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Clinical trial to assess the safety, feasibility, and efficacy of transferring a potentially anti-arthritic cytokine gene to human joints with rheumatoid arthritis
Evans, C H, Robbins, P D, Ghivizzani, S C, Herndon, J H, Kang, R, Bahnson, A B, Barranger, J A, Elders, E M, Gay, S, Tomaino, M M, Wasko, M C, Watkins, S C, Whiteside, T L, Glorioso, J C, Lotze, M T, Wright, T M
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Centrifugal enhancement of retroviral mediated gene transfer
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Genetic Heterogeneity in Type 1 Gaucher Disease: Multiple Genotypes in Ashkenazic and Non-Ashkenazic Individuals
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Long-term expression and secretion of human glucocerebrosidase by primary murine and human myoblasts and differentiated myotubes
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Biosynthesis of the lysosomal enzyme glucocerebrosidase
Erickson, A H, Ginns, E I, Barranger, J A
Published in The Journal of biological chemistry (15.11.1985)
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Role of pH in determining the cell-type-specific residual activity of glucocerebrosidase in type 1 Gaucher disease
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Interaction of saposins, acidic lipids, and glucosylceramidase
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Published in The Journal of biological chemistry (05.02.1990)
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Retroviral gene transfer and sustained expression of human arylsulfatase A
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Published in Gene therapy (01.04.1996)
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Published in Gene therapy (01.04.1996)
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A Mutation in the Human Glucocerebrosidase Gene in Neuronopathic Gaucher's Disease
Tsuji, Shoji, Choudary, Prabhakara V, Martin, Brian M, Stubblefield, Barbara K, Mayor, June A, Barranger, John A, Ginns, Edward I
Published in The New England journal of medicine (05.03.1987)
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Retrovirus-mediated transfer of human alpha-galactosidase A gene to human CD34+ hematopoietic progenitor cells
Takiyama, N, Dunigan, J T, Vallor, M J, Kase, R, Sakuraba, H, Barranger, J A
Published in Human gene therapy (10.12.1999)
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Structure of the N-asparagine-linked oligosaccharide units of human placental beta-glucocerebrosidase
Takasaki, S, Murray, G J, Furbish, F S, Brady, R O, Barranger, J A, Kobata, A
Published in The Journal of biological chemistry (25.08.1984)
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Long-term expression of the glucocerebrosidase gene in mouse and human hematopoietic progenitors
Nimgaonkar, M, Bahnson, A, Kemp, A, Lancia, J, Mannion-Henderson, J, Boggs, S, Mohney, T, Baysal, B, Dunigan, J, Barranger, J A
Published in Leukemia (01.10.1995)
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