The Wiskott-Aldrich Syndrome and X-Linked Congenital Thrombocytopenia Are Caused by Mutations of the Same Gene
Zhu, Qili, Zhang, Min, Blaese, R. Michael, Derry, Jonathan M.J., Junker, Anne, Francke, Uta, Chen, Shi-Han, Ochs, Hans D.
Published in Blood (15.11.1995)
Published in Blood (15.11.1995)
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In situ delivery of suicide genes for cancer treatment
Blaese, R.M., Ishii-Morita, H., Mullen, C., Ramsey, J., Ram, Z., Oldfield, E., Culver, K.
Published in European journal of cancer (1990) (1994)
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AV.TK-mediated killing of subcutaneous tumors in situ results in effective immunization against established secondary intracranial tumor deposits
OKADA, T, SHAH, M, HIGGINBOTHAM, J. N, LI, Q, WILDNER, O, WALBRIDGE, S, OLDFIELD, E, BLAESE, R. M, RAMSEV, W. T
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Published in Gene therapy (01.09.2001)
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Persistence and expression of the adenosine deaminase gene for 12 years and immune reaction to gene transfer components: long-term results of the first clinical gene therapy trial
Muul, Linda Mesler, Tuschong, Laura M., Soenen, Sherry Lau, Jagadeesh, G. Jayashree, Ramsey, W. Jay, Long, Zhifeng, Carter, Charles S., Garabedian, Elizabeth K., Alleyne, Melinna, Brown, Margaret, Bernstein, Wendy, Schurman, Shepherd H., Fleisher, Thomas A., Leitman, Susan F., Dunbar, Cynthia E., Blaese, R. Michael, Candotti, Fabio
Published in Blood (01.04.2003)
Published in Blood (01.04.2003)
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Retroviral-Mediated Gene Correction for X-Linked Severe Combined Immunodeficiency
Candotti, Fabio, Johnston, James A., Puck, Jennifer M., Sugamura, Kazuo, O'Shea, John J., Blaese, R.Michael
Published in Blood (15.04.1996)
Published in Blood (15.04.1996)
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Therapy of malignant brain tumors by intratumoral implantation of retroviral vector-producing cells
Ram, Z, Culver, K W, Oshiro, E M, Viola, J J, DeVroom, H L, Otto, E, Long, Z, Chiang, Y, McGarrity, G J, Muul, L M, Katz, D, Blaese, R M, Oldfield, E H
Published in Nature medicine (01.12.1997)
Published in Nature medicine (01.12.1997)
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T Lymphocyte-Directed Gene Therapy for ADA$^-$ SCID: Initial Trial Results After 4 Years
Blaese, R. Michael, Culver, Kenneth W., Miller, A. Dusty, Carter, Charles S., Fleisher, Thomas, Clerici, Mario, Shearer, Gene, Chang, Lauren, Chiang, Yawen, Tolstoshev, Paul, Greenblatt, Jay J., Rosenberg, Steven A., Klein, Harvey, Berger, Melvin, Mullen, Craig A., Ramsey, W. Jay, Muul, Linda, Morgan, Richard A., Anderson, W. French
Published in Science (American Association for the Advancement of Science) (20.10.1995)
Published in Science (American Association for the Advancement of Science) (20.10.1995)
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A multiinstitutional survey of the Wiskott-Aldrich syndrome
Sullivan, Kathleen E., Mullen, Craig A., Blaese, R.Michael, Winkelstein, Jerry A.
Published in The Journal of pediatrics (01.12.1994)
Published in The Journal of pediatrics (01.12.1994)
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Long-term in vivo survival of receptor-modified syngeneic T cells in patients with human immunodeficiency virus infection
WALKER, R. E, BECHTEL, C. M, LEITMAN, S. F, PALENSKY, J, WITTES, J, DAVEY, R. T, FALLOON, J, POLIS, M. A, KOVACS, J. A, BROAD, D. F, LEVINE, B. L, ROBERTS, M. R, NATARAJAN, V, MASUR, H, LANE, H. C, BASELER, M, HEGE, K. M, METCALF, J. A, STEVENS, R, HAZEN, A, BLAESE, R. M, CHEN, C. C
Published in Blood (15.07.2000)
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Published in Blood (15.07.2000)
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In Vivo Gene Transfer with Retroviral Vector-Producer Cells for Treatment of Experimental Brain Tumors
Culver, Kenneth W., Ram, Zvi, Wallbridge, Stuart, Ishii, Hiroyuki, Oldfield, Edward H., Blaese, R. Michael
Published in Science (American Association for the Advancement of Science) (12.06.1992)
Published in Science (American Association for the Advancement of Science) (12.06.1992)
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T lymphocytes with a normal ADA gene accumulate after transplantation of transduced autologous umbilical cord blood CD34+ cells in ADA-deficient SCID neonates
Kohn, D B, Hershfield, M S, Carbonaro, D, Shigeoka, A, Brooks, J, Smogorzewska, E M, Barsky, L W, Chan, R, Burotto, F, Annett, G, Nolta, J A, Crooks, G, Kapoor, N, Elder, M, Wara, D, Bowen, T, Madsen, E, Snyder, F F, Bastian, J, Muul, L, Blaese, R M, Weinberg, K, Parkman, R
Published in Nature medicine (01.07.1998)
Published in Nature medicine (01.07.1998)
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Wiskott-Aldrich Syndrome/X-Linked Thrombocytopenia: WASP Gene Mutations, Protein Expression, and Phenotype
Zhu, Qili, Watanabe, Chiaki, Liu, Ting, Hollenbaugh, Diane, Blaese, R. Michael, Kanner, Steven B., Aruffo, Alejandro, Ochs, Hans D.
Published in Blood (01.10.1997)
Published in Blood (01.10.1997)
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Preferential survival of CD4+ T lymphocytes engineered with anti-human immunodeficiency virus (HIV) genes in HIV-infected individuals
Morgan, Richard A, Walker, Robert, Carter, Charles S, Natarajan, Ven, Tavel, Jorge A, Bechtel, Chris, Herpin, Betsy, Muul, Linda, Zheng, Zhili, Jagannatha, Shyla, Bunnell, Bruce A, Fellowes, Vicki, Metcalf, Julia A, Stevens, Randy, Baseler, Michael, Leitman, Susan F, Read, Elizabeth J, Blaese, R Michael, Lane, H Clifford
Published in Human gene therapy (01.09.2005)
Published in Human gene therapy (01.09.2005)
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Engraftment of gene-modified umbilical cord blood cells in neonates with adenosine deaminase deficiency
Kohn, D B, Weinberg, K I, Nolta, J A, Heiss, L N, Lenarsky, C, Crooks, G M, Hanley, M E, Annett, G, Brooks, J S, el-Khoureiy, A
Published in Nature medicine (01.10.1995)
Published in Nature medicine (01.10.1995)
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