The next generation of CRISPR–Cas technologies and applications
Pickar-Oliver, Adrian, Gersbach, Charles A.
Published in Nature reviews. Molecular cell biology (01.08.2019)
Published in Nature reviews. Molecular cell biology (01.08.2019)
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Journal Article
ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering
Gaj, Thomas, Gersbach, Charles A, Barbas, Carlos F
Published in Trends in biotechnology (Regular ed.) (01.07.2013)
Published in Trends in biotechnology (Regular ed.) (01.07.2013)
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Journal Article
Highly specific epigenome editing by CRISPR-Cas9 repressors for silencing of distal regulatory elements
Thakore, Pratiksha I, D'Ippolito, Anthony M, Song, Lingyun, Safi, Alexias, Shivakumar, Nishkala K, Kabadi, Ami M, Reddy, Timothy E, Crawford, Gregory E, Gersbach, Charles A
Published in Nature methods (01.12.2015)
Published in Nature methods (01.12.2015)
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Journal Article
In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy
Nelson, Christopher E., Hakim, Chady H., Ousterout, David G., Thakore, Pratiksha I., Moreb, Eirik A., Rivera, Ruth M. Castellanos, Madhavan, Sarina, Pan, Xiufang, Ran, F. Ann, Yan, Winston X., Asokan, Aravind, Zhang, Feng, Duan, Dongsheng, Gersbach, Charles A.
Published in Science (American Association for the Advancement of Science) (22.01.2016)
Published in Science (American Association for the Advancement of Science) (22.01.2016)
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Journal Article
RNA-guided transcriptional silencing in vivo with S. aureus CRISPR-Cas9 repressors
Thakore, Pratiksha I., Kwon, Jennifer B., Nelson, Christopher E., Rouse, Douglas C., Gemberling, Matthew P., Oliver, Matthew L., Gersbach, Charles A.
Published in Nature communications (26.04.2018)
Published in Nature communications (26.04.2018)
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Journal Article
Targeted Epigenetic Remodeling of Endogenous Loci by CRISPR/Cas9-Based Transcriptional Activators Directly Converts Fibroblasts to Neuronal Cells
Black, Joshua B., Adler, Andrew F., Wang, Hong-Gang, D’Ippolito, Anthony M., Hutchinson, Hunter A., Reddy, Timothy E., Pitt, Geoffrey S., Leong, Kam W., Gersbach, Charles A.
Published in Cell stem cell (01.09.2016)
Published in Cell stem cell (01.09.2016)
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Journal Article
Engineering Delivery Vehicles for Genome Editing
Nelson, Christopher E, Gersbach, Charles A
Published in Annual review of chemical and biomolecular engineering (07.06.2016)
Published in Annual review of chemical and biomolecular engineering (07.06.2016)
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Journal Article
Loss-of-function genetic tools for animal models: cross-species and cross-platform differences
Housden, Benjamin E., Muhar, Matthias, Gemberling, Matthew, Gersbach, Charles A., Stainier, Didier Y. R., Seydoux, Geraldine, Mohr, Stephanie E., Zuber, Johannes, Perrimon, Norbert
Published in Nature reviews. Genetics (01.01.2017)
Published in Nature reviews. Genetics (01.01.2017)
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Journal Article
A CRISPR/Cas9-Based System for Reprogramming Cell Lineage Specification
Chakraborty, Syandan, Ji, HaYeun, Kabadi, Ami M., Gersbach, Charles A., Christoforou, Nicolas, Leong, Kam W.
Published in Stem cell reports (09.12.2014)
Published in Stem cell reports (09.12.2014)
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Journal Article
Step‐Wise Chondrogenesis of Human Induced Pluripotent Stem Cells and Purification Via a Reporter Allele Generated by CRISPR‐Cas9 Genome Editing
Adkar, Shaunak S., Wu, Chia‐Lung, Willard, Vincent P., Dicks, Amanda, Ettyreddy, Adarsh, Steward, Nancy, Bhutani, Nidhi, Gersbach, Charles A., Guilak, Farshid
Published in Stem cells (Dayton, Ohio) (01.01.2019)
Published in Stem cells (Dayton, Ohio) (01.01.2019)
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Journal Article
Cas9-specific immune responses compromise local and systemic AAV CRISPR therapy in multiple dystrophic canine models
Hakim, Chady H., Kumar, Sandeep R. P., Pérez-López, Dennis O., Wasala, Nalinda B., Zhang, Dong, Yue, Yongping, Teixeira, James, Pan, Xiufang, Zhang, Keqing, Million, Emily D., Nelson, Christopher E., Metzger, Samantha, Han, Jin, Louderman, Jacqueline A., Schmidt, Florian, Feng, Feng, Grimm, Dirk, Smith, Bruce F., Yao, Gang, Yang, N. Nora, Gersbach, Charles A., Chen, Shi-jie, Herzog, Roland W., Duan, Dongsheng
Published in Nature communications (24.11.2021)
Published in Nature communications (24.11.2021)
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Journal Article
Synergistic and tunable human gene activation by combinations of synthetic transcription factors
Perez-Pinera, Pablo, Ousterout, David G, Brunger, Jonathan M, Farin, Alicia M, Glass, Katherine A, Guilak, Farshid, Crawford, Gregory E, Hartemink, Alexander J, Gersbach, Charles A
Published in Nature methods (01.03.2013)
Published in Nature methods (01.03.2013)
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Journal Article
Regulation of chromatin accessibility and Zic binding at enhancers in the developing cerebellum
Frank, Christopher L, Liu, Fang, Wijayatunge, Ranjula, Song, Lingyun, Biegler, Matthew T, Yang, Marty G, Vockley, Christopher M, Safi, Alexias, Gersbach, Charles A, Crawford, Gregory E, West, Anne E
Published in Nature neuroscience (01.05.2015)
Published in Nature neuroscience (01.05.2015)
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Journal Article
Structure and specificity of the RNA-guided endonuclease Cas9 during DNA interrogation, target binding and cleavage
Josephs, Eric A, Kocak, D Dewran, Fitzgibbon, Christopher J, McMenemy, Joshua, Gersbach, Charles A, Marszalek, Piotr E
Published in Nucleic acids research (15.10.2015)
Published in Nucleic acids research (15.10.2015)
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Journal Article
How vinculin regulates force transmission
Dumbauld, David W., Lee, Ted T., Singh, Ankur, Scrimgeour, Jan, Gersbach, Charles A., Zamir, Evan A., Fu, Jianping, Chen, Christopher S., Curtis, Jennifer E., Craig, Susan W., García, Andrés J.
Published in Proceedings of the National Academy of Sciences - PNAS (11.06.2013)
Published in Proceedings of the National Academy of Sciences - PNAS (11.06.2013)
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Journal Article
Branched-chain α-ketoacids are preferentially reaminated and activate protein synthesis in the heart
Walejko, Jacquelyn M., Christopher, Bridgette A., Crown, Scott B., Zhang, Guo-Fang, Pickar-Oliver, Adrian, Yoneshiro, Takeshi, Foster, Matthew W., Page, Stephani, van Vliet, Stephan, Ilkayeva, Olga, Muehlbauer, Michael J., Carson, Matthew W., Brozinick, Joseph T., Hammond, Craig D., Gimeno, Ruth E., Moseley, M. Arthur, Kajimura, Shingo, Gersbach, Charles A., Newgard, Christopher B., White, Phillip J., McGarrah, Robert W.
Published in Nature communications (15.03.2021)
Published in Nature communications (15.03.2021)
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