Mapping the COPD Assessment Test onto EQ-5D
Hoyle, Christopher K., PhD, Tabberer, Margaret, MSc, Brooks, Jean, MSc
Published in Value in health (01.06.2016)
Published in Value in health (01.06.2016)
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Journal Article
P037: Design of a multi-center randomized phase 3 clinical trial (HURCULES) evaluating OTL-203 in MPS-IH vs allogeneic hematopoietic stem cell transplantation
Harmatz, Paul, Wynn, Robert, Gupta, Ashish, Kharbanda, Sandhya, Lindemans, Caroline, Ahrens-Nicklas, Rebecca, van Hasselt, Peter, Lund, Troy, Olson, Timothy, Tucci, Francesca, Martin, Leonie, Boeglin, Nathalie, Brooks, Jean, Syonmez, Su, Campbell, Laura, Jones, Simon, Orchard, Paul, Bernardo, Maria Ester
Published in Genetics in Medicine Open (2024)
Published in Genetics in Medicine Open (2024)
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P005: Atidarsagene autotemcel (hematopoietic stem cell–gene therapy) preserves cognitive and motor development in metachromatic leukodystrophy with up to 12 years follow-up
Fumagalli, Francesca, Calbi, Valeria, De Mattia, Fabiola, Zambon, Alberto, Gallo, Vera, Recupero, Salvatore, Fratini, Elena Sophia, Ippolito, Alessia, Ciotti, Francesca, Fraschini, Maddalena, Sarzana, Marina, Scarparo, Stefano, Montini, Eugenio, Locatelli, Sara, Facchini, Marcella, Clerici, Alessandra, Morena, Francesco, Martino, Sabata, Yarzi, Muska, Moro, Sean, Shenker, Andrew, Brooks, Jean, Richardson, Alan, Meltzer, Leslie, Campbell, Laura, Aiuti, Alessandro
Published in Genetics in Medicine Open (2024)
Published in Genetics in Medicine Open (2024)
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Journal Article
Shortness of Breath with Daily Activities questionnaire: validation and responder thresholds in patients with chronic obstructive pulmonary disease
Watkins, Michael L, Wilcox, Teresa K, Tabberer, Maggie, Brooks, Jean M, Donohue, James F, Anzueto, Antonio, Chen, Wen-Hung, Crim, Courtney
Published in BMJ open (22.10.2013)
Published in BMJ open (22.10.2013)
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Journal Article
Once-Daily Single-Inhaler Triple versus Dual Therapy in Patients with COPD
Lipson, David A, Barnhart, Frank, Brealey, Noushin, Brooks, Jean, Criner, Gerard J, Day, Nicola C, Dransfield, Mark T, Halpin, David M.G, Han, MeiLan K, Jones, C. Elaine, Kilbride, Sally, Lange, Peter, Lomas, David A, Martinez, Fernando J, Singh, Dave, Tabberer, Maggie, Wise, Robert A, Pascoe, Steven J
Published in The New England journal of medicine (03.05.2018)
Published in The New England journal of medicine (03.05.2018)
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Safety and tolerability of once-daily umeclidinium/vilanterol 125/25 mcg and umeclidinium 125 mcg in patients with chronic obstructive pulmonary disease: results from a 52-week, randomized, double-blind, placebo-controlled study
Donohue, James F, Niewoehner, Dennis, Brooks, Jean, O'Dell, Dianne, Church, Alison
Published in Respiratory research (11.07.2014)
Published in Respiratory research (11.07.2014)
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Journal Article
Efficacy and Safety of Umeclidinium Added to Fluticasone Propionate/Salmeterol in Patients with COPD: Results of Two Randomized, Double-Blind Studies
Siler, Thomas M., Kerwin, Edward, Singletary, Karen, Brooks, Jean, Church, Alison
Published in Chronic obstructive pulmonary disease (02.01.2016)
Published in Chronic obstructive pulmonary disease (02.01.2016)
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Journal Article
A meta-analysis of four randomized clinical trials to confirm the reliability and responsiveness of the Shortness of Breath with Daily Activities (SOBDA) questionnaire in chronic obstructive pulmonary disease
