EBMT/ESID inborn errors working party guidelines for hematopoietic stem cell transplantation for inborn errors of immunity
Lankester, A. C., Albert, M. H., Booth, C., Gennery, A. R., Güngör, T., Hönig, M., Morris, E. C., Moshous, D., Neven, B., Schulz, A., Slatter, M., Veys, P.
Published in Bone marrow transplantation (Basingstoke) (01.09.2021)
Published in Bone marrow transplantation (Basingstoke) (01.09.2021)
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Levy, R, Gérard, L, Kuemmerle-Deschner, J, Lachmann, H J, Koné-Paut, I, Cantarini, L, Woo, P, Naselli, A, Bader-Meunier, B, Insalaco, A, Al-Mayouf, S M, Ozen, S, Hofer, M, Frenkel, J, Modesto, C, Nikishina, I, Schwarz, T, Martino, S, Meini, A, Quartier, P, Martini, A, Ruperto, N, Neven, B, Gattorno, M
Published in Annals of the rheumatic diseases (01.11.2015)
Published in Annals of the rheumatic diseases (01.11.2015)
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Hacein-Bey-Abina, Salima, Pai, Sung-Yun, Gaspar, H. Bobby, Armant, Myriam, Berry, Charles C, Blanche, Stephane, Bleesing, Jack, Blondeau, Johanna, de Boer, Helen, Buckland, Karen F, Caccavelli, Laure, Cros, Guilhem, De Oliveira, Satiro, Fernández, Karen S, Guo, Dongjing, Harris, Chad E, Hopkins, Gregory, Lehmann, Leslie E, Lim, Annick, London, Wendy B, van der Loo, Johannes C.M, Malani, Nirav, Male, Frances, Malik, Punam, Marinovic, M. Angélica, McNicol, Anne-Marie, Moshous, Despina, Neven, Benedicte, Oleastro, Matías, Picard, Capucine, Ritz, Jerome, Rivat, Christine, Schambach, Axel, Shaw, Kit L, Sherman, Eric A, Silberstein, Leslie E, Six, Emmanuelle, Touzot, Fabien, Tsytsykova, Alla, Xu-Bayford, Jinhua, Baum, Christopher, Bushman, Frederic D, Fischer, Alain, Kohn, Donald B, Filipovich, Alexandra H, Notarangelo, Luigi D, Cavazzana, Marina, Williams, David A, Thrasher, Adrian J
Published in The New England journal of medicine (09.10.2014)
Published in The New England journal of medicine (09.10.2014)
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Published in Rheumatology (Oxford, England) (01.06.2014)
Published in Rheumatology (Oxford, England) (01.06.2014)
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Assessing acute toxicity profiles of HLA-identical hematopoietic stem cell transplantation in pediatric patients with sickle cell anemia: A comprehensive analysis on behalf of the SFGM-TC
Delafoy, M, Dalle, J H, Pondarre, C, Andrieu, G P, Fahd, M, Yakouben, K, Castelle, M, Koehl, B, Neven, B, Grain, A
Published in American journal of hematology (24.09.2024)
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Frémond, M.-L., Pérot, P., Muth, E., Cros, G., Dumarest, M., Mahlaoui, N., Seilhean, D., Desguerre, I., Hébert, C., Corre-Catelin, N., Neven, B., Lecuit, M., Blanche, S., Picard, C., Eloit, M.
Published in Journal of the Pediatric Infectious Diseases Society (01.09.2015)
Published in Journal of the Pediatric Infectious Diseases Society (01.09.2015)
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Dhunputh, C., Ducassou, S., Fernandes, H., Picard, Capucine, Rieux-Laucat, Frédéric, Viallard, J.-F., Lazaro, E., Hermine, O., Jouvray, M., Machelard, I., Lambilliotte, A., Malphettes, M., Moshous, D., Neven, B., Gauthier, A., Garnier, N., Leblanc, T., Landman-Parker, J., Leverger, G., Aladjidi, N.
