Hepatic expression of GAA results in enhanced enzyme bioavailability in mice and non-human primates
Costa-Verdera, Helena, Collaud, Fanny, Riling, Christopher R, Sellier, Pauline, Nordin, Jayme M L, Preston, G Michael, Cagin, Umut, Fabregue, Julien, Barral, Simon, Moya-Nilges, Maryse, Krijnse-Locker, Jacomina, van Wittenberghe, Laetitia, Daniele, Natalie, Gjata, Bernard, Cosette, Jeremie, Abad, Catalina, Simon-Sola, Marcelo, Charles, Severine, Li, Mathew, Crosariol, Marco, Antrilli, Tom, Quinn, 3rd, William J, Gross, David A, Boyer, Olivier, Anguela, Xavier M, Armour, Sean M, Colella, Pasqualina, Ronzitti, Giuseppe, Mingozzi, Federico
Published in Nature communications (04.11.2021)
Published in Nature communications (04.11.2021)
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Journal Article
Hepatic expression of GAA results in enhanced enzyme bioavailability in mice and non-human primates
Costa-Verdera, Helena, Collaud, Fanny, Riling, Christopher, Sellier, Pauline, Nordin, Jayme, Preston, G. Michael, Cagin, Umut, Fabregue, Julien, Barral, Simon, Moya-Nilges, Maryse, Krijnse-Locker, Jacomina, van Wittenberghe, Laetitia, Daniele, Natalie, Gjata, Bernard, Cosette, Jeremie, Abad, Catalina, Simon-Sola, Marcelo, Charles, Severine, Li, Mathew, Crosariol, Marco, Antrilli, Tom, Quinn, William, Gross, David, Boyer, Olivier, Anguela, Xavier, Armour, Sean, Colella, Pasqualina, Ronzitti, Giuseppe, Mingozzi, Federico
Published in Nature communications (04.11.2021)
Published in Nature communications (04.11.2021)
Get full text
Journal Article