Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott-Aldrich syndrome
Magnani, A, Semeraro, M, Adam, F, Booth, C, Dupré, L, Morris, E C, Gabrion, A, Roudaut, C, Borgel, D, Toubert, A, Clave, E, Abdo, C, Gorochov, G, Petermann, R, Guiot, M, Miyara, M, Moshous, D, Magrin, E, Denis, A, Suarez, F, Lagresle, C, Roche, A M, Everett, J, Trinquand, A, Guisset, M, Bayford, J Xu, Hacein-Bey-Abina, S, Kauskot, A, Elfeky, R, Rivat, C, Abbas, S, Gaspar, H B, Macintyre, E, Picard, C, Bushman, F D, Galy, A, Fischer, A, Six, E, Thrasher, A J, Cavazzana, M
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Author Correction: Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott–Aldrich syndrome
Magnani, A., Semeraro, M., Adam, F., Booth, C., Dupré, L., Morris, E. C., Gabrion, A., Roudaut, C., Borgel, D., Toubert, A., Clave, E., Abdo, C., Gorochov, G., Petermann, R., Guiot, M., Miyara, M., Moshous, D., Magrin, E., Denis, A., Suarez, F., Lagresle, C., Roche, A. M., Everett, J., Trinquand, A., Guisset, M., Bayford, J. Xu, Hacein-Bey-Abina, S., Kauskot, A., Elfeky, R., Rivat, C., Abbas, S., Gaspar, H. B., Macintyre, E., Picard, C., Bushman, F. D., Galy, A., Fischer, A., Six, E., Thrasher, A. J., Cavazzana, M.
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Real-time PCR-based assay to quantify the relative amount of human and mouse tissue present in tumor xenografts
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Gross deletions/duplications in PROS1 are relatively common in point mutation-negative hereditary protein S deficiency
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Therapeutic vulnerability of an in vivo model of alveolar soft part sarcoma (ASPS) to antiangiogenic therapy
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Novel human pathological mutations. Gene symbol: PROS1. Disease: Protein S deficiency
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The protein S thrombin‐sensitive region modulates phospholipid binding and the γ‐carboxyglutamic acid‐rich (Gla) domain conformation in a non‐specific manner
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Published in Cancer research (Chicago, Ill.) (01.06.2003)
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Molecular bases of type II protein S deficiency: the I203‐D204 deletion in the EGF4 domain alters GLA domain function
BARONI, M., MAZZOLA, G., KAABACHE, T., BORGEL, D., GANDRILLE, S., D'ANGELO, S. VIGANO', MARCHETTI, G., DI IASIO, M. G., PINOTTI, M., D'ANGELO, A., BERNARDI, F.
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Protein C and protein S deficiencies
Aiach, M, Borgel, D, Gaussem, P, Emmerich, J, Alhenc-Gelas, M, Gandrille, S
Published in Seminars in hematology (01.07.1997)
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Published in Seminars in hematology (01.07.1997)
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A potential role for imaging technology in anticancer efficacy evaluations
Hollingshead, M.G., Bonomi, C.A., Borgel, S.D., Carter, J.P., Shoemaker, R., Melillo, G., Sausville, E.A.
Published in European journal of cancer (1990) (01.04.2004)
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Identification of 15 Different Candidate Causal Point Mutations and Three Polymorphisms in 19 Patients With Protein S Deficiency Using a Scanning Method for the Analysis of the Protein S Active Gene
Gandrille, S., Borgel, D., Eschwege-Gufflet, V., Aillaud, Mf, Dreyfus, M., Matheron, C., Gaussem, P., Abgrall, J.F., Jude, B., Sie, P., Toulon, P., Aiach, M.
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Implication of protein S thrombin-sensitive region with membrane binding via conformational changes in the gamma-carboxyglutamic acid-rich domain
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