Published in Blood (13.01.2022)
Published in Blood (13.01.2022)
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Neven, Bénédicte, Mamessier, Emilie, Bruneau, Julie, Kaltenbach, Sophie, Kotlarz, Daniel, Suarez, Felipe, Masliah-Planchon, Julien, Billot, Katy, Canioni, Danielle, Frange, Pierre, Radford-Weiss, Isabelle, Asnafi, Vahid, Murugan, Dhaarini, Bole, Christine, Nitschke, Patrick, Goulet, Olivier, Casanova, Jean-Laurent, Blanche, Stéphane, Picard, Capucine, Hermine, Olivier, Rieux-Laucat, Frederic, Brousse, Nicole, Davi, Frederic, Baud, Véronique, Klein, Christoph, Nadel, Bertrand, Ruemmele, Frank, Fischer, Alain
Published in Blood (28.11.2013)
Published in Blood (28.11.2013)
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Schuetz, C., Gerke, J., Ege, M., Walter, J., Kusters, M., Worth, A., Kanakry, J. A., Dimitrova, D., Wolska-Kuśnierz, B., Chen, K., Unal, E., Karakukcu, M., Pashchenko, O., Leiding, J., Kawai, T., Amrolia, P. J., Berghuis, D., Buechner, J., Buchbinder, D., Cowan, M. J., Gennery, A. R., Güngör, T., Heimall, J., Miano, M., Meyts, I., Morris, E. C., Rivière, J., Sharapova, S. O., Shaw, P. J., Slatter, M., Honig, M., Veys, P., Fischer, A., Cavazzana, M., Moshous, D., Schulz, A., Albert, M. H., Puck, J. M., Lankester, A. C., Notarangelo, L. D., Neven, B.
Published in Blood (16.02.2023)
Published in Blood (16.02.2023)
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Efficacy of haematopoietic stem cell boost as a rescue for poor graft function after haematopoietic stem cell transplantation: A multicentre retrospective study on behalf of the Francophone Society of Bone Marrow Transplantation and Cellular Therapy (SFGM‐TC)
Gaffet, M., Wiedemann, A., Dalle, J.‐H., Bilger, K., Forcade, E., Robin, M., Cornillon, J., Labussière‐Wallet, H., Ceballos, P., Bulabois, C.‐E., Loschi, M., Orvain, C., Rubio, M. T., Neven, B., Pagliuca, S., Pochon, C.
Published in British journal of haematology (01.06.2023)
Published in British journal of haematology (01.06.2023)
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Cutaneous granulomas with primary immunodeficiency in children: a report of 17 new patients and a review of the literature
Leclerc‐Mercier, S., Moshous, D., Neven, B., Mahlaoui, N., Martin, L., Pellier, I, Blanche, S., Picard, C., Fischer, A., Perot, P., Eloit, M., Fraitag, S., Bodemer, C.
Published in Journal of the European Academy of Dermatology and Venereology (01.07.2019)
Published in Journal of the European Academy of Dermatology and Venereology (01.07.2019)
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Rubella vaccine–induced granulomas are a novel phenotype with incomplete penetrance of genetic defects in cytotoxicity
Groß, Miriam, Speckmann, Carsten, May, Annette, Gajardo-Carrasco, Tania, Wustrau, Katharina, Maier, Sarah Lena, Panning, Marcus, Huzly, Daniela, Agaimy, Abbas, Bryceson, Yenan T., Choo, Sharon, Chow, C.W., Dückers, Gregor, Fasth, Anders, Fraitag, Sylvie, Gräwe, Katja, Haxelmans, Sabine, Holzinger, Dirk, Hudowenz, Ole, Hübschen, Judith M., Khurana, Claudia, Kienle, Korbinian, Klifa, Roman, Korn, Klaus, Kutzner, Heinz, Lämmermann, Tim, Ledig, Svea, Lipsker, Dan, Meeths, Marie, Naumann-Bartsch, Nora, Rascon, Jelena, Schänzer, Anne, Seidl, Maximilian, Tesi, Bianca, Vauloup-Fellous, Christelle, Vollmer-Kary, Beate, Warnatz, Klaus, Wehr, Claudia, Neven, Bénédicte, Vargas, Pablo, Sepulveda, Fernando E., Lehmberg, Kai, Schmitt-Graeff, Annette, Ehl, Stephan
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Published in Journal of allergy and clinical immunology (01.01.2022)
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The first steps towards a diverse and inclusive EBMT: a position paper
Montoto, S., Snowden, J. A., Chabannon, C., Corbacioglu, S., de la Camara, R., Dolstra, H., Greco, R., Gusi, A., Hamad, N., Kenyon, M., Kröger, N., Mohty, M., Murray, J., Mueller, A., Neven, B., Peffault de Latour, R., Peric, Z., Sánchez-Ortega, I., Sureda, A., Verhoeven, B., Villar, A., Yakoub-Agha, I.
