Oral cysteamine bitartrate and N-acetylcysteine for patients with infantile neuronal ceroid lipofuscinosis: a pilot study
Levin, Sondra W, MD, Baker, Eva H, PhD, Zein, Wadih M, MD, Zhang, Zhongjian, MD, Quezado, Zenaide M N, MD, Miao, Ning, MD, Gropman, Andrea, MD, Griffin, Kurt J, MD, Bianconi, Simona, MD, Chandra, Goutam, PhD, Khan, Omar I, MD, Caruso, Rafael C, MD, Liu, Aiyi, PhD, Mukherjee, Anil B, Dr
Published in Lancet neurology (01.08.2014)
Published in Lancet neurology (01.08.2014)
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