Safety, tolerability, and preliminary efficacy of an IGF-1 mimetic in patients with spinal and bulbar muscular atrophy: a randomised, placebo-controlled trial
Grunseich, Christopher, Miller, Ram, Swan, Therese, Glass, David J, El Mouelhi, Mohamed, Fornaro, Mara, Petricoul, Olivier, Vostiar, Igor, Roubenoff, Ronenn, Meriggioli, Matthew N, Kokkinis, Angela, Guber, Robert D, Budron, Maher S, Vissing, John, Soraru, Gianni, Mozaffar, Tahseen, Ludolph, Albert, Kissel, John T, Fischbeck, Kenneth H, Grunseich, Christopher, Miller, Ram, Swan, Therese, Glass, David J, Mouelhi, Mohamed El, Fornaro, Mara, Petricoul, Olivier, Vostiar, Igor, Roubenoff, Ronenn, Meriggioli, Matthew N, Dahlqvist, Julia, Witting, Nanna, Vissing, John, Martinelli, Ilaria, Querin, Giorgia, Soraru, Gianni, Goyal, Namita A, Cash, Tiyonnoh M, Minton, Brian, Mozaffar, Tahseen, Rosenbohm, Angela, Weiland, Ulrike, Weydt, Patrick, Ludolph, Albert, Chelnick, Sharon, Iyadurai, Stanley, King, Wendy, Kissel, John T, Budron, Maher S, Guber, Robert D, Kokkinis, Angela, Fischbeck, Kenneth H
Published in Lancet neurology (01.12.2018)
Published in Lancet neurology (01.12.2018)
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Nucleocytoplasmic transport defect in a North American patient with ALS8
Guber, Robert D., Schindler, Alice B., Budron, Maher S., Chen, Ke‐lian, Li, Yuebing, Fischbeck, Kenneth H., Grunseich, Christopher
Published in Annals of clinical and translational neurology (01.03.2018)
Published in Annals of clinical and translational neurology (01.03.2018)
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Journal Article
Nucleocytoplasmic transport defect in a North American patient with ALS 8
Guber, Robert D., Schindler, Alice B., Budron, Maher S., Chen, Ke‐lian, Li, Yuebing, Fischbeck, Kenneth H., Grunseich, Christopher
Published in Annals of clinical and translational neurology (01.03.2018)
Published in Annals of clinical and translational neurology (01.03.2018)
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Journal Article
A randomized, placebo-controlled study to evaluate the safety, tolerability, and preliminary efficacy of an IGF-1 mimetic in patients with spinal and bulbar muscular atrophy
Grunseich, Christopher, Miller, Ram, Swan, Therese, Glass, David J, El Mouelhi, Mohamed, Fornaro, Mara, Petricoul, Olivier, Vostiar, Igor, Roubenoff, Ronenn, Meriggioli, Matthew N, Kokkinis, Angela, Guber, Robert D, Budron, Maher S, Vissing, John, Soraru, Gianni, Mozaffar, Tahseen, Ludolph, Albert, Kissel, John T, Fischbeck, Kenneth H
Published in Lancet neurology (15.10.2018)
Published in Lancet neurology (15.10.2018)
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A Comprehensive Enumeration of the Human Proteostasis Network. 2. Components of the Autophagy-Lysosome Pathway
Elsasser, Suzanne, Elia, Lisa P, Morimoto, Richard I, Powers, Evan T, Finley, Daniel, Costa, Beatrice, Budron, Maher, Tokuno, Zachary, Wang, Shijie, Iyer, Rajshri G, Barth, Bianca, Mockler, Eric, Finkbeiner, Steve, Gestwicki, Jason E, Richardson, Reese A K, Stoeger, Thomas, Tan, Ee Phie, Xiao, Qiang, Cole, Christian M, Massey, Lynée A, Garza, Dan, Kelly, Jeffery W, Rainbolt, T Kelly, Chou, Ching-Chieh, Masto, Vincent B, Frydman, Judith, Nixon, Ralph A
Published in bioRxiv (24.03.2023)
Published in bioRxiv (24.03.2023)
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