Eprenetapopt Plus Azacitidine in TP53 -Mutated Myelodysplastic Syndromes and Acute Myeloid Leukemia: A Phase II Study by the Groupe Francophone des Myélodysplasies (GFM)
Cluzeau, Thomas, Sebert, Marie, Rahmé, Ramy, Cuzzubbo, Stefania, Lehmann-Che, Jacqueline, Madelaine, Isabelle, Peterlin, Pierre, Bève, Blandine, Attalah, Habiba, Chermat, Fatiha, Miekoutima, Elsa, Rauzy, Odile Beyne, Recher, Christian, Stamatoullas, Aspasia, Willems, Lise, Raffoux, Emmanuel, Berthon, Céline, Quesnel, Bruno, Loschi, Michael, Carpentier, Antoine F, Sallman, David A, Komrokji, Rami, Walter-Petrich, Anouk, Chevret, Sylvie, Ades, Lionel, Fenaux, Pierre
Published in Journal of clinical oncology (10.05.2021)
Published in Journal of clinical oncology (10.05.2021)
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Journal Article
Single agent talacotuzumab demonstrates limited efficacy but considerable toxicity in elderly high-risk MDS or AML patients failing hypomethylating agents
Kubasch, Anne Sophie, Schulze, Freya, Giagounidis, Aristoteles, Götze, Katharina S., Krönke, Jan, Sockel, Katja, Middeke, Jan Moritz, Chermat, Fatiha, Gloaguen, Silke, Puttrich, Martin, Weigt, Carmen, William, Doreen, Fenaux, Pierre, Schlenk, Richard F., Thiede, Christian, Stasik, Sebastian, Mies, Anna, Adès, Lionel, Oelschlägel, Uta, Platzbecker, Uwe
Published in Leukemia (01.04.2020)
Published in Leukemia (01.04.2020)
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A phase II study of guadecitabine in higher-risk myelodysplastic syndrome and low blast count acute myeloid leukemia after azacitidine failure
Sébert, Marie, Renneville, Aline, Bally, Cécile, Peterlin, Pierre, Beyne-Rauzy, Odile, Legros, Laurence, Gourin, Marie-Pierre, Sanhes, Laurence, Wattel, Eric, Gyan, Emmanuel, Park, Sophie, Stamatoullas, Aspasia, Banos, Anne, Laribi, Kamel, Jueliger, Simone, Bevan, Luke, Chermat, Fatiha, Sapena, Rosa, Nibourel, Olivier, Chaffaut, Cendrine, Chevret, Sylvie, Preudhomme, Claude, Adès, Lionel, Fenaux, Pierre
Published in Haematologica (Roma) (01.08.2019)
Published in Haematologica (Roma) (01.08.2019)
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Characteristics and outcome of patients with low-/intermediate-risk acute promyelocytic leukemia treated with arsenic trioxide: an international collaborative study
Kayser, Sabine, Schlenk, Richard F, Lebon, Delphine, Carre, Martin, Götze, Katharina S, Stölzel, Friedrich, Berceanu, Ana, Schäfer-Eckart, Kerstin, Peterlin, Pierre, Hicheri, Yosr, Rahme, Ramy, Raffoux, Emmanuel, Chermat, Fatiha, Krause, Stefan W, Aulitzky, Walter E, Rigaudeau, Sophie, Noppeney, Richard, Berthon, Celine, Görner, Martin, Jost, Edgar, Carassou, Philippe, Keller, Ulrich, Orvain, Corentin, Braun, Thorsten, Saillard, Colombe, Arar, Ali, Kunzmann, Volker, Wemeau, Mathieu, De Wit, Maike, Niemann, Dirk, Bonmati, Caroline, Schwänen, Carsten, Abraham, Julie, Aljijakli, Ahmad, Haiat, Stephanie, Krämer, Alwin, Reichle, Albrecht, Gnadler, Martina, Willekens, Christophe, Spiekermann, Karsten, Hiddemann, Wolfgang, Müller-Tidow, Carsten, Thiede, Christian, Röllig, Christoph, Serve, Hubert, Bornhäuser, Martin, Baldus, Claudia D, Lengfelder, Eva, Fenaux, Pierre, Platzbecker, Uwe, Adès, Lionel
Published in Haematologica (Roma) (01.12.2021)
Published in Haematologica (Roma) (01.12.2021)
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Journal Article
Acadesine Circumvents Azacitidine Resistance in Myelodysplastic Syndrome and Acute Myeloid Leukemia
Cluzeau, Thomas, Furstoss, Nathan, Savy, Coline, El Manaa, Wejdane, Zerhouni, Marwa, Blot, Lauriane, Calleja, Anne, Dufies, Maeva, Dubois, Alix, Ginet, Clemence, Mounier, Nicolas, Garnier, Georges, Raynaud, Sophie, Rohrlich, Pierre Simon, Peterlin, Pierre, Stamatoullas, Aspasia, Chermat, Fatiha, Fenaux, Pierre, Jacquel, Arnaud, Robert, Guillaume, Auberger, Patrick
