Transposon-mediated gene transfer into adult and induced pluripotent stem cells
Belay, Eyayu, Dastidar, Sumitava, VandenDriessche, Thierry, Chuah, Marinee K L
Published in Current gene therapy (01.10.2011)
Published in Current gene therapy (01.10.2011)
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Molecular evolution of a novel hyperactive Sleeping Beauty transposase enables robust stable gene transfer in vertebrates
Chuah, Marinee K L, Ma, Ling, VandenDriessche, Thierry, Manoj, Namitha, Samara-Kuko, Ermira, Grzela, Dawid P, Schmitt, Andrea, Pryputniewicz, Diana, Fletcher, Bradley, Jerchow, Boris, Mátés, Lajos, Matrai, Janka, Gysemans, Conny, Becker, Katja, Miskey, Csaba, Belay, Eyayu, Acosta-Sanchez, Abel, Ivics, Zoltán, Izsvák, Zsuzsanna
Published in Nature genetics (01.06.2009)
Published in Nature genetics (01.06.2009)
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Restoration of Plasma von Willebrand Factor Deficiency Is Sufficient to Correct Thrombus Formation After Gene Therapy for Severe von Willebrand Disease
De Meyer, Simon F, Vandeputte, Nele, Pareyn, Inge, Petrus, Inge, Lenting, Peter J, Chuah, Marinee K.L, VandenDriessche, Thierry, Deckmyn, Hans, Vanhoorelbeke, Karen
Published in Arteriosclerosis, thrombosis, and vascular biology (01.09.2008)
Published in Arteriosclerosis, thrombosis, and vascular biology (01.09.2008)
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Efficient Lentiviral Transduction and Improved Engraftment of Human Bone Marrow Mesenchymal Cells
Van Damme, An, Thorrez, Lieven, Ma, Ling, Vandenburgh, Herman, Eyckmans, Jeroen, Dell'Accio, Francesco, De Bari, Cosimo, Luyten, Frank, Lillicrap, David, Collen, Désiré, VandenDriessche, Thierry, Chuah, Marinee K.L.
Published in Stem cells (Dayton, Ohio) (01.04.2006)
Published in Stem cells (Dayton, Ohio) (01.04.2006)
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Comparative Analysis of Transposable Element Vector Systems in Human Cells
Grabundzija, Ivana, Irgang, Markus, Mátés, Lajos, Belay, Eyayu, Matrai, Janka, Gogol-Döring, Andreas, Kawakami, Koichi, Chen, Wei, Ruiz, Patricia, Chuah, Marinee K.L., VandenDriessche, Thierry, Izsvák, Zsuzsanna, Ivics, Zoltán
Published in Molecular therapy (01.06.2010)
Published in Molecular therapy (01.06.2010)
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Emerging potential of transposons for gene therapy and generation of induced pluripotent stem cells
VandenDriessche, Thierry, Ivics, Zoltán, Izsvák, Zsuzsanna, Chuah, Marinee K.L.
Published in Blood (20.08.2009)
Published in Blood (20.08.2009)
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Gene therapy for hemophilia: hopes and hurdles
Chuah, Marinee K.L, Collen, Desire, VandenDriessche, Thierry
Published in Critical reviews in oncology/hematology (01.09.1998)
Published in Critical reviews in oncology/hematology (01.09.1998)
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Codon optimization of human factor VIII cDNAs leads to high-level expression
Ward, Natalie J., Buckley, Suzanne M.K., Waddington, Simon N., VandenDriessche, Thierry, Chuah, Marinee K.L., Nathwani, Amit C., McIntosh, Jenny, Tuddenham, Edward G.D., Kinnon, Christine, Thrasher, Adrian J., McVey, John H.
