Onasemnogene abeparvovec gene therapy for symptomatic infantile-onset spinal muscular atrophy type 1 (STR1VE-EU): an open-label, single-arm, multicentre, phase 3 trial
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Published in Lancet neurology (01.10.2021)
Published in Lancet neurology (01.10.2021)
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G.P.170
Pasanisi, M.B, Vai, S, Baranello, G, Maggi, L, Moroni, I, Arnoldi, M.T, Bussolino, C, Brenna, G, Bianchi, M.L, Morandi, L
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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G.P.311
Baranello, G, Morandi, L, Sansanelli, S, Savadori, P, Saredi, S, Pantaleoni, C, Balestri, P, Malandrini, A, Arnoldi, M.T, Chiapparini, L, Mora, M
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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G.P.170: Bone mineral density and body composition in 39 Duchenne muscular dystrophy patients: A two-years follow up
Pasanisi, M.B., Vai, S., Baranello, G., Maggi, L., Moroni, I., Arnoldi, M.T., Bussolino, C., Brenna, G., Bianchi, M.L., Morandi, L.
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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G.P.311: A new homozygous ISPD mutation is associated with either early limb-girdle or congenital muscular dystrophy within the same family depending on different levels of alpha-dystroglycan glycosylation
Baranello, G., Morandi, L., Sansanelli, S., Savadori, P., Saredi, S., Pantaleoni, C., Balestri, P., Malandrini, A., Arnoldi, M.T., Chiapparini, L., Mora, M.
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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