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Study design and baseline characteristics for the reflect gene therapy trial ofm.11778g>A/ND4-LHON

by Subramanian, Prem S, Newman, Nancy J, Moster, Mark, Wang, An-Guor, Yu-Wai-Man, Patrick, Donahue, Sean, Leroy, Bart P, Carelli, Valerio, Biousse, Valerie, Vignal-Clermont, Catherine, Sergott, Robert C, Sadun, Alfredo A, Rebolleda, Gema, Chwalisz, Bart K, Banik, Rudrani, Bazin, Fabienne, Cox, Eric, Roux, Michel, Taiel, Magali, Sahel, Jose-Alain, Giulia, Amore, Shweta, Anand, Rudrani, Banik, Piero, Barboni, Valérie, Biousse, Hayley, Boston, Asma, Burale, Michele, Carbonelli, Valerio, Carelli, Celia, Chen, Hui-Chen, Cheng, Steve, Cho, Chwalisz Bart, K, Manuela, Contin, Pietro, D’Agati, DeBusk Adam, A, Julie, De Zaeytijd, Jannah, Dobbs, Donahue Sean, P, Lindreth, DuBois, Simona, Esposti, Alcides, Fernandes Filho, Elizabeth, Fortin, Sapna, Gangaputra, Deborah, Gibbs, François, Girmens Jean, Rabih, Hage, Haller Julia, A, Gad, Heilweil, GeorgeBaker, Hubbard III, Jeong-Min, Hwang, Laia, Jaumendreu Urquijo, Neringa, Jurkute, Rustum, Karanjia, Wahiba, Khemliche, Chiara, La Morgia, Leroy Bart, P, Maria, Massini, Marc, Mathias, Memon Muhammad, A, Susan, Mohamed, Moster Mark, L, Muñoz NegreteFrancisco, J, Newman Nancy, J, Ghazala, O’Keefe, Shriji, Patel, Paula, Pecen, Peragallo Jason, H, Lise, Plaine, Mary, Preston, Gema, Rebolleda Fernández, Martina, Romagnoli, Sadun Alfredo, A, Sahel José, A, Melissa, SantaMaria, Sergott Robert, C, Subramanian Prem, S, Chuanbin, Sun, Katy, Tai, Heather, Tollis, Irena, Tsui, Tucker William, R, Catherine, Vignal-Clermont, An-Guor, Wang, Saige, Wilkins, Patrick, Yu-Wai-Man
Published in BMJ open ophthalmology (15.11.2022)

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