AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington’s Disease Minipig Model
Evers, Melvin M., Miniarikova, Jana, Juhas, Stefan, Vallès, Astrid, Bohuslavova, Bozena, Juhasova, Jana, Skalnikova, Helena Kupcova, Vodicka, Petr, Valekova, Ivona, Brouwers, Cynthia, Blits, Bas, Lubelski, Jacek, Kovarova, Hana, Ellederova, Zdenka, van Deventer, Sander J., Petry, Harald, Motlik, Jan, Konstantinova, Pavlina
Published in Molecular therapy (05.09.2018)
Published in Molecular therapy (05.09.2018)
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Journal Article
Transplantation of BDNF-secreting mesenchymal stem cells provides neuroprotection in chronically hypertensive rat eyes
Harper, Matthew M, Grozdanic, Sinisa D, Blits, Bas, Kuehn, Markus H, Zamzow, Daniel, Buss, Janice E, Kardon, Randy H, Sakaguchi, Donald S
Published in Investigative ophthalmology & visual science (01.06.2011)
Published in Investigative ophthalmology & visual science (01.06.2011)
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Journal Article
Comparison of AAV Serotypes for Gene Delivery to Dorsal Root Ganglion Neurons
Mason, Matthew RJ, Ehlert, Erich ME, Eggers, Ruben, Pool, Chris W, Hermening, Stephan, Huseinovic, Angelina, Timmermans, Eric, Blits, Bas, Verhaagen, Joost
Published in Molecular therapy (01.04.2010)
Published in Molecular therapy (01.04.2010)
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Journal Article
α9 Integrin Promotes Neurite Outgrowth on Tenascin-C and Enhances Sensory Axon Regeneration
Andrews, Melissa R., Czvitkovich, Stefan, Dassie, Elisa, Vogelaar, Christina F., Faissner, Andreas, Blits, Bas, Gage, Fred H., ffrench-Constant, Charles, Fawcett, James W.
Published in The Journal of neuroscience (29.04.2009)
Published in The Journal of neuroscience (29.04.2009)
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Journal Article
Adeno-associated viral vector (AAV)-mediated gene transfer in the red nucleus of the adult rat brain: Comparative analysis of the transduction properties of seven AAV serotypes and lentiviral vectors
Blits, Bas, Derks, Sanne, Twisk, Jaap, Ehlert, Erich, Prins, Jolanda, Verhaagen, Joost
Published in Journal of neuroscience methods (15.01.2010)
Published in Journal of neuroscience methods (15.01.2010)
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Journal Article
Brain-derived neurotrophic factor released from engineered mesenchymal stem cells attenuates glutamate- and hydrogen peroxide-mediated death of staurosporine-differentiated RGC-5 cells
Harper, Matthew M., Adamson, Laura, Blits, Bas, Bunge, Mary Bartlett, Grozdanic, Sinisa D., Sakaguchi, Donald S.
Published in Experimental eye research (01.10.2009)
Published in Experimental eye research (01.10.2009)
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Journal Article
Gene therapy and peripheral nerve repair: a perspective
Hoyng, Stefan A, de Winter, Fred, Tannemaat, Martijn R, Blits, Bas, Malessy, Martijn J A, Verhaagen, Joost
Published in Frontiers in molecular neuroscience (15.07.2015)
Published in Frontiers in molecular neuroscience (15.07.2015)
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Journal Article
Rapid Directional Shift of Mitochondrial DNA Heteroplasmy in Animal Tissues by a Mitochondrially Targeted Restriction Endonuclease
Bayona-Bafaluy, Maria Pilar, Blits, Bas, Battersby, Brendan J., Shoubridge, Eric A., Moraes, Carlos T., Caskey, C. Thomas
Published in Proceedings of the National Academy of Sciences - PNAS (04.10.2005)
Published in Proceedings of the National Academy of Sciences - PNAS (04.10.2005)
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Journal Article
PhP.B Enhanced Adeno-Associated Virus Mediated-Expression Following Systemic Delivery or Direct Brain Administration
Pietersz, Kimberly L., Plessis, Francois Du, Pouw, Stephan M., Liefhebber, Jolanda M., van Deventer, Sander J., Martens, Gerard J. M., Konstantinova, Pavlina S., Blits, Bas
Published in Frontiers in bioengineering and biotechnology (03.08.2021)
Published in Frontiers in bioengineering and biotechnology (03.08.2021)
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Journal Article
Ex Vivo Adenoviral Vector-Mediated Neurotrophin Gene Transfer to Olfactory Ensheathing Glia: Effects on Rubrospinal Tract Regeneration, Lesion Size, and Functional Recovery after Implantation in the Injured Rat Spinal Cord
Ruitenberg, Marc J, Plant, Giles W, Hamers, Frank P. T, Wortel, Joke, Blits, Bas, Dijkhuizen, Paul A, Gispen, Willem Hendrik, Boer, Gerard J, Verhaagen, Joost
Published in The Journal of neuroscience (06.08.2003)
Published in The Journal of neuroscience (06.08.2003)
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Journal Article
In-Depth Characterization of a Mifepristone-Regulated Expression System for AAV5-Mediated Gene Therapy in the Liver
Liefhebber, Jolanda M., Martier, Raygene, Van der Zon, Tom, Keskin, Sonay, Huseinovic, Angelina, Lubelski, Jacek, Blits, Bas, Petry, Harald, Konstantinova, Pavlina
Published in Molecular therapy. Methods & clinical development (14.06.2019)
Published in Molecular therapy. Methods & clinical development (14.06.2019)
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Journal Article
GFAP-driven GFP expression in activated mouse Müller glial cells aligning retinal blood vessels following intravitreal injection of AAV2/6 vectors
Aartsen, Wendy M, van Cleef, Koen W R, Pellissier, Lucie P, Hoek, Robert M, Vos, Rogier M, Blits, Bas, Ehlert, Erich M E, Balaggan, Kamaljit S, Ali, Robin R, Verhaagen, Joost, Wijnholds, Jan
Published in PloS one (24.08.2010)
Published in PloS one (24.08.2010)
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Journal Article
Viral vector-mediated gene transfer of neurotrophins to promote regeneration of the injured spinal cord
Hendriks, William T.J., Ruitenberg, Marc J., Blits, Bas, Boer, Gerard J., Verhaagen, Joost
Published in Progress in Brain Research (2004)
Published in Progress in Brain Research (2004)
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Book Chapter
Journal Article
Adeno-associated viral vector-mediated gene transfer of brain-derived neurotrophic factor reverses atrophy of rubrospinal neurons following both acute and chronic spinal cord injury
Ruitenberg, Marc J, Blits, Bas, Dijkhuizen, Paul A, te Beek, Erik T, Bakker, Arne, van Heerikhuize, Joop J, Pool, Chris W, Hermens, Wim T.J, Boer, Gerard J, Verhaagen, Joost
Published in Neurobiology of disease (01.03.2004)
Published in Neurobiology of disease (01.03.2004)
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Journal Article
Pharmacological, Cell, and Gene Therapy Strategies to Promote Spinal Cord Regeneration
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Book Review
Journal Article