Improving clinical trial outcomes in amyotrophic lateral sclerosis
Kiernan, Matthew C, Vucic, Steve, Talbot, Kevin, McDermott, Christopher J, Hardiman, Orla, Shefner, Jeremy M, Al-Chalabi, Ammar, Huynh, William, Cudkowicz, Merit, Talman, Paul, Van den Berg, Leonard H, Dharmadasa, Thanuja, Wicks, Paul, Reilly, Claire, Turner, Martin R
Published in Nature reviews. Neurology (01.02.2021)
Published in Nature reviews. Neurology (01.02.2021)
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Addressing heterogeneity in amyotrophic lateral sclerosis CLINICAL TRIALS
Goyal, Namita A., Berry, James D., Windebank, Anthony, Staff, Nathan P., Maragakis, Nicholas J., Berg, Leonard H., Genge, Angela, Miller, Robert, Baloh, Robert H., Kern, Ralph, Gothelf, Yael, Lebovits, Chaim, Cudkowicz, Merit
Published in Muscle & nerve (01.08.2020)
Published in Muscle & nerve (01.08.2020)
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Microglia innately develop within cerebral organoids
Ormel, Paul R, Vieira de Sá, Renata, van Bodegraven, Emma J, Karst, Henk, Harschnitz, Oliver, Sneeboer, Marjolein A M, Johansen, Lill Eva, van Dijk, Roland E, Scheefhals, Nicky, Berdenis van Berlekom, Amber, Ribes Martínez, Eduardo, Kling, Sandra, MacGillavry, Harold D, van den Berg, Leonard H, Kahn, René S, Hol, Elly M, de Witte, Lot D, Pasterkamp, R Jeroen
Published in Nature communications (09.10.2018)
Published in Nature communications (09.10.2018)
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The genetics and neuropathology of amyotrophic lateral sclerosis
Al-Chalabi, Ammar, Jones, Ashley, Troakes, Claire, King, Andrew, Al-Sarraj, Safa, van den Berg, Leonard H.
Published in Acta neuropathologica (01.09.2012)
Published in Acta neuropathologica (01.09.2012)
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Protein aggregation in amyotrophic lateral sclerosis
Blokhuis, Anna M., Groen, Ewout J. N., Koppers, Max, van den Berg, Leonard H., Pasterkamp, R. Jeroen
Published in Acta neuropathologica (01.06.2013)
Published in Acta neuropathologica (01.06.2013)
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The Beginning of Genomic Therapies for ALS
Hardiman, Orla, van den Berg, Leonard H
Published in The New England journal of medicine (09.07.2020)
Published in The New England journal of medicine (09.07.2020)
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Neural stem cell homeostasis is affected in cortical organoids carrying a mutation in Angiogenin
Ferguson, Ross, Es, Michael A, Berg, Leonard H, Subramanian, Vasanta
Published in The Journal of pathology (01.04.2024)
Published in The Journal of pathology (01.04.2024)
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Dexpramipexole versus placebo for patients with amyotrophic lateral sclerosis (EMPOWER): a randomised, double-blind, phase 3 trial
Cudkowicz, Merit E, Prof, van den Berg, Leonard H, Prof, Shefner, Jeremy M, Prof, Mitsumoto, Hiroshi, Prof, Mora, Jesus S, MD, Ludolph, Albert, Prof, Hardiman, Orla, Prof, Bozik, Michael E, MD, Ingersoll, Evan W, PhD, Archibald, Donald, MPhil, Meyers, Adam L, MS, Dong, Yingwen, PhD, Farwell, Wildon R, MD, Kerr, Douglas A, MD
Published in Lancet neurology (01.11.2013)
Published in Lancet neurology (01.11.2013)
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Mutations in the profilin 1 gene cause familial amyotrophic lateral sclerosis
WU, Chi-Hong, FALLINI, Claudia, KOST, Jason E, GONZALEZ-PEREZ, Paloma, FOX, Andrew D, ADAMS, Jenni, TARONI, Franco, TILOCA, Cinzia, LYN LECLERC, Ashley, CHAFE, Shawn C, MANGROO, Dev, MOORE, Melissa J, TICOZZI, Nicola, ZITZEWITZ, Jill A, XU, Zuo-Shang, DEN BERG, Leonard H. Van, GLASS, Jonathan D, SICILIANO, Gabriele, CIRULLI, Elizabeth T, GOLDSTEIN, David B, SALACHAS, Francois, MEININGER, Vincent, ROSSOLL, Wilfried, KEAGLE, Pamela J, RATTI, Antonia, GELLERA, Cinzia, BOSCO, Daryl A, BASSELL, Gary J, SILANI, Vincenzo, DRORY, Vivian E, BROWN, Robert H, LANDERS, John E, SAPP, Peter C, PIOTROWSKA, Katarzyna, LOWE, Patrick, KOPPERS, Max, MCKENNA-YASEK, Diane, BARON, Desiree M
Published in Nature (London) (23.08.2012)
Published in Nature (London) (23.08.2012)
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Connectome‐Based Propagation Model in Amyotrophic Lateral Sclerosis
Meier, Jil M., Burgh, Hannelore K., Nitert, Abram D., Bede, Peter, Lange, Siemon C., Hardiman, Orla, Berg, Leonard H., Heuvel, Martijn P.
