Harnessing whole human liver ex situ normothermic perfusion for preclinical AAV vector evaluation
Cabanes-Creus, Marti, Liao, Sophia H Y, Gale Navarro, Renina, Knight, Maddison, Nazareth, Deborah, Lau, Ngee-Soon, Ly, Mark, Zhu, Erhua, Roca-Pinilla, Ramon, Bugallo Delgado, Ricardo, Vicente, Ana F, Baltazar, Grober, Westhaus, Adrian, Merjane, Jessica, Crawford, Michael, McCaughan, Geoffrey W, Unzu, Carmen, González-Aseguinolaza, Gloria, Alexander, Ian E, Pulitano, Carlo, Lisowski, Leszek
Published in Nature communications (14.03.2024)
Published in Nature communications (14.03.2024)
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Novel human liver-tropic AAV variants define transferable domains that markedly enhance the human tropism of AAV7 and AAV8
Cabanes-Creus, Marti, Navarro, Renina Gale, Zhu, Erhua, Baltazar, Grober, Liao, Sophia H.Y., Drouyer, Matthieu, Amaya, Anais K., Scott, Suzanne, Nguyen, Loan Hanh, Westhaus, Adrian, Hebben, Matthias, Wilson, Laurence O.W., Thrasher, Adrian J., Alexander, Ian E., Lisowski, Leszek
Published in Molecular therapy. Methods & clinical development (10.03.2022)
Published in Molecular therapy. Methods & clinical development (10.03.2022)
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Attenuation of Heparan Sulfate Proteoglycan Binding Enhances In Vivo Transduction of Human Primary Hepatocytes with AAV2
Cabanes-Creus, Marti, Westhaus, Adrian, Navarro, Renina Gale, Baltazar, Grober, Zhu, Erhua, Amaya, Anais K., Liao, Sophia H.Y., Scott, Suzanne, Sallard, Erwan, Dilworth, Kimberley L., Rybicki, Arkadiusz, Drouyer, Matthieu, Hallwirth, Claus V., Bennett, Antonette, Santilli, Giorgia, Thrasher, Adrian J., Agbandje-McKenna, Mavis, Alexander, Ian E., Lisowski, Leszek
Published in Molecular therapy. Methods & clinical development (12.06.2020)
Published in Molecular therapy. Methods & clinical development (12.06.2020)
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Characterization of the humanized FRG mouse model and development of an AAV-LK03 variant with improved liver lobular biodistribution
Cabanes-Creus, Marti, Navarro, Renina Gale, Liao, Sophia H.Y., Scott, Suzanne, Carlessi, Rodrigo, Roca-Pinilla, Ramon, Knight, Maddison, Baltazar, Grober, Zhu, Erhua, Jones, Matthew, Denisenko, Elena, Forrest, Alistair R.R., Alexander, Ian E., Tirnitz-Parker, Janina E.E., Lisowski, Leszek
Published in Molecular therapy. Methods & clinical development (09.03.2023)
Published in Molecular therapy. Methods & clinical development (09.03.2023)
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Single amino acid insertion allows functional transduction of murine hepatocytes with human liver tropic AAV capsids
Cabanes-Creus, Marti, Navarro, Renina Gale, Liao, Sophia H.Y., Baltazar, Grober, Drouyer, Matthieu, Zhu, Erhua, Scott, Suzanne, Luong, Clement, Wilson, Laurence O.W., Alexander, Ian E., Lisowski, Leszek
Published in Molecular therapy. Methods & clinical development (11.06.2021)
Published in Molecular therapy. Methods & clinical development (11.06.2021)
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AAV-p40 Bioengineering Platform for Variant Selection Based on Transgene Expression
Westhaus, Adrian, Cabanes-Creus, Marti, Jonker, Timo, Sallard, Erwan, Navarro, Renina Gale, Zhu, Erhua, Baltazar Torres, Grober, Lee, Scott, Wilmott, Patrick, Gonzalez-Cordero, Anai, Santilli, Giorgia, Thrasher, Adrian J, Alexander, Ian E, Lisowski, Leszek
Published in Human gene therapy (01.06.2022)
Published in Human gene therapy (01.06.2022)
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High-Throughput In Vitro , Ex Vivo, and In Vivo Screen of Adeno-Associated Virus Vectors Based on Physical and Functional Transduction
Westhaus, Adrian, Cabanes-Creus, Marti, Rybicki, Arkadiusz, Baltazar, Grober, Navarro, Renina Gale, Zhu, Erhua, Drouyer, Matthieu, Knight, Maddison, Albu, Razvan F, Ng, Boaz H, Kalajdzic, Predrag, Kwiatek, Magdalena, Hsu, Kenneth, Santilli, Giorgia, Gold, Wendy, Kramer, Belinda, Gonzalez-Cordero, Anai, Thrasher, Adrian J, Alexander, Ian E, Lisowski, Leszek
Published in Human gene therapy (01.05.2020)
Published in Human gene therapy (01.05.2020)
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Restoring the natural tropism of AAV2 vectors for human liver
Cabanes-Creus, Marti, Hallwirth, Claus V, Westhaus, Adrian, Ng, Boaz H, Liao, Sophia H Y, Zhu, Erhua, Navarro, Renina Gale, Baltazar, Grober, Drouyer, Matthieu, Scott, Suzanne, Logan, Grant J, Santilli, Giorgia, Bennett, Antonette, Ginn, Samantha L, McCaughan, Geoff, Thrasher, Adrian J, Agbandje-McKenna, Mavis, Alexander, Ian E, Lisowski, Leszek
Published in Science translational medicine (09.09.2020)
Published in Science translational medicine (09.09.2020)
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Treatment of Skin Inflammation with Benzoxaborole Phosphodiesterase Inhibitors: Selectivity, Cellular Activity, and Effect on Cytokines Associated with Skin Inflammation and Skin Architecture Changes
Dong, Chen, Virtucio, Charlotte, Zemska, Olga, Baltazar, Grober, Zhou, Yasheen, Baia, Diogo, Jones-Iatauro, Shannon, Sexton, Holly, Martin, Shamra, Dee, Joshua, Mak, Yvonne, Meewan, Maliwan, Rock, Fernando, Akama, Tsutomu, Jarnagin, Kurt
Published in The Journal of pharmacology and experimental therapeutics (01.09.2016)
Published in The Journal of pharmacology and experimental therapeutics (01.09.2016)
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Na+/H+ Exchangers Are Required for the Development and Function of Vertebrate Mucociliary Epithelia
Sun, Dingyuan I, Tasca, Alexia, Haas, Maximilian, Baltazar, Grober, Harland, Richard M, Finkbeiner, Walter E, Walentek, Peter
Published in Cells, tissues, organs (01.01.2018)
Published in Cells, tissues, organs (01.01.2018)
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