A master protocol to investigate a novel therapy acetyl-L-leucine for three ultra-rare neurodegenerative diseases: Niemann-Pick type C, the GM2 gangliosidoses, and ataxia telangiectasia
Fields, T, Patterson, M, Bremova-Ertl, T, Belcher, G, Billington, I, Churchill, G C, Davis, W, Evans, W, Flint, S, Galione, A, Granzer, U, Greenfield, J, Karl, R, Kay, R, Lewi, D, Mathieson, T, Meyer, T, Pangonis, D, Platt, F M, Tsang, L, Verburg, C, Factor, M, Strupp, M
Published in Current controlled trials in cardiovascular medicine (22.01.2021)
Published in Current controlled trials in cardiovascular medicine (22.01.2021)
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The neurological update: therapies for cerebellar ataxias in 2020
Gandini, J., Manto, Mario, Bremova-Ertl, T., Feil, K., Strupp, M.
Published in Journal of neurology (01.04.2020)
Published in Journal of neurology (01.04.2020)
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Journal Article