Case report: Novel treatment regimen for enterovirus encephalitis in SCID
Chetty, Kritika, Cheng, Iek, Kaliakatsos, Marios, Gonzalez-Granado, Luis Ignacio, Klapsa, Dimitra, Martin, Javier, Bamford, Alasdair, Breuer, Judith, Booth, Claire
Published in Frontiers in immunology (13.09.2022)
Published in Frontiers in immunology (13.09.2022)
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Journal Article
Severe Leukocyte Adhesion Deficiency-I (LAD-I) Lentiviral-Mediated Ex-Vivo Gene Therapy: Ongoing Phase 1/2 Study Results
Booth, Claire, Sevilla, Julian, Lopez, Maria Chitty, Almarza, Elena, Zubicaray, Josune, Chetty, Kritika, Moore, Theodore, Bueren, Juan, Schwartz, Jonathan, Kohn, Donald
Published in Clinical immunology (Orlando, Fla.) (01.05.2023)
Published in Clinical immunology (Orlando, Fla.) (01.05.2023)
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Journal Article
Lentiviral Gene Therapy with Low Dose Conditioning for X-Linked SCID Results in Complete Immune Reconstitution and No Evidence of Clonal Expansion
Booth, Claire, Kohn, Donald B., Armant, Myriam, Prockop, Susan, Buckland, Karen, Chandra, Sharat, Chandrakasan, Shanmuganathan, Chetty, Kritika, Dansereau, Colleen, de Oliveira, Satiro, Everett, John, León Rico, Diego, London, Wendy B., Xu-Bayford, Jin Hua, Moore, Theodore B., Nagarsheth, Nisha, Parikh, Suhag, Terrazas, Dayna, White, Shanna L, Schambach, Axel, Bushman, Frederic D., Thrasher, Adrian J., Williams, David A., Pai, Sung-Yun
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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Journal Article
Lentiviral-mediated Gene Therapy for Patients with Fanconi Anemia [Group A]: Updated Results from Global RP-L102 Clinical Trials
Czechowicz, Agnieszka, Sevilla, Julián, Booth, Claire, Agarwal, Rajni, Zubicaray, Josune, Río, Paula, Navarro, Susana, Chetty, Kritika, O'Toole, Grainne, Xu-Bayford, Jinhua, Ancliff, Philip, Sebastián, Elena, Choi, Grace, Zeini, Miriam, Nicoletti, Eileen, Wagner, John E, Rao, Gayatri R., Thrasher, Adrian J., Schwartz, Jonathan D., Roncarolo, Maria Grazia, Bueren, Juan A.
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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Journal Article
Interim Results from an Ongoing Phase 1/2 Study of Lentiviral-mediated Ex-vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I)
Booth, Claire, Sevilla, Julián, Rao, Gayatri R., Chitty Lopez, Maria, Almarza, Elena, Terrazas, Dayna, Zubicaray, Josune, González Vicent, Marta, Chetty, Kritika, O'Toole, Grainne, Xu-Bayford, Jinhua, Nicoletti, Eileen, Fernandes, Augustine, Kuo, Caroline, de Oliveira, Satiro, Moore, Theodore B., Choi, Grace, Zeini, Miriam, Mesa-Núñez, Cristina, Thrasher, Adrian J., Bueren, Juan A., Schwartz, Jonathan D., Kohn, Donald B.
