Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of β-hemoglobinopathies
Venkatesan, Vigneshwaran, Christopher, Abisha Crystal, Rhiel, Manuel, Azhagiri, Manoj Kumar K., Babu, Prathibha, Walavalkar, Kaivalya, Saravanan, Bharath, Andrieux, Geoffroy, Rangaraj, Sumathi, Srinivasan, Saranya, Karuppusamy, Karthik V., Jacob, Annlin, Bagchi, Abhirup, Pai, Aswin Anand, Nakamura, Yukio, Kurita, Ryo, Balasubramanian, Poonkuzhali, Pai, Rekha, Marepally, Srujan Kumar, Mohankumar, Kumarasamypet Murugesan, Velayudhan, Shaji R., Boerries, Melanie, Notani, Dimple, Cathomen, Toni, Srivastava, Alok, Thangavel, Saravanabhavan
Published in Molecular therapy. Nucleic acids (13.06.2023)
Published in Molecular therapy. Nucleic acids (13.06.2023)
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Preferential Expansion of Human CD34 + CD133 + CD90 + Hematopoietic Stem Cells Enhances Gene-Modified Cell Frequency for Gene Therapy
Christopher, Abisha Crystal, Venkatesan, Vigneshwaran, Karuppusamy, Karthik V, Srinivasan, Saranya, Babu, Prathibha, Azhagiri, Manoj Kumar K, Chambayil, Karthik, Bagchi, Abhirup, Rajendiran, Vignesh, Ravi, Nithin Sam, Kumar, Sanjay, Marepally, Srujan Kumar, Mohankumar, Kumarasamypet Murugesan, Srivastava, Alok, Velayudhan, Shaji R, Thangavel, Saravanabhavan
Published in Human gene therapy (01.02.2022)
Published in Human gene therapy (01.02.2022)
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