Published in Annals of neurology (01.05.2020)
Published in Annals of neurology (01.05.2020)
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MRI Clustering Reveals Three ALS Subtypes With Unique Neurodegeneration Patterns
Tan, Harold H. G., Westeneng, Henk‐Jan, Nitert, Abram D., Veenhuijzen, Kevin, Meier, Jil M., Burgh, Hannelore K., Zandvoort, Martine J. E., Es, Michael A., Veldink, Jan H., Berg, Leonard H.
Published in Annals of neurology (01.12.2022)
Published in Annals of neurology (01.12.2022)
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Correlation between structural and functional connectivity impairment in amyotrophic lateral sclerosis
Schmidt, Ruben, Verstraete, Esther, de Reus, Marcel A., Veldink, Jan H., van den Berg, Leonard H., van den Heuvel, Martijn P.
Published in Human brain mapping (01.09.2014)
Published in Human brain mapping (01.09.2014)
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Gene discovery in amyotrophic lateral sclerosis: implications for clinical management
Al-Chalabi, Ammar, van den Berg, Leonard H, Veldink, Jan
Published in Nature reviews. Neurology (01.02.2017)
Published in Nature reviews. Neurology (01.02.2017)
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Joint sequencing of human and pathogen genomes reveals the genetics of pneumococcal meningitis
Lees, John A, Ferwerda, Bart, Kremer, Philip H C, Wheeler, Nicole E, Serón, Mercedes Valls, Croucher, Nicholas J, Gladstone, Rebecca A, Bootsma, Hester J, Rots, Nynke Y, Wijmega-Monsuur, Alienke J, Sanders, Elisabeth A M, Trzciński, Krzysztof, Wyllie, Anne L, Zwinderman, Aeilko H, van den Berg, Leonard H, van Rheenen, Wouter, Veldink, Jan H, Harboe, Zitta B, Lundbo, Lene F, de Groot, Lisette C P G M, van Schoor, Natasja M, van der Velde, Nathalie, Ängquist, Lars H, Sørensen, Thorkild I A, Nohr, Ellen A, Mentzer, Alexander J, Mills, Tara C, Knight, Julian C, du Plessis, Mignon, Nzenze, Susan, Weiser, Jeffrey N, Parkhill, Julian, Madhi, Shabir, Benfield, Thomas, von Gottberg, Anne, van der Ende, Arie, Brouwer, Matthijs C, Barrett, Jeffrey C, Bentley, Stephen D, van de Beek, Diederik
Published in Nature communications (15.05.2019)
Published in Nature communications (15.05.2019)
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Hybrid Controlled Clinical Trials Using Concurrent Registries in Amyotrophic Lateral Sclerosis: A Feasibility Study
Eijk, Ruben P. A., Berg, Leonard H., Roes, Kit C. B., Tian, Lu, Lai, Tze L., Nelson, Lorene M., Li, Chenyu, Scowcroft, Anna, Garcia‐Segovia, Jesus, Lu, Ying
Published in Clinical pharmacology and therapeutics (01.10.2023)
Published in Clinical pharmacology and therapeutics (01.10.2023)
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European Academy of Neurology (EAN) guideline on the management of amyotrophic lateral sclerosis in collaboration with European Reference Network for Neuromuscular Diseases (ERN EURO‐NMD)
Van Damme, Philip, Al‐Chalabi, Ammar, Andersen, Peter M., Chiò, Adriano, Couratier, Philippe, De Carvalho, Mamede, Hardiman, Orla, Kuźma‐Kozakiewicz, Magdalena, Ludolph, Albert, McDermott, Christopher J., Mora, Jesus S., Petri, Susanne, Probyn, Katrin, Reviers, Evy, Salachas, François, Silani, Vincenzo, Tysnes, Ole‐Bjørn, Berg, Leonard H., Villanueva, Gemma, Weber, Markus
Published in European journal of neurology (01.06.2024)
Published in European journal of neurology (01.06.2024)
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Dutch population structure across space, time and GWAS design
Byrne, Ross P, van Rheenen, Wouter, van den Berg, Leonard H, Veldink, Jan H, McLaughlin, Russell L
Published in Nature communications (11.09.2020)
Published in Nature communications (11.09.2020)
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