The innovative dimension of the research training programmes under H2020-MSCA-ITN1: a methodological approach to track, measure and analyse innovative aspects and provide policy-feedback conclusions. [version 1; peer review: 3 approved]
Bitsios, Ioannis, Martone, Fabrizio, Ricci, Riccardo, Arfi, Audrey
Published in F1000 research (01.01.2023)
Published in F1000 research (01.01.2023)
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Journal Article
The innovative dimension of the research training programmes under H2020-MSCA-ITN: a methodological approach to track, measure and analyse innovative aspects and provide policy-feedback conclusions
Bitsios, Ioannis, Martone, Fabrizio, Ricci, Riccardo, Arfi, Audrey
Published in F1000 research (2023)
Published in F1000 research (2023)
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Journal Article
Neuroinflammatory and oxidative stress phenomena in MPS IIIA mouse model: The positive effect of long-term aspirin treatment
Arfi, Audrey, Richard, Magali, Gandolphe, Christelle, Bonnefont-Rousselot, Dominique, Thérond, Patrice, Scherman, Daniel
Published in Molecular genetics and metabolism (01.05.2011)
Published in Molecular genetics and metabolism (01.05.2011)
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Induced secretion of β-hexosaminidase by human brain endothelial cells: A novel approach in Sandhoff disease?
Batista, Lionel, Miller, Florence, Clave, Céline, Arfi, Audrey, Douillard-Guilloux, Gaëlle, Couraud, Pierre-Olivier, Caillaud, Catherine
Published in Neurobiology of disease (01.03.2010)
Published in Neurobiology of disease (01.03.2010)
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Bicistronic lentiviral vector corrects β-hexosaminidase deficiency in transduced and cross-corrected human Sandhoff fibroblasts
Arfi, Audrey, Bourgoin, Christophe, Basso, Luisa, Emiliani, Carla, Tancini, Brunella, Chigorno, Vanna, Li, Yu-Teh, Orlacchio, Aldo, Poenaru, Livia, Sonnino, Sandro, Caillaud, Catherine
Published in Neurobiology of disease (01.11.2005)
Published in Neurobiology of disease (01.11.2005)
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Storage correction in cells of patients suffering from mucopolysaccharidoses types IIIA and VII after treatment with genistein and other isoflavones
Arfi, Audrey, Richard, Magali, Gandolphe, Christelle, Scherman, Daniel
Published in Journal of inherited metabolic disease (01.02.2010)
Published in Journal of inherited metabolic disease (01.02.2010)
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Journal Article
Reversion of the biochemical defects in murine embryonic Sandhoff neurons using a bicistronic lentiviral vector encoding hexosaminidase [alpha] and [beta]
Arfi, Audrey, Zisling, Rivka, Emmanuel, Richard, Batista, Lionel, Poenaru, Livia, Futerman, Anthony H, Caillaud, Catherine
Published in Journal of neurochemistry (01.03.2006)
Published in Journal of neurochemistry (01.03.2006)
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Journal Article
Reversion of the biochemical defects in murine embryonic Sandhoff neurons using a bicistronic lentiviral vector encoding hexosaminidase α and β
Arfi, Audrey, Zisling, Rivka, Richard, Emmanuel, Batista, Lionel, Poenaru, Livia, Futerman, Anthony H., Caillaud, Catherine
Published in Journal of neurochemistry (01.03.2006)
Published in Journal of neurochemistry (01.03.2006)
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Journal Article
870. Gene Transfer in the Sandhoff Murine Model Using Lentiviral Vectors
Arfi, Audrey, Bourgoin, Christophe, Basso, Luisa, Sonnino, Sandro, Poenaru, Livia, Caillaud, Catherine
Published in Molecular therapy (01.05.2004)
Published in Molecular therapy (01.05.2004)
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Identification of new markers for neurodegeneration process in the mouse model of Sly disease as revealed by expression profiling of selected genes
Richard, Magali, Arfı, Audrey, Rhinn, Hervé, Gandolphe, Christelle, Scherman, Daniel
Published in Journal of neuroscience research (15.11.2008)
Published in Journal of neuroscience research (15.11.2008)
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