Development of an mRNA replacement therapy for phenylketonuria
Perez-Garcia, Carlos G., Diaz-Trelles, Ramon, Vega, Jerel Boyd, Bao, Yanjie, Sablad, Marciano, Limphong, Patty, Chikamatsu, Simon, Yu, Hailong, Taylor, Wendy, Karmali, Priya P., Tachikawa, Kiyoshi, Chivukula, Padmanabh
Published in Molecular therapy. Nucleic acids (14.06.2022)
Published in Molecular therapy. Nucleic acids (14.06.2022)
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