Published in Bone marrow transplantation (Basingstoke) (01.03.2022)
Published in Bone marrow transplantation (Basingstoke) (01.03.2022)
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Clinical Heterogeneity of Immune Dysregulation, Polyendocrinopathy, Enteropathy, X-Linked Syndrome: A French Multicenter Retrospective Study
Duclaux-Loras, R, Charbit-Henrion, F, Neven, B, Nowak, J, Collardeau-Frachon, S, Malcus, C, Ray, P F, Moshous, D, Beltrand, J, Goulet, O, Cerf-Bensussan, N, Lachaux, A, Rieux-Laucat, F, Ruemmele, F M
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THU0053 CONTRIBUTION OF DEFECTIVE NON-APOPTOTIC FAS SIGNALING TO IMMUNE DYSREGULATION IN AUTOIMMUNE LYMPHOPROLIFERATIVE SYNDROME (ALPS)
Staniek, J., Kalina, T., Andrieux, G., Boerries, M., Janowska, I., Fuentes, M., Bakardjieva, M., Raabe, J., Neumann, J., Stuchly, J., Benes, V., Garcia, R., Garcia, J., Diez, P., Catala, A., Neven, B., Neth, O., Olbrich, P., Voll, R., Alsina, L., Allende, L., Gonzales-Granado, L., Thiel, J., Venhoff, N., Lorenzetti, R., Unger, S., Seidl, M., Mielenz, D., Schneider, P., Ehl, S., Rensing-Ehl, A., Smulski, C., Rizzi, M.
Published in Annals of the rheumatic diseases (01.06.2020)
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Cutaneous manifestations of immune dysregulation, polyendocrinopathy, enteropathy, X-linked (IPEX) syndrome
Halabi-Tawil, M., Ruemmele, F.M., Fraitag, S., Rieux-Laucat, F., Neven, B., Brousse, N., De Prost, Y., Fischer, A., Goulet, O., Bodemer, C.
Published in British journal of dermatology (1951) (01.03.2009)
Published in British journal of dermatology (1951) (01.03.2009)
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P‐027: SICKLE CELL DISEASE AND AUTOIMMUNE LIVER DISORDERS: SHOULD HEMATOPOIETIC STEM CELL TRANSPLANTATION BE DISCUSSED EARLY?
F., LACAILLE, S., ALLALI, M., TAYLOR, M., CASTELLE, J., REBEUH, B., NEVEN, C., PAILLARD, M., DE MONTALEMBERT
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Published in HemaSphere (16.08.2022)
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Molecular basis of the spectral expression of CIAS1 mutations associated with phagocytic cell-mediated autoinflammatory disorders CINCA/NOMID, MWS, and FCU
NEVEN, Bénédicte, CALLEBAUT, Isabelle, OERTLE, Stefan, ALLEN, Roger, MORGAN, Gareth, BORKHARDT, Arndt, HILL, Clare, GARDNER-MEDWIN, Janet, FISCHER, Alain, DE SAINT BASILE, Geneviève, PRIEUR, Anne-Marie, FELDMANN, Jérome, BODEMER, Christine, LEPORE, Loredana, DERFALVI, Beata, BENJAPONPITAK, Suata, VESELY, Richard, SAUVAIN, Marie Jose
Published in Blood (01.04.2004)
Published in Blood (01.04.2004)
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Paroxysmal strabismus and stridor acquired in childhood: Do not overlook calcemia
Escudier, A., Giabicani, E., Neven, B., Gouache, E., Blanchard, M., Isapof, A., Nougues, M.-C., Freihuber, C.
Published in Archives de pédiatrie : organe officiel de la Société française de pédiatrie (01.02.2020)
Published in Archives de pédiatrie : organe officiel de la Société française de pédiatrie (01.02.2020)
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