Evaluation of the safety, tolerability and pharmacokinetics of ALN-RSV01, a novel RNAi antiviral therapeutic directed against respiratory syncytial virus (RSV)
DeVincenzo, John, Cehelsky, Jeffrey E., Alvarez, Rene, Elbashir, Sayda, Harborth, Jens, Toudjarska, Iva, Nechev, Lubomir, Murugaiah, Veeravagu, Vliet, Andre Van, Vaishnaw, Akshay K., Meyers, Rachel
Published in Antiviral research (01.03.2008)
Published in Antiviral research (01.03.2008)
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Phase II trial of intravenous lobradimil and carboplatin in childhood brain tumors : a report from the Children's Oncology Group
WARREN, K, JAKACKI, R, OSBORNE, C, CEHELSKY, J, CALDWELL, D, STANWOOD, J, STEINBERG, S. M, BALIS, F. M, WIDEMANN, B, AIKIN, A, LIBUCHA, M, PACKER, R, VEZINA, G, REAMAN, G, SHAW, D, KRAILO, M
Published in Cancer chemotherapy and pharmacology (01.09.2006)
Published in Cancer chemotherapy and pharmacology (01.09.2006)
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Burden of Illness for Patients with familial amyloidotic Polyneuropathy (Fap) Begins Early and Increases with Disease Progression
Denoncourt, R.N, Adams, D, Coelho, T, Bettencourt, B.R, Plaisted, A, Amitay, O, Falzone, R, Harrop, J, White, L, De Frutos, R, Cehelsky, J, Nochur, S, Vaishnaw, A.K, Gollob, J
Published in Value in health (01.05.2015)
Published in Value in health (01.05.2015)
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41: Results of a Randomized Phase 2 Trial of ALN-RSV01, an RNAi Therapeutic, Lung Transplant (LTX) Patients Infected with Respiratory Syncytial Virus (RSV)
Zamora, M.R, Budev, M, Rolfe, M, Gottlieb, J, DeVincenzo, J, Cehelsky, J, Albert, G, Gollob, J, Nochur, S, Vaishnaw, A, Glanville, A
Published in The Journal of heart and lung transplantation (01.02.2010)
Published in The Journal of heart and lung transplantation (01.02.2010)
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Development of a Human Experimental Infection Model of Respiratory Syncytial Virus (RSV) and Evaluation of an RNA Interference (RNAi) Therapeutic for Safety and Anti-Viral Efficacy in Man
DeVincenzo, J, Lambkin-Williams, R, Cehelsky, J, Wilkinson, T, Obute, O, Foote, K, Nochur, S, Gilberts, A, Mann, A, Moane, E, Walsh, E, Studholme, B, Dorset, P, Oxford, J, Meyers, R, Vaishnaw, A
Published in Journal of allergy and clinical immunology (01.02.2008)
Published in Journal of allergy and clinical immunology (01.02.2008)
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PND52 - Burden of Illness for Patients with familial amyloidotic Polyneuropathy (Fap) Begins Early and Increases with Disease Progression
Denoncourt, R.N., Adams, D., Coelho, T., Bettencourt, B.R., Plaisted, A., Amitay, O., Falzone, R., Harrop, J., White, L., De Frutos, R., Cehelsky, J., Nochur, S., Vaishnaw, A.K., Gollob, J.
Published in Value in health (01.05.2015)
Published in Value in health (01.05.2015)
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Phase 2 open-label extension study (ole) of patisiran, an investigational sIRNA investigational agent for familial amyloid polyneuropathy (fap)
Coelho, T., Suhr, Ole, Conceicao, I, Waddington-Cruz, M., Schmidt, H., Buades, J., Campistol, J., Pouget, J., Berk, J., Falzone, R., White, L., Bettencourt, B., Cehelsky, J., Nochur, S., Vaishnaw, A., Gollob, J., Adams, D.
Published in Journal of the peripheral nervous system (2015)
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Published in Journal of the peripheral nervous system (2015)
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Interim safety and pharmacodynamic results for ALN-VSP02, a novel RNAi therapeutic for solid tumors with liver involvement
Gollob, J., Infante, J. R., Shapiro, G., LoRusso, P., Dezube, B. J., Heymach, J., Cehelsky, J., Falzone, R., Vaishnaw, A., Burris, H. A.
