Randomized, blinded trial of weekend vs daily prednisone in Duchenne muscular dystrophy
Escolar, D M, Hache, L P, Clemens, P R, Cnaan, A, McDonald, C M, Viswanathan, V, Kornberg, A J, Bertorini, T E, Nevo, Y, Lotze, T, Pestronk, A, Ryan, M M, Monasterio, E, Day, J W, Zimmerman, A, Arrieta, A, Henricson, E, Mayhew, J, Florence, J, Hu, F, Connolly, A M
Published in Neurology (02.08.2011)
Published in Neurology (02.08.2011)
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Clinical evaluator reliability for quantitative and manual muscle testing measures of strength in children
Escolar, D. M., Henricson, E. K., Mayhew, J., Florence, J., Leshner, R., Patel, K. M., Clemens, P. R.
Published in Muscle & nerve (01.06.2001)
Published in Muscle & nerve (01.06.2001)
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Journal Article
Improvement of the mdx mouse dystrophic phenotype by systemic in utero AAV8 delivery of a minidystrophin gene
KOPPANATI, B. M, LI, J, REAY, D. P, WANG, B, DAOOD, M, ZHENG, H, XIAO, X, WATCHKO, J. F, CLEMENS, P. R
Published in Gene therapy (01.11.2010)
Published in Gene therapy (01.11.2010)
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Journal Article
Full-length dystrophin gene transfer to the mdx mouse in utero
REAY, D. P, BILBAO, R, KOPPANATI, B. M, CAI, L, O'DAY, T. L, JIANG, Z, ZHENG, H, WATCHKO, J. F, CLEMENS, P. R
Published in Gene therapy (01.04.2008)
Published in Gene therapy (01.04.2008)
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Journal Article
Effects of irradiating adult mdx mice before full-length dystrophin cDNA transfer on host anti-dystrophin immunity
EGHTESAD, S, ZHENG, H, NAKAI, H, EPPERLY, M. W, CLEMENS, P. R
Published in Gene therapy (01.09.2010)
Published in Gene therapy (01.09.2010)
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Journal Article
Pentoxifylline as a rescue treatment for DMD: a randomized double-blind clinical trial
Escolar, D M, Zimmerman, A, Bertorini, T, Clemens, P R, Connolly, A M, Mesa, L, Gorni, K, Kornberg, A, Kolski, H, Kuntz, N, Nevo, Y, Tesi-Rocha, C, Nagaraju, K, Rayavarapu, S, Hache, L P, Mayhew, J E, Florence, J, Hu, F, Arrieta, A, Henricson, E, Leshner, R T, Mah, J K
Published in Neurology (20.03.2012)
Published in Neurology (20.03.2012)
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A New Adenoviral Vector: Replacement of All Viral Coding Sequences with 28 kb of DNA Independently Expressing Both Full-Length Dystrophin and β -Galactosidase
Kochanek, Stefan, Clemens, Paula R., Mitani, Kohnosuke, Chen, Hsiao-Huei, Chan, Suzanne, Caskey, C. Thomas
Published in Proceedings of the National Academy of Sciences - PNAS (11.06.1996)
Published in Proceedings of the National Academy of Sciences - PNAS (11.06.1996)
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Journal Article
In vivo muscle gene transfer of full-length dystrophin with an adenoviral vector that lacks all viral genes
Clemens, P R, Kochanek, S, Sunada, Y, Chan, S, Chen, H H, Campbell, K P, Caskey, C T
Published in Gene therapy (01.11.1996)
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Published in Gene therapy (01.11.1996)
Journal Article
CTLA4Ig delivered by high-capacity adenoviral vector induces stable expression of dystrophin in mdx mouse muscle
JIANG, Z, SCHIEDNER, G, GILCHRIST, S. C, KOCHANEK, S, CLEMENS, P. R
Published in Gene therapy (01.10.2004)
Published in Gene therapy (01.10.2004)
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Journal Article
Comparison of high-capacity and first-generation adenoviral vector gene delivery to murine muscle in utero
BILBAO, R, REAY, D. P, WU, E, ZHENG, H, BIERMANN, V, KOCHANEK, S, CLEMENS, P. R