Tabberer, Maggie, Brooks, Jean, Wilcox, Teresa
Published in Health and quality of life outcomes (31.10.2015)
Published in Health and quality of life outcomes (31.10.2015)
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Journal Article
Lentiviral hematopoietic stem cell gene therapy (atidarsagene autotemcel) for late juvenile metachromatic leukodystrophy (MLD)
Gallo, Vera, Calbi, Valeria, De Mattia, Fabiola, Zambon, Alberto Andrea, Recupero, Salvatore, Fratini, Elena Sophia, Ciotti, Francesca, Fraschini, Maddalena, Sangalli, Mara, Sarzana, Marina, Clerici, Alessandra, Morena, Francesco, Martino, Sabata, Brooks, Jean, Richardson, Alan, Campbell, Laura, Aiuti, Alessandro, Fumagalli, Francesca
Published in Molecular genetics and metabolism (01.02.2024)
Published in Molecular genetics and metabolism (01.02.2024)
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Journal Article
Design of a multi-center randomized active controlled phase 3 clinical trial (HURCULES) evaluating the safety and efficacy of OTL-203 in patients with MPS IH versus standard of care with allogeneic hematopoietic stem cell transplantation
Orchard, Paul J., Wynn, Robert F., Kharbanda, Sandhya, Ahrens-Nicklas, Rebecca, van Hasselt, Peter M., Lund, Troy C., Olson, Timothy S., Tucci, Francesca, Martin, Leonie, Boeglin, Nathalie, Brooks, Jean, Syonmez, Su, Campbell, Laura, Harmatz, Paul, Jones, Simon A., Gupta, Ashish O., Bernardo, Maria Ester
Published in Molecular genetics and metabolism (01.02.2024)
Published in Molecular genetics and metabolism (01.02.2024)
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Journal Article
Atidarsagene autotemcel (autologous hematopoietic stem cell gene therapy) preserves cognitive and motor development in early-onset metachromatic leukodystrophy with up to 12 years follow-up
Fumagalli, Francesca, Calbi, Valeria, De Mattia, Fabiola, Zambon, Alberto Andrea, Gallo, Vera, Recupero, Salvatore, Fratini, Elena Sophia, Ippolito, Alessia, Ciotti, Francesca, Fraschini, Maddalena, Sarzana, Marina, Scarparo, Stefano, Montini, Eugenio, Locatelli, Sara, Facchini, Marcella, Clerici, Alessandra, Morena, Francesco, Martino, Sabata, Yarzi, Muska, Moro, Sean, Shenker, Andrew, Brooks, Jean, Richardson, Alan, Campbell, Laura, Aiuti, Alessandro
Published in Molecular genetics and metabolism (01.02.2024)
Published in Molecular genetics and metabolism (01.02.2024)
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Journal Article
Long-term clinical outcomes of atidarsagene autotemcel (autologous hematopoietic stem cell gene therapy [HSC-GT] for metachromatic leukodystrophy) with up to 11 years follow-up
Fumagalli, Francesca, Calbi, Valeria, De Mattia, Fabiola, Zambon, Alberto A., Gallo, Vera, Recupero, Salvatore, Baldoli, Cristina, Fratini, Elena Sophia, Ciotti, Francesca, Fraschini, Maddalena, Sarzana, Marina, Scarparo, Stefano, Calabria, Andrea, Montini, Eugenio, Locatelli, Sara, Facchini, Marcella, Clerici, Alessandra, Morena, Francesco, Martino, Sabata, Claros, Angelica, Kaviya, Arpeat, Moro, Sean, Brooks, Jean, Richardson, Alan, Aiuti, Alessandro
Published in Molecular genetics and metabolism (01.02.2023)
Published in Molecular genetics and metabolism (01.02.2023)
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Journal Article
Effect of coexisting vascular disease on long-term risk of recurrent events after TIA or stroke
Boulanger, Marion, Li, Linxin, Lyons, Shane, Lovett, Nicola G, Kubiak, Magdalena M, Silver, Louise, Touzé, Emmanuel, Rothwell, Peter M
Published in Neurology (13.08.2019)
Published in Neurology (13.08.2019)
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