Published in Journal of clinical oncology (20.05.2010)
Published in Journal of clinical oncology (20.05.2010)
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Phase I dose-escalation study of ALN-VSP02, a novel RNAi therapeutic for solid tumors with liver involvement
Cervantes, A., Alsina, M., Tabernero, J., Infante, J. R., LoRusso, P., Shapiro, G., Paz-Ares, L. G., Falzone, R., Hill, J., Cehelsky, J., White, A., Toudjarska, I., Bumcrot, D., Meyers, R., Hinkle, G., Svrzikapa, N., Sah, D. W., Vaishnaw, A., Gollob, J., Burris, H. A.
Published in Journal of clinical oncology (20.05.2011)
Published in Journal of clinical oncology (20.05.2011)
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Interim results from phase ii trial of aln-ttr02, a novel RNAi therapeutic for the treatment of familial amyloidotic polyneuropathy
Adams, D., Coelho, T., Suhr, Ole, Conceicao, I., Waddington-Cruz, M., Schmidt, H., Campistol, J., Pouget, J., Buades, J., Falzone, R., Harrop, J., De Frutos, R., Butler, J., Cehelsky, J., Nochur, S., Vaishnaw, A., Gollob, J.
Published in Journal of the peripheral nervous system (2013)
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Published in Journal of the peripheral nervous system (2013)
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Abstracts7th Annual Meeting of the Oligonucleotide Therapeutics SocietyCopenhagen, DenmarkSeptember 8–10, 2011
Aartsma-Rus, Annemieke, Karnaoek, Tatyana, I, Bestel, Leatherbury, Neil, SA, Schwabe, J, Hunziker, Rockey, William M, Spencer, David M, Giangrande, Paloma H, Tavitian, Bertrand, Kjems, Jørgen, Bolcato-Bellemin, Anne-Laure, Deglane, Gaëlle, Goldeck, M., Schuberth, C., van Kessel, Ingeborg, Hartmann, Roland K., Hall, Jonathan, Gait, Michael J, Hornung, Veit, Hartmann, Gunther, Schlee, Martin, MW, Lindholm, Veedu, Rakesh N., Harbottle, R., Kazakov, S. A., NarayanannairJayaprakash, K., Wang, Gang, Sah, Dinah W.Y., Manoharan, Muthiah, Nielsen, Niels Fisker, Kauppinen, Sakari, Elmén, Joacim, Fettes, Kevin, Sobczak, Milena, Kim, Hee Won, Svrzikapa, Nenad, Qin, June, Tracy, Mark A., Makita, Naoki, Nagahara, Shunji, Stockdale, Katie R., Hanin, Geula, Gilboa-Geffen, Adi, Soreq, Hermona, McClorey, Graham, Shibata, Atsushi, Kummer, Ursula, Nawrot, Barbara, Snead, Nicholas M., Kamiya, D., Matsui, Yuriko, Tran, Phong Lan Thao, Rayner, Bernard, Urban, Johannes, Phua, Kyle Kok Loong, Harada-Shiba, Mariko, Obika, Satoshi, Agapkina, J., Aouadi, Myriam, Guo, Chang-An, Byun, Jonghoe, Tula, Saison-Behmoaras, Galun, Eithan, M, Yamamoto, Iversen, Patrick, Kim, Sera, Komoriya, Akira, Nagatsugi, Fumi, Kusano, Shuhei, Mohri, Kohta, Bernhard, Noll, Philipp, Hadwiger, Shrewsbury, Stephen, Takahashi, Mayumi, Matsuda, Akira, Sah, D.W., Gantier, Michael P., Sczakiel, Georg, C., Coch, B., Kümmerer, S., Herberhold, G., Kochs, M., Schlee, Trujillo, Robin Deis, Edbrooke, Mark, Fitzgerald-Bocarsly, Patricia, Gibson, Neil W., Bhat, Balkrishen, Chen, Hubert, Jackson, Aimee L., A, Buchbinder, Hawkins, Philip, Cehelsky, Jeff, Gollob, Jared, Moore, Michael D., Chomchan, Pritsana, Hua, Yimin, Sahashi, Kentaro, Aarts, Marieke
Published in Nucleic acid therapeutics (01.10.2011)
Published in Nucleic acid therapeutics (01.10.2011)
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