Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutations: a follow-on phase 1 trial
Bennett, Jean, Prof, Wellman, Jennifer, MSc, Marshall, Kathleen A, COT, McCague, Sarah, BA, Ashtari, Manzar, PhD, DiStefano-Pappas, Julie, BA, Elci, Okan U, PhD, Chung, Daniel C, DO, Sun, Junwei, MSc, Wright, J Fraser, PhD, Cross, Dominique R, MPH, Aravand, Puya, BA, Cyckowski, Laura L, BA, Bennicelli, Jeannette L, PhD, Mingozzi, Federico, PhD, Auricchio, Alberto, MD, Pierce, Eric A, MD, Ruggiero, Jason, MD, Leroy, Bart P, Prof, Simonelli, Francesca, Prof, High, Katherine A, MD, Maguire, Albert M, Prof
Published in The Lancet (British edition) (13.08.2016)
Published in The Lancet (British edition) (13.08.2016)
Get full text
Journal Article
Rescue of retinal ganglion cells in optic nerve injury using cell-selective AAV mediated delivery of SIRT1
Ross, Ahmara G, McDougald, Devin S, Khan, Reas S, Duong, Thu T, Dine, Kimberly E, Aravand, Puya, Bennett, Jean, Chavali, Venkata Ramana Murthy, Shindler, Kenneth S
Published in Gene therapy (01.05.2021)
Published in Gene therapy (01.05.2021)
Get full text
Journal Article
The Role of the Human Visual Cortex in Assessment of the Long-Term Durability of Retinal Gene Therapy in Follow-on RPE65 Clinical Trial Patients
Ashtari, Manzar, PhD, Nikonova, Elena S., BA, Marshall, Kathleen A., COT, Young, Gloria J., BA, Aravand, Puya, BA, Pan, Wei, MS, Ying, Gui-shuang, PhD, Willett, Aimee E., BS, Mahmoudian, Mani, MD, Maguire, Albert M., MD, Bennett, Jean, MD, PhD
Published in Ophthalmology (Rochester, Minn.) (01.06.2017)
Published in Ophthalmology (Rochester, Minn.) (01.06.2017)
Get full text
Journal Article
Amelioration of Neurosensory Structure and Function in Animal and Cellular Models of a Congenital Blindness
Song, Ji Yun, Aravand, Puya, Nikonov, Sergei, Leo, Lanfranco, Lyubarsky, Arkady, Bennicelli, Jeannette L., Pan, Jieyan, Wei, Zhangyong, Shpylchak, Ivan, Herrera, Pamela, Bennett, Daniel J., Commins, Nicoletta, Maguire, Albert M., Pham, Jennifer, den Hollander, Anneke I., Cremers, Frans P.M., Koenekoop, Robert K., Roepman, Ronald, Nishina, Patsy, Zhou, Shangzhen, Pan, Wei, Ying, Gui-shuang, Aleman, Tomas S., de Melo, Jimmy, McNamara, Ilan, Sun, Junwei, Mills, Jason, Bennett, Jean
Published in Molecular therapy (06.06.2018)
Published in Molecular therapy (06.06.2018)
Get full text
Journal Article
Restoration of Vision and Retinal Responses After Adeno-Associated Virus-Mediated Optogenetic Therapy in Blind Dogs
Nikonov, Sergei, Aravand, Puya, Lyubarsky, Arkady, Nikonov, Roman, Luo, Angela J, Wei, Zhangyong, Maguire, Albert M, Phelps, Nicholas T, Shpylchak, Ivan, Willett, Keirnan, Aleman, Tomas S, Huckfeldt, Rachel M, Ramachandran, Pavitra S, Bennett, Jean
Published in Translational vision science & technology (23.05.2022)
Published in Translational vision science & technology (23.05.2022)
Get full text
Journal Article
Protocols for Visually Guided Navigation Assessment of Efficacy of Retina-Directed Cell or Gene Therapy in Canines
Aravand, Puya, Ramachandran, Pavitra S, Schpylchak, Ivan, Phelps, Nicholas T, Nikonov, Sergei, Bennett, Jean
Published in Frontiers in neuroscience (26.04.2017)
Published in Frontiers in neuroscience (26.04.2017)
Get full text
Journal Article
Cell-Specific Expression of Human SIRT1 by Gene Therapy Reduces Retinal Ganglion Cell Loss Induced by Elevated Intraocular Pressure
Yue, Jipeng, Khan, Reas S., Duong, Thu T., Dine, Kimberly E., Cui, Qi N., O’Neill, Nuala, Aravand, Puya, Liu, Tehui, Chaqour, Brahim, Shindler, Kenneth S., Ross, Ahmara G.
Published in Neurotherapeutics (01.04.2023)
Published in Neurotherapeutics (01.04.2023)
Get full text
Journal Article
Treatment Potential for LCA5-Associated Leber Congenital Amaurosis
Uyhazi, Katherine E, Aravand, Puya, Bell, Brent A, Wei, Zhangyong, Leo, Lanfranco, Serrano, Leona W, Pearson, Denise J, Shpylchak, Ivan, Pham, Jennifer, Vasireddy, Vidyullatha, Bennett, Jean, Aleman, Tomas S
Published in Investigative ophthalmology & visual science (19.05.2020)
Published in Investigative ophthalmology & visual science (19.05.2020)
Get full text
Journal Article
Plasticity of the human visual system after retinal gene therapy in patients with Leber's congenital amaurosis
Ashtari, Manzar, Zhang, Hui, Cook, Philip A, Cyckowski, Laura L, Shindler, Kenneth S, Marshall, Kathleen A, Aravand, Puya, Vossough, Arastoo, Gee, James C, Maguire, Albert M, Baker, Chris I, Bennett, Jean
Published in Science translational medicine (15.07.2015)
Published in Science translational medicine (15.07.2015)
Get more information
Journal Article
RGC and Vision Loss From Traumatic Optic Neuropathy Induced by Repetitive Closed Head Trauma Is Dependent on Timing and Force of Impact
Khan, Reas S, Ross, Ahmara G, Aravand, Puya, Dine, Kimberly, Selzer, Evan B, Shindler, Kenneth S
Published in Translational vision science & technology (2021)
Published in Translational vision science & technology (2021)
Get full text
Journal Article
Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutatons: a follow-on phase 1 trial
Bennett, Jean, Wellman, Jennifer, Marshall, Kathleen A, McCague, Sarah, Ashtari, Manzar, DiStefano-Pappas, Julie, Elci, Okan U, Chung, Daniel C, Sun, Junwei, Wright, J Fraser, Cross, Dominique R, Aravand, Puya, Cyckowski, Laura L, Bennicelli, Jeannette L, Mingozzi, Federico, Auricchio, Alberto, Pierce, Eric A, Ruggiero, Jason, Leroy, Bart P, Simonelli, Francesca, High, Katherine A, Maguire, Albert M
Published in The Lancet (British edition) (30.06.2016)
Published in The Lancet (British edition) (30.06.2016)
Get full text
Journal Article