Long‐term effects of ivacaftor on nonpulmonary outcomes in individuals with cystic fibrosis, heterozygous for a S1251N mutation
Burghard, M (Marcella), Berkers, G (Gitte), Ghijsen, S (Sophie), Hollander‐Kraaijeveld, FM (Francis), Winter‐de Groot, KM (Karin), Ent, CK (Kors), Heijerman, HGM (Harry), Takken, T (Tim), Hulzebos, HJ (Erik)
Published in Pediatric pulmonology (01.06.2020)
Published in Pediatric pulmonology (01.06.2020)
Get full text
Journal Article
FDA-approved drug screening in patient-derived organoids demonstrates potential of drug repurposing for rare cystic fibrosis genotypes
de Poel, E., Spelier, S., Hagemeijer, M.C., van Mourik, P., Suen, S.W.F., Vonk, A.M., Brunsveld, J.E., Ithakisiou, G.N., Kruisselbrink, E., Oppelaar, H., Berkers, G., de Winter de Groot, K.M., Heida-Michel, S., Jans, S.R., van Panhuis, H., Bakker, M., van der Meer, R., Roukema, J., Dompeling, E., Weersink, E.J.M., Koppelman, G.H., Blaazer, A.R., Muijlwijk-Koezen, J.E., van der Ent, C.K., Beekman, J.M.
Published in Journal of cystic fibrosis (01.05.2023)
Published in Journal of cystic fibrosis (01.05.2023)
Get full text
Journal Article
WS12.4 The predictive value of oral glucose tolerance for the development of CFRD in CF children: a longitudinal study
van Oirschot-van de Ven, M.M.M, Kiviet, A.C. de, Berkers, G, Witmond, J.M, Arets, H.G.M, Ent, C.K. van der
Published in Journal of cystic fibrosis (01.06.2016)
Published in Journal of cystic fibrosis (01.06.2016)
Get full text
Journal Article
29 Validating the organoid model across European laboratories
van Mourik, P, Berkers, G, Vonk, A.M, Ramalho, A.S, Awatade, N.T, van der Ent, C.K, de Boeck, K, Amaral, M.D, Beekman, J.M
Published in Journal of cystic fibrosis (01.06.2017)
Published in Journal of cystic fibrosis (01.06.2017)
Get full text
Journal Article
WS18.2 The rainbow project: personalised medicine for CF-patients with rare mutations
van Mourik, P, Berkers, G, Vonk, A.M, de Poel, E, Hagemeijer, M.C, Majoor, C.J, Heijerman, H.G.M, Koppelman, G.H, Roukema, J, Bannier, M.A.G.E, Janssens, H.M, Beekman, J.M, van der Ent, C.K
Published in Journal of cystic fibrosis (01.06.2017)
Published in Journal of cystic fibrosis (01.06.2017)
Get full text
Journal Article
23 Stratifying young children with cystic fibrosis for disease severity using intestinal organoid swelling, intestinal current measurements or sweat chloride concentration as CFTR-dependent biomarker
Groot, K.M. de Winter-de, Janssens, H.M, Uum, R.T. van, Dekkers, J.F, Tiddens, H.A.W.M, Berkers, G, Vonk, A, Kruisselbrink, E, Vries, R.G.J, Clevers, H, Houwen, R.H.J, Escher, J.C, Beekman, J.M, van der Ent, C.K
Published in Journal of cystic fibrosis (01.06.2016)
Published in Journal of cystic fibrosis (01.06.2016)
Get full text
Journal Article
WS18.2 Prospective selection of potential CFTR-modifying treatments using intestinal organoids
Berkers, G, Dekkers, J.F, Kruisselbrink, E, Vonk, A.M, Heida-Michel, S, Geerdink, M, de Winter-de Groot, K.M, Arets, H.G.M, Bronsveld, I, van de Graaf, E.A, Majoor, C.J, Koppelman, G.H, Roukema, J, Janssens, H.M, Heijerman, H.G.M, Vries, R.G.J, Clevers, J.C, Jonge, H. de, Beekman, J.M, van der Ent, C.K
Published in Journal of cystic fibrosis (01.06.2016)
Published in Journal of cystic fibrosis (01.06.2016)
Get full text
Journal Article
24 Stratification for cystic fibrosis (CF) disease severity in adults with CF with homozygous F508del mutations by intestinal organoids
de Winter-de Groot, K.M, van der Meer, R, van der Wilt, R.E.M, Dekkers, J.F, Geerdink, M, Michel, S, Kruisselbrink, E, Vonk, A, Berkers, G, Vries, R.G.J, Clevers, H, van de Graaf, E.A, Vleggaar, F.P, Heijerman, H.G.M, van der Ent, C.K, Beekman, J.M
Published in Journal of cystic fibrosis (01.06.2016)
Published in Journal of cystic fibrosis (01.06.2016)
Get full text
Journal Article
P353 The effects of ivacaftor on resting energy expenditure, exercise capacity, and body composition in patients with cystic fibrosis, heterozygous for a S1251N mutation
Burghard, M., Berkers, G., Ghijsen, S., Hollander-Kraaijeveld, F., Winter-de Groot, K., van der Ent, K., Heijerman, H., Takken, T., Hulzebos, E.
Published in Journal of cystic fibrosis (01.06.2019)
Published in Journal of cystic fibrosis (01.06.2019)
Get full text
Journal Article
665: Forskolin-induced intestinal organoid swelling predicts long-term cystic fibrosis disease progression
Muilwijk, D., de Poel, E., van Mourik, P., Suen, S., Vonk, A., Brunsveld, J., Kruisselbrink, E., Oppelaar, H., Hagemeijer, M., Berkers, G., de Winter-de Groot, K., Michel, S., Jans, S., van Panhuis, H., van der Eerden, M., van der Meer, R., Roukema, J., Dompeling, E., Weersink, E., Koppelman, G., Vries, R., Zomer-van Ommen, D., Eijkemans, R., van der Ent, C., Beekman, J.
Published in Journal of cystic fibrosis (01.11.2021)
Published in Journal of cystic fibrosis (01.11.2021)
Get full text
Journal Article
ePS1.04 In vivo effect of three potentiator treatments found effective in rectal organoids
Berkers, G., van Mourik, P., Vonk, A.M., Kruisselbrink, E., Dekkers, J.F., de Winter - de Groot, K.M., Arets, H.G.M., Heijerman, H., Majoor, C.J., Koppelman, G.H., Roukema, J., Janssens, H.M., van der Meer, R., Vries, R.G.J., de Jonge, H.R., Beekman, J.M., van der Ent, C.K.
Published in Journal of cystic fibrosis (01.06.2019)
Published in Journal of cystic fibrosis (01.06.2019)
Get full text
Journal Article
FDA-Approved Drug Screening in Patient-Derived Organoids Demonstrates Potential of Drug Repurposing for Rare Cystic Fibrosis Genotypes
De Poel, E, Spelier, S, Hagemeijer, Mc, P Van Mourik, Suen, Swf, Vonk, Am, Brunsveld, Je, Ithakisiou, Gn, Kruisselbrink, E, Oppelaar, H, Berkers, G, De Winter-De Groot, Km, Heida-Michel, S, Jans, Sr, H Van Panhuis, Bakker, M, Van Der Meer, R, Roukema, J, Dompeling, E, Weersink, Ejm, Koppelman, Gh, Blaazer, Ar, Je Van Muijlwijk - Koezen, Ck Van Der Ent, Beekman, Jm
Published in bioRxiv (03.09.2022)
Published in bioRxiv (03.09.2022)
Get full text
Paper