Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy
Cartier, Nathalie, Hacein-Bey-Abina, Salima, Bartholomae, Cynthia C, Veres, Gabor, Schmidt, Manfred, Kutschera, Ina, Vidaud, Michel, Abel, Ulrich, Dal-Cortivo, Liliane, Caccavelli, Laure, Mahlaoui, Nizar, Kiermer, Véronique, Mittelstaedt, Denice, Bellesme, Céline, Lahlou, Najiba, Lefrère, François, Blanche, Stéphane, Audit, Muriel, Payen, Emmanuel, Leboulch, Philippe, l'Homme, Bruno, Bougnères, Pierre, Von Kalle, Christof, Fischer, Alain, Cavazzana-Calvo, Marina, Aubourg, Patrick
Published in Science (American Association for the Advancement of Science) (06.11.2009)
Published in Science (American Association for the Advancement of Science) (06.11.2009)
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Large-scale manufacture and characterization of a lentiviral vector produced for clinical ex vivo gene therapy application
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A phase I trial of adeno-associated virus serotype 1-γ-sarcoglycan gene therapy for limb girdle muscular dystrophy type 2C
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Published in Brain (London, England : 1878) (01.02.2012)
Published in Brain (London, England : 1878) (01.02.2012)
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A Clinical Trial of Gene Therapy for Mucopolysaccharidosis VI, a Severe Lysosomal Storage Disorder (MeuSIX)
Published in Human gene therapy. Clinical development
(01.06.2015)
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Hematopoietic Stem Cell Gene Therapy Trial with Lentiviral Vector in X-Linked Adrenoleukodystrophy
Cavazzana-Calvo, Marina, Cartier, Nathalie, Abina, Salima Hacein-Bey, Veres, Gabor, Schmidt, Manfred, Bartholomae, Cynthia, Vidaud, Michel, Dal-Cortivo, Liliane, Caccavelli, Laure, Malhaoui, Nizar, Frange, Pierre, Kiermer, Véronique, Mittelstaedt, Denice, Simmons, Andrew, Bellesme, Céline, Lefrère, François, Lagresle, Chantale, Blanche, Stephane, Charneau, Pierre, Audit, Muriel, L'Homme, Bruno, Zhao-Emonet, Jing Chao, Fichelson, Serge, Pflumio, Françoise, Dubart-Kupperschmitt, Anne, Salzman, Rachel, Salzman, Amber, Bougnères, Pierre, Von Kalle, Christof, Fischer, Alain, Aubourg, Patrick
Published in Blood (16.11.2008)
Published in Blood (16.11.2008)
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rAAV vector product characterization and stability studies
Snyder, Richard O, Audit, Muriel, Francis, Joyce D
Published in Methods in molecular biology (Clifton, N.J.) (01.01.2011)
Published in Methods in molecular biology (Clifton, N.J.) (01.01.2011)
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Isolation and Regional Mapping of cDNAs Expressed during Early Human Development
Jay, Philippe, Diriong, Sylvie, Taviaux, Sylvie, Roeckel, Nathalie, Mattéi, Marie-Geneviève, Audit, Muriel, Bergé-Lefranc, Jean-Louis, Fontès, Michel, Berta, Philippe
Published in Genomics (San Diego, Calif.) (01.01.1997)
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Cyclin B (p56 cdc13) localization in the yeast Schizosaccharomyces pombe: An ultrastructural and immunocytochemical study
Audit, Muriel, Barbier, Michèle, Soyer-Gobillard, Marie-Odile, Albert, Marie, Géraud, Marie-Line, Nicolas, Gisèle, Lenaers, Guy
Published in Biology of the cell (1996)
Published in Biology of the cell (1996)
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Cyclin B (p56cdc13) localization in the yeast Schizosaccharomyces pombe: An ultrastructural and immunocytochemical study
Audit, Muriel, Barbier, Michèle, Soyer-Gobillard, Marie-Odile, Albert, Marie, Géraud, Marie-Line, Nicolas, Gisèle, Lenaers, Guy
Published in Biology of the cell (1996)
Published in Biology of the cell (1996)
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