Loading…
Loading…
BCL11A enhancer dissection by Cas9-mediated in situ saturating mutagenesis
Canver, Matthew C., Smith, Elenoe C., Sher, Falak, Pinello, Luca, Sanjana, Neville E., Shalem, Ophir, Chen, Diane D., Schupp, Patrick G., Vinjamur, Divya S., Garcia, Sara P., Luc, Sidinh, Kurita, Ryo, Nakamura, Yukio, Fujiwara, Yuko, Maeda, Takahiro, Yuan, Guo-Cheng, Zhang, Feng, Orkin, Stuart H., Bauer, Daniel E.
Published in Nature (London) (12.11.2015)
Published in Nature (London) (12.11.2015)
Get full text
Journal Article
Loading…
Exome-wide Association Study Identifies GREB1L Mutations in Congenital Kidney Malformations
Sanna-Cherchi, Simone, Khan, Kamal, Westland, Rik, Krithivasan, Priya, Fievet, Lorraine, Rasouly, Hila Milo, Ionita-Laza, Iuliana, Capone, Valentina P., Fasel, David A., Kiryluk, Krzysztof, Kamalakaran, Sitharthan, Bodria, Monica, Otto, Edgar A., Sampson, Matthew G., Gillies, Christopher E., Vega-Warner, Virginia, Vukojevic, Katarina, Pediaditakis, Igor, Makar, Gabriel S., Mitrotti, Adele, Verbitsky, Miguel, Martino, Jeremiah, Liu, Qingxue, Na, Young-Ji, Goj, Vinicio, Ardissino, Gianluigi, Gigante, Maddalena, Gesualdo, Loreto, Janezcko, Magdalena, Zaniew, Marcin, Mendelsohn, Cathy Lee, Shril, Shirlee, Hildebrandt, Friedhelm, van Wijk, Joanna A.E., Arapovic, Adela, Saraga, Marijan, Allegri, Landino, Izzi, Claudia, Scolari, Francesco, Tasic, Velibor, Ghiggeri, Gian Marco, Latos-Bielenska, Anna, Materna-Kiryluk, Anna, Mane, Shrikant, Goldstein, David B., Lifton, Richard P., Katsanis, Nicholas, Davis, Erica E., Gharavi, Ali G.
Published in American journal of human genetics (02.11.2017)
Published in American journal of human genetics (02.11.2017)
Get full text
Journal Article
Loading…
Elimination of Calm1 long 3′-UTR mRNA isoform by CRISPR–Cas9 gene editing impairs dorsal root ganglion development and hippocampal neuron activation in mice
Bae, Bongmin, Gruner, Hannah N., Lynch, Maebh, Feng, Ting, So, Kevin, Oliver, Daniel, Mastick, Grant S., Yan, Wei, Pieraut, Simon, Miura, Pedro
Published in RNA (Cambridge) (01.10.2020)
Published in RNA (Cambridge) (01.10.2020)
Get full text
Journal Article
Loading…
Engineering microdeletions and microduplications by targeting segmental duplications with CRISPR
Tai, Derek J C, Ragavendran, Ashok, Manavalan, Poornima, Stortchevoi, Alexei, Seabra, Catarina M, Erdin, Serkan, Collins, Ryan L, Blumenthal, Ian, Chen, Xiaoli, Shen, Yiping, Sahin, Mustafa, Zhang, Chengsheng, Lee, Charles, Gusella, James F, Talkowski, Michael E
Published in Nature neuroscience (01.03.2016)
Published in Nature neuroscience (01.03.2016)
Get full text
Journal Article
Loading…
An autoregulatory enhancer controls mammary-specific STAT5 functions
Metser, Gil, Shin, Ha Youn, Wang, Chaochen, Yoo, Kyung Hyun, Oh, Sumin, Villarino, Alejandro V., O'Shea, John J., Kang, Keunsoo, Hennighausen, Lothar
Published in Nucleic acids research (18.02.2016)
Published in Nucleic acids research (18.02.2016)
Get full text
Journal Article
Loading…
Molecular mechanisms of CRISPR-mediated microbial immunity
Gasiunas, Giedrius, Sinkunas, Tomas, Siksnys, Virginijus
Published in Cellular and molecular life sciences : CMLS (01.02.2014)
Published in Cellular and molecular life sciences : CMLS (01.02.2014)
Get full text
Journal Article
Loading…
Loading…
Association between living environment and human oral viral ecology
Robles-Sikisaka, Refugio, Ly, Melissa, Boehm, Tobias, Naidu, Mayuri, Salzman, Julia, Pride, David T
Published in The ISME Journal (01.09.2013)
Published in The ISME Journal (01.09.2013)
Get full text
Journal Article
Loading…
Personalized therapeutic strategies for patients with retinitis pigmentosa
Zheng, Andrew, Li, Yao, Tsang, Stephen H
Published in Expert opinion on biological therapy (01.03.2015)
Published in Expert opinion on biological therapy (01.03.2015)
Get more information
Journal Article
Loading…
Fragmentation of the CRISPR-Cas Type I-B signature protein Cas8b
Richter, Hagen, Rompf, Judith, Wiegel, Julia, Rau, Kristina, Randau, Lennart
Published in Biochimica et biophysica acta. General subjects (01.11.2017)
Published in Biochimica et biophysica acta. General subjects (01.11.2017)
Get full text
Journal Article
Loading…