CRISPR/Cas9-Induced (CTG⋅CAG)n Repeat Instability in the Myotonic Dystrophy Type 1 Locus: Implications for Therapeutic Genome Editing
van Agtmaal, Ellen L., André, Laurène M., Willemse, Marieke, Cumming, Sarah A., van Kessel, Ingeborg D.G., van den Broek, Walther J.A.A., Gourdon, Geneviève, Furling, Denis, Mouly, Vincent, Monckton, Darren G., Wansink, Derick G., Wieringa, Bé
Published in Molecular therapy (04.01.2017)
Published in Molecular therapy (04.01.2017)
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Journal Article
Recovery in the Myogenic Program of Congenital Myotonic Dystrophy Myoblasts after Excision of the Expanded (CTG) n Repeat
André, Laurène M, van Cruchten, Remco T P, Willemse, Marieke, Bezstarosti, Karel, Demmers, Jeroen A A, van Agtmaal, Ellen L, Wansink, Derick G, Wieringa, Bé
Published in International journal of molecular sciences (13.11.2019)
Published in International journal of molecular sciences (13.11.2019)
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Journal Article
Abnormalities in Skeletal Muscle Myogenesis, Growth, and Regeneration in Myotonic Dystrophy
André, Laurène M, Ausems, C Rosanne M, Wansink, Derick G, Wieringa, Bé
Published in Frontiers in neurology (28.05.2018)
Published in Frontiers in neurology (28.05.2018)
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Journal Article
Trinucleotide-repeat expanded and normal DMPK transcripts contain unusually long poly(A) tails despite differential nuclear residence
Gudde, Anke E.E.G., van Kessel, Ingeborg D.G., André, Laurène M., Wieringa, Bé, Wansink, Derick G.
Published in Biochimica et biophysica acta. Gene regulatory mechanisms (01.06.2017)
Published in Biochimica et biophysica acta. Gene regulatory mechanisms (01.06.2017)
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Journal Article