Selection-free precise gene repair using high-capacity adenovector delivery of advanced prime editing systems rescues dystrophin synthesis in DMD muscle cells
Wang, Qian, Capelletti, Sabrina, Liu, Jin, Janssen, Josephine M, Gonçalves, Manuel A F V
Published in Nucleic acids research (21.03.2024)
Published in Nucleic acids research (21.03.2024)
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