Published in International journal of molecular sciences (25.12.2019)
Published in International journal of molecular sciences (25.12.2019)
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Journal Article
Designing a single-arm phase 2 clinical trial of mitapivat for adult patients with erythrocyte membranopathies (SATISFY): a framework for interventional trials in rare anaemias – pilot study protocol
Glenthøj, Andreas, van Beers, Eduard J, van Wijk, Richard, Rab, Minke A E, Groot, Evelyn, Vejlstrup, Niels, Toft, Nina, Bendtsen, Selma Kofoed, Petersen, Jesper, Helby, Jens, Chermat, Fatiha, Fenaux, Pierre, Kuo, Kevin H M
Published in BMJ open (30.07.2024)
Published in BMJ open (30.07.2024)
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Journal Article
A randomized phase II trial of azacitidine +/- epoetin-β in lower-risk myelodysplastic syndromes resistant to erythropoietic stimulating agents
Thépot, Sylvain, Ben Abdelali, Raouf, Chevret, Sylvie, Renneville, Aline, Beyne-Rauzy, Odile, Prébet, Thomas, Park, Sophie, Stamatoullas, Aspasia, Guerci-Bresler, Agnes, Cheze, Stéphane, Tertian, Gérard, Choufi, Bachra, Legros, Laurence, Bastié, Jean Noel, Delaunay, Jacques, Chaury, Marie Pierre, Sanhes, Laurence, Wattel, Eric, Dreyfus, Francois, Vey, Norbert, Chermat, Fatiha, Preudhomme, Claude, Fenaux, Pierre, Gardin, Claude
Published in Haematologica (Roma) (01.08.2016)
Published in Haematologica (Roma) (01.08.2016)
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Journal Article
Phase I/II Clinical Trial Evaluating Azacitidine + Venetoclax + Donor Lymphocyte Infusion in Post-Transplant Relapse Myelodysplastic Syndromes and Acute Myeloid Leukemia: Preliminary Results of Ventograft, a GFM Study
Cluzeau, Thomas, Sebert, Marie, Loschi, Michael, Ades, Lionel, Thepot, Sylvain, Carre, Martin, Duployez, Nicolas, Sapena, Rosa, Chermat, Fatiha, Preudhomme, Claude, Fenaux, Pierre, Robin, Marie
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Journal Article
MDS/CMML from resource‐limited region: Characteristics and comparison to tertiary reference European center
Sevoyan, Anna, Mekinian, Arsène, Chermat, Fatiha, Adès, Lionel, Ivanyan, A., Fenaux, Pierre, Hakobyan, Yervand
Published in European journal of haematology (01.02.2024)
Published in European journal of haematology (01.02.2024)
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Journal Article
A Phase II prospective trial of azacitidine in steroid-dependent or refractory systemic autoimmune/inflammatory disorders and VEXAS syndrome associated with MDS and CMML
Mekinian, Arsene, Zhao, Lin Pierre, Chevret, Sylvie, Desseaux, Kristell, Pascal, Laurent, Comont, Thibaut, Maria, Alexandre, Peterlin, Pierre, Terriou, Louis, D’Aveni Piney, Maud, Gourin, Marie-Pierre, Vey, Norbert, Rauzy, Odile Beyne, Grobost, Vincent, Bezanahary, Holy, Dimicoli-Salazar, Sophie, Banos, Anne, Wickenhauser, Stefan, De Renzis, Benoit, Durot, Eric, Natarajan-Amé, Shanti, Voillat, Laurent, Chermat, Fatiha, Lemaire, Karine, Jachiet, Vincent, Himberlin, Chantal, Thépot, Sylvain, Diaz, Jose Miguel Torregrosa, Frenzel, Laurent, Gyan, Emmanuel, Denis, Guillaume, Hirsch, Pierre, Kosmider, Olivier, Ades, Lionel, Fain, Olivier, Fenaux, Pierre
Published in Leukemia (01.11.2022)
Published in Leukemia (01.11.2022)
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Journal Article
Safety and Efficacy of Mitapivat in Adult Patients with Erythrocyte Membranopathies (SATISFY)
Glenthoej, Andreas, Van Beers, Eduard J., van Wijk, Richard, Rab, Minke A.E., Groot, Evelyn, Vejlstrup, Niels G, Bendtsen, Selma K, Toft, Nina, Petersen, Jesper, Helby, Jens, Chermat, Fatiha, Fenaux, Pierre, Kuo, Kevin H.M.
