Safety and Efficacy of Erythrocyte Encapsulated Thymidine Phosphorylase in Mitochondrial Neurogastrointestinal Encephalomyopathy
Levene, Michelle, Bain, Murray D, Moran, Nicholas F, Nirmalananthan, Niranjanan, Poulton, Joanna, Scarpelli, Mauro, Filosto, Massimiliano, Mandel, Hanna, MacKinnon, Andrew D, Fairbanks, Lynette, Pacitti, Dario, Bax, Bridget E
Published in Journal of clinical medicine (05.04.2019)
Published in Journal of clinical medicine (05.04.2019)
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Journal Article
Erythrocyte Encapsulated Thymidine Phosphorylase for the Treatment of Patients with Mitochondrial Neurogastrointestinal Encephalomyopathy: Study Protocol for a Multi-Centre, Multiple Dose, Open Label Trial
Bax, Bridget E, Levene, Michelle, Bain, Murray D, Fairbanks, Lynette D, Filosto, Massimiliano, Kalkan Uçar, Sema, Klopstock, Thomas, Kornblum, Cornelia, Mandel, Hanna, Rahman, Shamima, Roubertie, Agathe, Scarpelli, Mauro, Sedgwick, Philip M, Baru, Moshe, Sellos-Moura, Marcia, Price, Jeanie, Horn, Patrick, Nirmalananthan, Niranjanan
Published in Journal of clinical medicine (24.07.2019)
Published in Journal of clinical medicine (24.07.2019)
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Journal Article
Clinical and biochemical improvements in a patient with MNGIE following enzyme replacement
Bax, Bridget E, Bain, Murray D, Scarpelli, Mauro, Filosto, Massimiliano, Tonin, Paola, Moran, Nicholas
Published in Neurology (01.10.2013)
Published in Neurology (01.10.2013)
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Journal Article
Unexplained gastrointestinal symptoms: Think mitochondrial disease
Chapman, Thomas P, Hadley, Gina, Fratter, Carl, Cullen, Sue N, Bax, Bridget E, Bain, Murray D, Sapsford, Robert A, Poulton, Joanna, Travis, Simon P
Published in Digestive and liver disease (01.01.2014)
Published in Digestive and liver disease (01.01.2014)
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Journal Article
A 9-yr evaluation of carrier erythrocyte encapsulated adenosine deaminase (ADA) therapy in a patient with adult-type ADA deficiency
Bax, Bridget E., Bain, Murray D., Fairbanks, Lynette D., Webster, A David B., Ind, Philip W., Hershfield, Michael S., Chalmers, Ronald A.
Published in European journal of haematology (01.10.2007)
Published in European journal of haematology (01.10.2007)
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Journal Article
The mouse immune response to carrier erythrocyte entrapped antigens
Murray, Anne M., Pearson, Ian F.S., Fairbanks, Lynette D., Chalmers, Ronald A., Bain, Murray D., Bax, Bridget E.
Published in Vaccine (28.08.2006)
Published in Vaccine (28.08.2006)
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Journal Article
Riboflavin-responsive glutaryl CoA dehydrogenase deficiency
Chalmers, Ronald A., Bain, Murray D., Zschocke, Johannes
Published in Molecular genetics and metabolism (01.05.2006)
Published in Molecular genetics and metabolism (01.05.2006)
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Journal Article
Survival of human carrier erythrocytes in vivo
BAX, Bridget E., BAIN, Murray D., TALBOT, Peter J., John PARKER-WILLIAMS, E., CHALMERS, Ronald A.
Published in Clinical science (1979) (01.02.1999)
Published in Clinical science (1979) (01.02.1999)
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Journal Article
Haemorheology in Gaucher disease
Bax, Bridget E., Richfield, Linda, Bain, Murray D., Mehta, Atul B., Chalmers, Ronald A., Rampling, Michael W.
Published in European journal of haematology (01.09.2005)
Published in European journal of haematology (01.09.2005)
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Journal Article
Survival of human carrier erythrocytes in vivo
BAX, B. E, BAIN, M. D, TALBOT, P. J, PARKER-WILLIAMS, E. J, CHALMERS, R. A
Published in Clinical science (1979) (01.02.1999)
Published in Clinical science (1979) (01.02.1999)
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Conference Proceeding
Journal Article
Oral cobalamin therapy
Chalmers, Ronald A, Bain, Murray D, Costello, lan
Published in The Lancet (British edition) (08.01.2000)
Published in The Lancet (British edition) (08.01.2000)
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Journal Article
Secondary analysis of economic data: a review of cost-benefit studies of neonatal screening for phenylketonuria
Lord, J, Thomason, M J, Littlejohns, P, Chalmers, R A, Bain, M D, Addison, G M, Wilcox, A H, Seymour, C A
Published in Journal of epidemiology and community health (1979) (01.03.1999)
Published in Journal of epidemiology and community health (1979) (01.03.1999)
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Journal Article
A systematic review of evidence for the appropriateness of neonatal screening programmes for inborn errors of metabolism
Thomason, Margaret J., Lord, Joanne, Bain, Murray D., Chalmers, Ronald A., Littlejohns, Peter, Addison, G. Michael, Wilcox, A. Hervey, Seymour, Carol A.
Published in Journal of public health (Oxford, England) (01.09.1998)
Published in Journal of public health (Oxford, England) (01.09.1998)
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Journal Article
The entrapment of mannose-terminated glucocerebrosidase (Alglucerase) in human carrier erythrocytes
Bax, B E, Bain, M D, Ward, C P, Fensom, A H, Chalmers, R A
Published in Biochemical Society transactions (01.08.1996)
Published in Biochemical Society transactions (01.08.1996)
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