Improved Specificity and Safety of Anti-Hepatitis B Virus TALENs Using Obligate Heterodimeric FokI Nuclease Domains
Smith, Tiffany, Singh, Prashika, Chmielewski, Kay Ole, Bloom, Kristie, Cathomen, Toni, Arbuthnot, Patrick, Ely, Abdullah
Published in Viruses (12.07.2021)
Published in Viruses (12.07.2021)
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On- and off-target effects of paired CRISPR-Cas nickase in primary human cells
Klermund, Julia, Rhiel, Manuel, Kocher, Thomas, Chmielewski, Kay Ole, Bischof, Johannes, Andrieux, Geoffroy, el Gaz, Melina, Hainzl, Stefan, Boerries, Melanie, Cornu, Tatjana I., Koller, Ulrich, Cathomen, Toni
Published in Molecular therapy (01.05.2024)
Published in Molecular therapy (01.05.2024)
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Safe and effective liver-directed AAV-mediated homology-independent targeted integration in mouse models of inherited diseases
Esposito, Federica, Dell’Aquila, Fabio, Rhiel, Manuel, Auricchio, Stefano, Chmielewski, Kay Ole, Andrieux, Geoffroy, Ferla, Rita, Horrach, Paula Sureda, Padmanabhan, Arjun, Di Cunto, Roberto, Notaro, Simone, Santeularia, Manel Llado, Boerries, Melanie, Dell’Anno, Margherita, Nusco, Edoardo, Padula, Agnese, Nutarelli, Sofia, Cornu, Tatjana I., Sorrentino, Nicolina Cristina, Piccolo, Pasquale, Trapani, Ivana, Cathomen, Toni, Auricchio, Alberto
Published in Cell reports. Medicine (16.07.2024)
Published in Cell reports. Medicine (16.07.2024)
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