantcho, Barazani-Brutman, Tami, Voigt, Christine, Moises, Tina, Jacobs, Iris C., Martinowitz, Uri
Published in Blood (15.11.2013)
Published in Blood (15.11.2013)
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