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Ozimski, Lauren L., Sabater‐Arcis, Maria, Bargiela, Ariadna, Artero, Ruben
Published in Biological reviews of the Cambridge Philosophical Society (01.04.2021)
Published in Biological reviews of the Cambridge Philosophical Society (01.04.2021)
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miR-23b and miR-218 silencing increase Muscleblind-like expression and alleviate myotonic dystrophy phenotypes in mammalian models
Cerro-Herreros, Estefania, Sabater-Arcis, Maria, Fernandez-Costa, Juan M, Moreno, Nerea, Perez-Alonso, Manuel, Llamusi, Beatriz, Artero, Ruben
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Published in Nature communications (26.06.2018)
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Myotonic dystrophy: candidate small molecule therapeutics
Konieczny, Piotr, Selma-Soriano, Estela, Rapisarda, Anna S., Fernandez-Costa, Juan M., Perez-Alonso, Manuel, Artero, Ruben
Published in Drug discovery today (01.11.2017)
Published in Drug discovery today (01.11.2017)
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Genetic and chemical modifiers of a CUG toxicity model in Drosophila
Garcia-Lopez, Amparo, Monferrer, Lidon, Garcia-Alcover, Irma, Vicente-Crespo, Marta, Alvarez-Abril, M Carmen, Artero, Ruben D
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Published in PloS one (13.02.2008)
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Rabphilin involvement in filtration and molecular uptake in Drosophila nephrocytes suggests a similar role in human podocytes
Selma-Soriano, Estela, Llamusi, Beatriz, Fernández-Costa, Juan Manuel, Ozimski, Lauren Louise, Artero, Rubén, Redón, Josep
Published in Disease models & mechanisms (21.09.2020)
Published in Disease models & mechanisms (21.09.2020)
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Defined D-hexapeptides bind CUG repeats and rescue phenotypes of myotonic dystrophy myotubes in a Drosophila model of the disease
Rapisarda, Anna, Bargiela, Ariadna, Llamusi, Beatriz, Pont, Isabel, Estrada-Tejedor, Roger, Garcia-España, Enrique, Artero, Ruben, Perez-Alonso, Manuel
Published in Scientific reports (30.09.2021)
Published in Scientific reports (30.09.2021)
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Therapeutic Potential of AntagomiR-23b for Treating Myotonic Dystrophy
Cerro-Herreros, Estefanía, González-Martínez, Irene, Moreno-Cervera, Nerea, Overby, Sarah, Pérez-Alonso, Manuel, Llamusí, Beatriz, Artero, Rubén
Published in Molecular therapy. Nucleic acids (04.09.2020)
Published in Molecular therapy. Nucleic acids (04.09.2020)
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Taurine activates the AKT-mTOR axis to restore muscle mass and contractile strength in human 3D in vitro models of steroid myopathy
Mughal, Sheeza, Sabater-Arcis, Maria, Artero, Ruben, Ramón-Azcón, Javier, Fernández-Costa, Juan M
Published in Disease models & mechanisms (01.04.2024)
Published in Disease models & mechanisms (01.04.2024)
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Natural Compound Boldine Lessens Myotonic Dystrophy Type 1 Phenotypes in DM1 Drosophila Models, Patient-Derived Cell Lines, and HSA[sup.LR] Mice
Álvarez-Abril, Mari Carmen, García-Alcover, Irma, Colonques-Bellmunt, Jordi, Garijo, Raquel, Pérez-Alonso, Manuel, Artero, Rubén, López-Castel, Arturo
Published in International journal of molecular sciences (01.06.2023)
Published in International journal of molecular sciences (01.06.2023)
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rbFOX1/MBNL1 competition for CCUG RNA repeats binding contributes to myotonic dystrophy type 1/type 2 differences
Sellier, Chantal, Cerro-Herreros, Estefanía, Blatter, Markus, Freyermuth, Fernande, Gaucherot, Angeline, Ruffenach, Frank, Sarkar, Partha, Puymirat, Jack, Udd, Bjarne, Day, John W, Meola, Giovanni, Bassez, Guillaume, Fujimura, Harutoshi, Takahashi, Masanori P, Schoser, Benedikt, Furling, Denis, Artero, Ruben, Allain, Frédéric H T, Llamusi, Beatriz, Charlet-Berguerand, Nicolas
Published in Nature communications (22.05.2018)
Published in Nature communications (22.05.2018)
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In vivo discovery of a peptide that prevents CUG-RNA hairpin formation and reverses RNA toxicity in myotonic dystrophy models
GarcÃa-López, Amparo, LlamusÃ, Beatriz, Orzáez, Mar, Pérez-Payá, Enrique, Artero, Ruben D
Published in Proceedings of the National Academy of Sciences - PNAS (19.07.2011)
Published in Proceedings of the National Academy of Sciences - PNAS (19.07.2011)
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Protective effects of mirtazapine in mice lacking the Mbnl2 gene in forebrain glutamatergic neurons: Relevance for myotonic dystrophy 1
Ramon-Duaso, Carla, Rodríguez-Morató, Jose, Selma-Soriano, Estela, Fernández-Avilés, Cristina, Artero, Rubén, de la Torre, Rafael, Pozo, Óscar J., Robledo, Patricia
Published in Neuropharmacology (15.06.2020)
Published in Neuropharmacology (15.06.2020)
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Bioengineered in vitro 3D model of myotonic dystrophy type 1 human skeletal muscle
Fernández-Garibay, Xiomara, Ortega, María A, Cerro-Herreros, Estefanía, Comelles, Jordi, Martínez, Elena, Artero, Rubén, Fernández-Costa, Juan M, Ramón-Azcón, Javier
Published in Biofabrication (01.07.2021)
Published in Biofabrication (01.07.2021)
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Targeting RNA structure in SMN2 reverses spinal muscular atrophy molecular phenotypes
Garcia-Lopez, Amparo, Tessaro, Francesca, Jonker, Hendrik R A, Wacker, Anna, Richter, Christian, Comte, Arnaud, Berntenis, Nikolaos, Schmucki, Roland, Hatje, Klas, Petermann, Olivier, Chiriano, Gianpaolo, Perozzo, Remo, Sciarra, Daniel, Konieczny, Piotr, Faustino, Ignacio, Fournet, Guy, Orozco, Modesto, Artero, Ruben, Metzger, Friedrich, Ebeling, Martin, Goekjian, Peter, Joseph, Benoît, Schwalbe, Harald, Scapozza, Leonardo
Published in Nature communications (23.05.2018)
Published in Nature communications (23.05.2018)
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Proof of concept of peptide-linked blockmiR-induced MBNL functional rescue in myotonic dystrophy type 1 mouse model
Overby, Sarah J., Cerro-Herreros, Estefanía, González-Martínez, Irene, Varela, Miguel A., Seoane-Miraz, David, Jad, Yahya, Raz, Richard, Møller, Thorleif, Pérez-Alonso, Manuel, Wood, Matthew J., Llamusí, Beatriz, Artero, Rubén
Published in Molecular therapy. Nucleic acids (08.03.2022)
Published in Molecular therapy. Nucleic acids (08.03.2022)
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