Published in Gene therapy (01.01.2005)
Published in Gene therapy (01.01.2005)
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Journal Article
Fetal muscle gene transfer is not enhanced by an RGD capsid modification to high-capacity adenoviral vectors
BILBAO, R, REAY, D. P, HUGHES, T, BIERMANN, V, VOLPERS, C, GOLDBERG, L, BERGELSON, J, KOCHANEK, S, CLEMENS, P. R
Published in Gene therapy (01.10.2003)
Published in Gene therapy (01.10.2003)
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Journal Article
Carrier detection and prenatal diagnosis in Duchenne and Becker muscular dystrophy families, using dinucleotide repeat polymorphisms
CLEMENS, P. R, FENWICK, R. G, CHAMBERLAIN, J. S, GIBBS, R. A, DE ANDRADE, M, CHAKRABORTY, R, CASKEY, C. T
Published in American journal of human genetics (01.11.1991)
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Published in American journal of human genetics (01.11.1991)
Journal Article
Ex vivo gene transfer using adenovirus-mediated full-length dystrophin delivery to dystrophic muscles
FLOYD, S. S, CLEMENS, P. R, FEERO, G. W, EPPERLY, M, HUARD, J, ONTELL, M. R, KOCHANEK, S, DAY, C. S, YANG, J, HAUSCHKA, S. D, BALKIR, L, MORGAN, J, MORELAND, M. S
Published in Gene therapy (1998)
Published in Gene therapy (1998)
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Journal Article
Inhibition of the IKK/NF-[kappa]B pathway by AAV gene transfer improves muscle regeneration in older mdx mice
Tang, Y, Reay, D P, Salay, M N, Mi, M Y, Clemens, P R, Guttridge, D C, Robbins, P D, Huard, J, Wang, B
Published in Gene therapy (01.12.2010)
Published in Gene therapy (01.12.2010)
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Journal Article
Viral gene delivery to skeletal muscle: insights on maturation-dependent loss of fiber infectivity for adenovirus and herpes simplex type 1 viral vectors
Feero, W G, Rosenblatt, J D, Huard, J, Watkins, S C, Epperly, M, Clemens, P R, Kochanek, S, Glorioso, J C, Partridge, T A, Hoffman, E P
Published in Human gene therapy (01.03.1997)
Published in Human gene therapy (01.03.1997)
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Inhibition of the IKK/NF-κB pathway by AAV gene transfer improves muscle regeneration in older mdx mice
Tang, Y, Reay, D P, Salay, M N, Mi, M Y, Clemens, P R, Guttridge, D C, Robbins, P D, Huard, J, Wang, B
Published in Gene therapy (01.12.2010)
Published in Gene therapy (01.12.2010)
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Journal Article
Polylysine modification of adenoviral fiber protein enhances muscle cell transduction
Bouri, K, Feero, W G, Myerburg, M M, Wickham, T J, Kovesdi, I, Hoffman, E P, Clemens, P R
Published in Human gene therapy (01.07.1999)
Published in Human gene therapy (01.07.1999)
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Journal Article
Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management
Bushby, Katharine, MD, Finkel, Richard, MD, Birnkrant, David J, MD, Case, Laura E, DPT, Clemens, Paula R, MD, Cripe, Linda, MD, Kaul, Ajay, MD, Kinnett, Kathi, MSN, McDonald, Craig, MD, Pandya, Shree, PT, Poysky, James, PhD, Shapiro, Frederic, MD, Tomezsko, Jean, PhD, Constantin, Carolyn, PhD
Published in Lancet neurology (2010)
Published in Lancet neurology (2010)
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Journal Article
Pentanucleotide repeat length polymorphism at the human CD4 locus
EDWARDS, M. C, CLEMENS, P. R, TRISTAN, M, PIZZUTI, A, GIBBS, R. A
Published in Nucleic acids research (11.09.1991)
Published in Nucleic acids research (11.09.1991)
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