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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A Phase II Study of Single Agent Aspacytarabine (BST-236) in Adults Unfit for Intensive Chemotherapy with Relapsed or Refractory Acute Myeloid Leukemia (R/R AML) or Higher Risk Myelodysplastic Syndromes (R/R HR MDS)
Hospital, Marie Anne, Cluzeau, Thomas, Garnier, Alice, Marconi, Giovanni, Tavernier, Emmanuelle, Thepot, Sylvain, Stamatoullas, Aspasia, Papayannidis, Cristina, Park, Sophie, Bigot, Noemie, AIT SI Selmi, Lamya, Chermat, Fatiha, Chevret, Sylvie, Fenaux, Pierre
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Journal Article
Eltrombopag in chronic myelomonocytic leukemia with severe thrombocytopenia. A Groupe Francophone des Myélodysplasies (GFM) study
Rabian, Florence, Chevret, Sylvie, Gruson, Bérengère, Thépot, Sylvain, Walter-Petrich, Anouk, Braun, Thorsten, Vey, Norbert, Torregrosa-Diaz, José Miguel, Peterlin, Pierre, Toma, Andrea, D’Aveni, Maud, Delaunay, Jacques, Legros, Laurence, Droin, Nathalie, Chermat, Fatiha, Lusina, Daniel, Adès, Lionel, Sapena, Rosa, Solary, Eric, Fenaux, Pierre, Itzykson, Raphael
Published in Leukemia (12.09.2024)
Published in Leukemia (12.09.2024)
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Journal Article
Clinical impact of genetic alterations including germline DDX41 mutations in MDS/low-blast count AML patients treated with azacitidine-based regimens
Sébert, Marie, Freiman, Lucie, Chaffaut, Cendrine, Guerci, Agnès, Peterlin, Pierre, Thépot, Sylvain, Beyne-Rauzy, Odile, Park, Sophie, Cluzeau, Thomas, Chermat, Fatiha, Fenaux, Pierre, Preudhomme, Claude, Clappier, Emmanuelle, Chevret, Sylvie, Adès, Lionel, Duployez, Nicolas, Duchmann, Matthieu
Published in Leukemia (01.04.2024)
Published in Leukemia (01.04.2024)
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Journal Article
FLT3 Ligand Kinetic Profile Predicts Response to Treatment and Event-Free Survival (EFS) in Adults with High-Risk MDS/CMML Receiving CPX-351: A GFM Study
Peterlin, Pierre, Gaschet, Joëlle, Turlure, Pascal, Gourin, Marie-Pierre, Dumas, Pierre-Yves, Thepot, Sylvain, Berceanu, Ana, Park, Sophie, Hospital, Marie Anne, Cluzeau, Thomas, Torregrosa-Diaz, Jose-Miguel, Drevon, Louis, Sapena, Rosa, Chermat, Fatiha, Dimicoli-Salazar, Sophie, Jullien, Maxime, Fenaux, Pierre, Chevallier, Patrice
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Journal Article
Impact of Arsenic Trioxide in the Treatment of Higher Risk Acute Promyelocytic Leukemia
Da Rocha, Audrey, Cassinat, Bruno, Heiblig, Mael, Recher, Christian, Bertoli, Sarah, Bonmati, Caroline, Roth-Guepin, Gabrielle, Zilliox, Anne, Laloi, Marie, Hunault, Mathilde, Berthon, Céline, Duployez, Nicolas, Willekens, Christophe, Gallego Hernanz, Maria Pilar, Ochmann, Marlene, Cluzeau, Thomas, Chermat, Fatiha, Caulier, Alexis, Raffoux, Emmanuel, Fenaux, Pierre, Marolleau, Jean Pierre, Ades, Lionel, Lebon, Delphine
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Journal Article