Published in Blood (20.01.2011)
Published in Blood (20.01.2011)
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Intrinsic cell memory reinforces myogenic commitment of pericyte-derived iPSCs
Quattrocelli, Mattia, Palazzolo, Giacomo, Floris, Giuseppe, Schöffski, Patrick, Anastasia, Luigi, Orlacchio, Aldo, Vandendriessche, Thierry, Chuah, Marinee KL, Cossu, Giulio, Verfaillie, Catherine, Sampaolesi, Maurilio
Published in The Journal of pathology (01.04.2011)
Published in The Journal of pathology (01.04.2011)
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Efficacy and safety of adeno‐associated viral vectors based on serotype 8 and 9 vs. lentiviral vectors for hemophilia B gene therapy
VANDENDRIESSCHE, T., THORREZ, L., ACOSTA‐SANCHEZ, A., PETRUS, I., WANG, L., MA, L., DE WAELE, L., IWASAKI, Y., GILLIJNS, V., WILSON, J. M., COLLEN, D., CHUAH, M. K. L.
Published in Journal of thrombosis and haemostasis (01.01.2007)
Published in Journal of thrombosis and haemostasis (01.01.2007)
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Nanoparticles for the delivery of genes and drugs to human hepatocytes
Kuroda, Shun'ichi, Yamada, Tadanori, Iwasaki, Yasushi, Tada, Hiroko, Iwabuki, Hidehiko, Chuah, Marinee KL, VandenDriessche, Thierry, Fukuda, Hideki, Kondo, Akihiko, Ueda, Masakazu, Seno, Masaharu, Tanizawa, Katsuyuki
Published in Nature biotechnology (01.08.2003)
Published in Nature biotechnology (01.08.2003)
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Novel Hyperactive Transposons for Genetic Modification of Induced Pluripotent and Adult Stem Cells: A Nonviral Paradigm for Coaxed Differentiation
Belay, Eyayu, Mátrai, Janka, Acosta‐Sanchez, Abel, Ma, Ling, Quattrocelli, Mattia, Mátés, Lajos, Sancho‐Bru, Pau, Geraerts, Martine, Yan, Bing, Vermeesch, Joris, Rincón, Melvin Yesid, Samara‐Kuko, Ermira, Ivics, Zoltán, Verfaillie, Catherine, Sampaolesi, Maurilio, Izsvák, Zsuzsanna, VandenDriessche, Thierry, Chuah, Marinee K. L.
Published in Stem cells (Dayton, Ohio) (01.10.2010)
Published in Stem cells (Dayton, Ohio) (01.10.2010)
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Lentiviral vectors containing the human immunodeficiency virus type-1 central polypurine tract can efficiently transduce nondividing hepatocytes and antigen-presenting cells in vivo
VandenDriessche, Thierry, Thorrez, Lieven, Naldini, Luigi, Follenzi, Antonia, Moons, Lieve, Berneman, Zwi, Collen, Desire, Chuah, Marinee K.L.
Published in Blood (01.08.2002)
Published in Blood (01.08.2002)
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Therapeutic factor VIII levels and negligible toxicity in mouse and dog models of hemophilia A following gene therapy with high-capacity adenoviral vectors
Chuah, Marinee K.L., Schiedner, Gudrun, Thorrez, Lieven, Brown, Brian, Johnston, Marion, Gillijns, Veerle, Hertel, Sabine, Van Rooijen, Nico, Lillicrap, David, Collen, Désiré, VandenDriessche, Thierry, Kochanek, Stefan
Published in Blood (01.03.2003)
Published in Blood (01.03.2003)
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Preclinical and clinical progress in hemophilia gene therapy
Mátrai, Janka, Chuah, Marinee K L, VandenDriessche, Thierry
Published in Current opinion in hematology (01.09.2010)
Published in Current opinion in hematology (01.09.2010)
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PiggyBac toolbox
Di Matteo, Mario, Mátrai, Janka, Belay, Eyayu, Firdissa, Tewodros, Vandendriessche, Thierry, Chuah, Marinee K L
Published in Methods in molecular biology (Clifton, N.J.) (2012)
Published in Methods in molecular biology (Clifton, N.J.) (2012)
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