A synthetic AAV vector enables safe and efficient gene transfer to the mammalian inner ear
Landegger, Lukas D, Pan, Bifeng, Askew, Charles, Wassmer, Sarah J, Gluck, Sarah D, Galvin, Alice, Taylor, Ruth, Forge, Andrew, Stankovic, Konstantina M, Holt, Jeffrey R, Vandenberghe, Luk H
Published in Nature biotechnology (01.03.2017)
Published in Nature biotechnology (01.03.2017)
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Gene therapy restores auditory and vestibular function in a mouse model of Usher syndrome type 1c
Pan, Bifeng, Askew, Charles, Galvin, Alice, Heman-Ackah, Selena, Asai, Yukako, Indzhykulian, Artur A, Jodelka, Francine M, Hastings, Michelle L, Lentz, Jennifer J, Vandenberghe, Luk H, Holt, Jeffrey R, Géléoc, Gwenaëlle S
Published in Nature biotechnology (01.03.2017)
Published in Nature biotechnology (01.03.2017)
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Customized blood-brain barrier shuttle peptide to increase AAV9 vector crossing the BBB and augment transduction in the brain
Zhang, Xintao, Chai, Zheng, Lee Dobbins, Amanda, Itano, Michelle S., Askew, Charles, Miao, Zhe, Niu, Hongqian, Samulski, R. Jude, Li, Chengwen
Published in Biomaterials (01.02.2022)
Published in Biomaterials (01.02.2022)
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Deletion of PDZD7 disrupts the Usher syndrome type 2 protein complex in cochlear hair cells and causes hearing loss in mice
Zou, Junhuang, Zheng, Tihua, Ren, Chongyu, Askew, Charles, Liu, Xiao-Ping, Pan, Bifeng, Holt, Jeffrey R, Wang, Yong, Yang, Jun
Published in Human molecular genetics (01.05.2014)
Published in Human molecular genetics (01.05.2014)
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Grxcr2 is required for stereocilia morphogenesis in the cochlea
Avenarius, Matthew R, Jung, Jae-Yun, Askew, Charles, Jones, Sherri M, Hunker, Kristina L, Azaiez, Hela, Rehman, Atteeq U, Schraders, Margit, Najmabadi, Hossein, Kremer, Hannie, Smith, Richard J H, Géléoc, Gwenaëlle S G, Dolan, David F, Raphael, Yehoash, Kohrman, David C
Published in PloS one (29.08.2018)
Published in PloS one (29.08.2018)
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Development of AAV Variants with Human Hepatocyte Tropism and Neutralizing Antibody Escape Capacity
Pei, Xiaolei, Shao, Wenwei, Xing, Allene, Askew, Charles, Chen, Xiaojing, Cui, Caibin, Abajas, Yasmina L., Gerber, David A., Merricks, Elizabeth P., Nichols, Timothy C., Li, Wuping, Samulski, R. Jude, Li, Chengwen
Published in Molecular therapy. Methods & clinical development (11.09.2020)
Published in Molecular therapy. Methods & clinical development (11.09.2020)
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Tmc gene therapy restores auditory function in deaf mice
Askew, Charles, Rochat, Cylia, Pan, Bifeng, Asai, Yukako, Ahmed, Hena, Child, Erin, Schneider, Bernard L, Aebischer, Patrick, Holt, Jeffrey R
Published in Science translational medicine (08.07.2015)
Published in Science translational medicine (08.07.2015)
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Hair cell and neural contributions to the cochlear summating potential
Pappa, Andrew K, Hutson, Kendall A, Scott, William C, Wilson, J David, Fox, Kevin E, Masood, Maheer M, Giardina, Christopher K, Pulver, Stephen H, Grana, Gilberto D, Askew, Charles, Fitzpatrick, Douglas C
Published in Journal of neurophysiology (01.06.2019)
Published in Journal of neurophysiology (01.06.2019)
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Superior human hepatocyte transduction with adeno-associated virus vector serotype 7
Shao, Wenwei, Pei, Xiaolei, Cui, Caibin, Askew, Charles, Dobbins, Amanda, Chen, Xiaojing, Abajas, Yasmina L, Gerber, David A, Samulski, R Jude, Nichols, Timothy C, Li, Chengwen
Published in Gene therapy (01.12.2019)
Published in Gene therapy (01.12.2019)
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The postnatal accumulation of junctional E-cadherin is inversely correlated with the capacity for supporting cells to convert directly into sensory hair cells in mammalian balance organs
Collado, Maria Sol, Thiede, Benjamin R, Baker, Wendy, Askew, Charles, Igbani, Lisa M, Corwin, Jeffrey T
Published in The Journal of neuroscience (17.08.2011)
Published in The Journal of neuroscience (17.08.2011)
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The mechanosensory structure of the hair cell requires clarin-1, a protein encoded by Usher syndrome III causative gene
Geng, Ruishuang, Melki, Sami, Chen, Daniel H-C, Tian, Guilian, Furness, David N, Oshima-Takago, Tomoko, Neef, Jakob, Moser, Tobias, Askew, Charles, Horwitz, Geoff, Holt, Jeffrey R, Imanishi, Yoshikazu, Alagramam, Kumar N
Published in The Journal of neuroscience (11.07.2012)
Published in The Journal of neuroscience (11.07.2012)
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Localization and expression of clarin-1, the Clrn1 gene product, in auditory hair cells and photoreceptors
Zallocchi, Marisa, Meehan, Daniel T., Delimont, Duane, Askew, Charles, Garige, Suneetha, Gratton, Michael Anne, Rothermund-Franklin, Christie A., Cosgrove, Dominic
Published in Hearing research (01.09.2009)
Published in Hearing research (01.09.2009)
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Matrix Metalloproteinase Dysregulation in the Stria Vascularis of Mice with Alport Syndrome: Implications for Capillary Basement Membrane Pathology
Gratton, Michael Anne, Rao, Velidi H, Meehan, Daniel T, Askew, Charles, Cosgrove, Dominic
Published in The American journal of pathology (01.05.2005)
Published in The American journal of pathology (01.05.2005)
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