Efficacy and Safety of Luspatercept +/- Erythropoiesis-Stimulating Agent (ESA) in Patients with Myelodysplastic Syndromes with Ring Sideroblasts (MDS-RS): A French Multicenter Prospective Real-Life Registry
Comont, Thibault, D'Aveni, Maud, Schenone, Laurence, Torregrosa-Díaz, Jose Miguel, Aguinaga, Lorea, Pardo, Juan, Sebert, Marie, Visanica, Sorin, Santana, Clemence, Le Clech, Lenaig, Stamatoullas, Aspasia, Thepot, Sylvain, Daguindau, Etienne, Beziat, Guillaume, Botin, Teresa, Dimicoli, Sophie, Park, Sophie, Paubelle, Etienne, Slama, Bohrane, Willems, Lise, Debarri, Houria, Gyan, Emmanuel, Calmettes, Claire, Rauzy, Odile, Chermat, Fatiha, Fontenay, Michaela, Ades, Lionel, Fenaux, Pierre
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Journal Article
Decitabine Versus Hydroxyurea for Advanced Proliferative Chronic Myelomonocytic Leukemia: Results of a Randomized Phase III Trial Within the EMSCO Network
Itzykson, Raphael, Santini, Valeria, Thepot, Sylvain, Ades, Lionel, Chaffaut, Cendrine, Giagounidis, Aristoteles, Morabito, Margot, Droin, Nathalie, Lübbert, Michael, Sapena, Rosa, Nimubona, Stanislas, Goasguen, Jean, Wattel, Eric, Zini, Gina, Torregrosa Diaz, Jose Miguel, Germing, Ulrich, Pelizzari, Anna Maria, Park, Sophie, Jaekel, Nadja, Metzgeroth, Georgia, Onida, Francesco, Navarro, Robert, Patriarca, Andrea, Stamatoullas, Aspasia, Götze, Katharina, Puttrich, Martin, Mossuto, Sandra, Solary, Eric, Gloaguen, Silke, Chevret, Sylvie, Chermat, Fatiha, Platzbecker, Uwe, Fenaux, Pierre
Published in Journal of clinical oncology (01.04.2023)
Published in Journal of clinical oncology (01.04.2023)
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Journal Article
Dynamics of Mortality and Transformation Risk within Different Risk Groups of Patients with Myelodysplastic Syndromes Stratified According to the IPSS-R - Comparison of Treated and Untreated Patients and Consequences for the Description of Risk Categories
Pfeilstocker, Michael, Tuechler, Heinz, Ades, Lionel, Cermak, Jaroslav, Chermat, Fatiha, Della Porta, Matteo G., Fenaux, Pierre, Garcia-Manero, Guillermo, Germing, Ulrich, Haase, Detlef, Kuendgen, Andrea, Luebbert, Michael, Magalhaes, Silvia Maria Meira, Malcovati, Luca, Miyazaki, Yasushi, Sanz, Guillermo, Santini, Valeria, Sekeres, Mikkael A., Walter, Matthew J, Valent, Peter, Greenberg, Peter L
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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Journal Article
Molecular Response Analysis By High Throughput Sequencing in Higher Risk Myelodysplastic Syndrome (HR-MDS) Treated Intensively with CPX-351
Le Bris, Yannick, Bouzy, Simon, Ménard, Audrey, Turlure, Pascal, Chevallier, Patrice, Gourin, Marie-Pierre, Dumas, Pierre-Yves, Thepot, Sylvain, Berceanu, Anna, Park, Sophie, Hospital, Marie-Anne, Cluzeau, Thomas, Torregrosa Diaz, Jose-Miguel, Devron, Louis, Sapena, Rosa, Chermat, Fatiha, Dimicoli Salazar, Sophie, Béné, Marie C, Fenaux, Pierre, Peterlin, Pierre
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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