Therapeutic base editing of human hematopoietic stem cells
Zeng, Jing, Wu, Yuxuan, Ren, Chunyan, Bonanno, Jasmine, Shen, Anne H, Shea, Devlin, Gehrke, Jason M, Clement, Kendell, Luk, Kevin, Yao, Qiuming, Kim, Rachel, Wolfe, Scot A, Manis, John P, Pinello, Luca, Joung, J Keith, Bauer, Daniel E
Published in Nature medicine (01.04.2020)
Published in Nature medicine (01.04.2020)
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Journal Article
BCL11A enhancer-edited hematopoietic stem cells persist in rhesus monkeys without toxicity
Demirci, Selami, Zeng, Jing, Wu, Yuxuan, Uchida, Naoya, Shen, Anne H, Pellin, Danilo, Gamer, Jackson, Yapundich, Morgan, Drysdale, Claire, Bonanno, Jasmine, Bonifacino, Aylin C, Krouse, Allen E, Linde, Nathaniel S, Engels, Theresa, Donahue, Robert E, Haro-Mora, Juan J, Leonard, Alexis, Nassehi, Tina, Luk, Kevin, Porter, Shaina N, Lazzarotto, Cicera R, Tsai, Shengdar Q, Weiss, Mitchell J, Pruett-Miller, Shondra M, Wolfe, Scot A, Bauer, Daniel E, Tisdale, John F
Published in The Journal of clinical investigation (01.12.2020)
Published in The Journal of clinical investigation (01.12.2020)
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Journal Article
Therapeutic Base Editing of Human Hematopoietic Stem Cells
Zeng, Jing, Wu, Yuxuan, Ren, Chunyan, Bonanno, Jasmine, Shen, Anne H., Shea, Devlin, Gehrke, Jason M, Manis, John P, Gehrke, J. Keith, Bauer, Daniel E.
Published in Blood (13.11.2019)
Published in Blood (13.11.2019)
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Journal Article
유전자 편집을 위한 내부 링커를 포함하는 변형된 가이드 RNA
ALEXANDER SETH C, MULEPATI SABIN, YOUNG MICHELLE, BONANNO JASMINE JOSEPHINE, PARMAR RUBINA GIARE, STRETZ LINDSEY JEAN
Year of Publication 08.03.2024
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Year of Publication 08.03.2024
Patent
BCL11A enhancer-edited hematopoietic stem cells persist in rhesus monkeys without toxicity
Demirci, Selami, Zeng, Jing, Wu, Yuxuan, Uchida, Naoya, Shen, Anne H, Pellin, Danilo, Gamer, Jackson, Yapundich, Morgan, Drysdale, Claire, Bonanno, Jasmine, Bonifacino, Aylin C, Krouse, Allen E, Linde, Nathaniel S, Engels, Theresa, Donahue, Robert E, Haro-Mora, Juan J, Leonard, Alexis, Nassehi, Tina, Luk, Kevin, Porter, Shaina N, Lazzarotto, Cicera R, Tsai, Shengdar Q, Weiss, Mitchell J, Pruett-Miller, Shondra M, Wolfe, Scot A, Bauer, Daniel E, Tisdale, John F
Published in The Journal of clinical investigation (01.12.2020)
Published in The Journal of clinical investigation (01.12.2020)
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Journal Article
Modified Guide RNAs Comprising an Internal Linker for Gene Editing
Alexander, Seth C, Stretz, Lindsey Jean, Mulepati, Sabin, Parmar, Rubina Giare, Young, Michelle, Bonanno, Jasmine Josephine
Year of Publication 09.05.2024
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Year of Publication 09.05.2024
Patent
MODIFIED GUIDE RNAS COMPRISING AN INTERNAL LINKER FOR GENE EDITING
PARMAR, Rubina Giare, STRETZ, Lindsey Jean, MULEPATI, Sabin, BONANNO, Jasmine Josephine, ALEXANDER, Seth C, YOUNG, Michelle
Year of Publication 17.04.2024
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Year of Publication 17.04.2024
Patent
MODIFIED GUIDE RNAS COMPRISING AN INTERNAL LINKER FOR GENE EDITING
PARMAR, Rubina Giare, STRETZ, Lindsey Jean, MULEPATI, Sabin, BONANNO, Jasmine Josephine, ALEXANDER, Seth C, YOUNG, Michelle
Year of Publication 21.12.2023
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Year of Publication 21.12.2023
Patent
MODIFIED GUIDE RNAS COMPRISING AN INTERNAL LINKER FOR GENE EDITING
YOUNG, MICHELLE, MULEPATI, SABIN, ALEXANDER, SETH C, BONANNO, JASMINE JOSEPHINE, PARMAR, RUBINA GIARE, STRETZ, LINDSEY JEAN
Year of Publication 15.12.2022
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Year of Publication 15.12.2022
Patent
MODIFIED GUIDE RNAS COMPRISING AN INTERNAL LINKER FOR GENE EDITING
PARMAR, Rubina Giare, STRETZ, Lindsey Jean, MULEPATI, Sabin, BONANNO, Jasmine Josephine, YOUNG, Michelle
Year of Publication 15.12.2022
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Year of Publication 15.12.2022
Patent
MODIFIED GUIDE RNAS COMPRISING AN INTERNAL LINKER FOR GENE EDITING
STRETZ Lindsey Jean, BONANNO Jasmine Josephine, PARMAR Rubina Giare, MULEPATI Sabin, ALEXANDER Seth C, YOUNG Michelle
Year of Publication 05.03.2024
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Year of Publication 05.03.2024
Patent
Modified guide RNAs comprising an internal linker for gene editing
YOUNG, MICHELLE, MULEPATI, SABIN, BONANNO, JASMINE JOSEPHINE, PARMAR, RUBINA GIARE, STRETZ, LINDSEY JEAN
Year of Publication 01.05.2023
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Year of Publication 01.05.2023
Patent