Sex Difference Leads to Differential Gene Expression Patterns and Therapeutic Efficacy in Mucopolysaccharidosis IVA Murine Model Receiving AAV8 Gene Therapy
Piechnik, Matthew, Amendum, Paige C, Sawamoto, Kazuki, Stapleton, Molly, Khan, Shaukat, Fnu, Nidhi, Álvarez, Victor, Pachon, Angelica Maria Herreño, Danos, Olivier, Bruder, Joseph T, Karumuthil-Melethil, Subha, Tomatsu, Shunji
Published in International journal of molecular sciences (21.10.2022)
Published in International journal of molecular sciences (21.10.2022)
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Glycosaminoglycans as Biomarkers for Mucopolysaccharidoses and Other Disorders
Amendum, Paige C, Khan, Shaukat, Yamaguchi, Seiji, Kobayashi, Hironori, Ago, Yasuhiko, Suzuki, Yasuyuki, Celik, Betul, Rintz, Estera, Hossain, Jobayer, Xiao, Wendi, Tomatsu, Shunji
Published in Diagnostics (Basel) (28.08.2021)
Published in Diagnostics (Basel) (28.08.2021)
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