Gene Therapy Using a Self-Inactivating Lentiviral Vector Improves Clinical and Laboratory Manifestations of Wiskott-Aldrich Syndrome
Chu, Julia I, Henderson, Lauren A, Armant, Myriam, Male, Frances, Dansereau, Colleen H, MacKinnon, Brenda, Burke, Christopher J, Cavanaugh, Matthew E, London, Wendy B., Barlan, Isil B, Özen, Ahmet, Baris, Safa, Karakoc-Aydiner, Elif, Kiykim, Ayça, Hanson, Imelda Celine, Despotovic, Jenny M., Saitoh, Akihiko, Takachi, Takayuki, Imai, Kohsuke, King, Alejandra, Arredondo, Silvia, Ritz, Jerome, Bushman, Frederic D, Galy, Anne, Notarangelo, Luigi Daniele, Williams, David A., Pai, Sung-Yun
Published in Blood (03.12.2015)
Published in Blood (03.12.2015)
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