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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Journal Article
Novel antivirals for severe enterovirus infection in immunocompromised hosts; A case series
Meinhardt, Andrea, Reilly, Liam, Kaliakatsos, Marios, Abdel-Aziz, Khaled, Alsharidah, Sondus, Bodi, Istvan, Booth, Claire, Chetty, Kritika, Evans, Jennifer, Ferreras-Antolín, Laura, Froude, Susannah, Galtrey, Clare M., Guruprasad, Suba, Hadden, Robert D., Hassell, Jane, Hyöty, Heikki, Kreins, Alexandra Y., Laiho, Jutta E., Lowe, David M., Lunn, Michael P., Mankad, Kshitij, Struik, Siske, Whittaker, Elizabeth, Worth, Austen, Yong, Patrick, Zhang, Liqun, Breuer, Judith, Kadambari, Seilesh
Published in The Journal of infection (01.05.2024)
Published in The Journal of infection (01.05.2024)
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Journal Article
Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim Results from an Ongoing Phase 1/2 Study
Booth, Claire, Sevilla, Julian, Rao, Gayatri, Lopez, Maria Chitty, Almarza, Elena, Terrazas, Dayna, Zubicaray, Josune, Gonzalez-Vicent, Marta, Chetty, Kritika, Xu-Bayford, Jinhua, O’Toole, Grainne, Fernandes, Augustine, Kuo, Caroline Y., De Oliveira, Satiro N., Mesa-Núñez, Cristina, Moore, Theodore B., Nicoletti, Eileen, Choi, Grace, Zeini, Miriam, Thrasher, Adrian J., Bueren, Juan, Schwartz, Jonathan, Kohn, Donald B.
Published in Transplantation and cellular therapy (01.02.2023)
Published in Transplantation and cellular therapy (01.02.2023)
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Journal Article
Lentiviral-Mediated Gene Therapy for Patients with Fanconi Anemia [Group A]: Updated Results from Global RP-L102 Clinical Trials
Czechowicz, Agnieszka, Sevilla, Julian, Booth, Claire, Agarwal, Rajni, Zubicaray, Josune, Río, Paula, Navarro, Susana, Chetty, Kritika, O’Toole, Grainne, Xu-Bayford, Jinhua, Ancliff, Philip, Sebastián, Elena, Choi, Grace, Zeini, Miriam, Nicoletti, Eileen, Wagner, John E., Rao, Gayatri, Thrasher, Adrian J., Schwartz, Jonathan, Roncarolo, Maria Grazia, Bueren, Juan
Published in Transplantation and cellular therapy (01.02.2023)
Published in Transplantation and cellular therapy (01.02.2023)
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Journal Article
113 - Lentiviral-Mediated Gene Therapy for Patients with Fanconi Anemia [Group A]: Updated Results from Global RP-L102 Clinical Trials
Czechowicz, Agnieszka, Sevilla, Julian, Booth, Claire, Agarwal, Rajni, Zubicaray, Josune, Río, Paula, Navarro, Susana, Chetty, Kritika, O’Toole, Grainne, Xu-Bayford, Jinhua, Ancliff, Philip, Sebastián, Elena, Choi, Grace, Zeini, Miriam, Nicoletti, Eileen, Wagner, John E., Rao, Gayatri, Thrasher, Adrian J., Schwartz, Jonathan, Roncarolo, Maria Grazia, Bueren, Juan
Published in Transplantation and cellular therapy (01.02.2023)
Published in Transplantation and cellular therapy (01.02.2023)
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Journal Article
3 - Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim Results from an Ongoing Phase 1/2 Study
Booth, Claire, Sevilla, Julian, Rao, Gayatri, Lopez, Maria Chitty, Almarza, Elena, Terrazas, Dayna, Zubicaray, Josune, Gonzalez-Vicent, Marta, Chetty, Kritika, Xu-Bayford, Jinhua, O’Toole, Grainne, Fernandes, Augustine, Kuo, Caroline Y., De Oliveira, Satiro N., Mesa-Núñez, Cristina, Moore, Theodore B., Nicoletti, Eileen, Choi, Grace, Zeini, Miriam, Thrasher, Adrian J., Bueren, Juan, Schwartz, Jonathan, Kohn, Donald B.
Published in Transplantation and cellular therapy (01.02.2023)
Published in Transplantation and cellular therapy (01.02.2023)
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Journal Article
Case report: Novel treatment regimen for enterovirus encephalitis in SCID
Chetty, Kritika, Cheng, Iek, Kaliakatsos, Marios, Gonzalez-Granado, Luis Ignacio, Klapsa, Dimitra, Martin, Javier, Bamford, Alasdair, Breuer, Judith, Booth, Claire
Published in Frontiers in immunology (01.01.2022)
Published in Frontiers in immunology (01.01.2022)
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