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Published in Tropical animal health and production (01.08.2000)
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Glucocerebrosidase mutations in subjects with parkinsonism
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Schoser, B., Kishnani, P., Bratkovic, D., Byrne, B., Clemens, P., Goker-Alpan, O., Ming, X., Roberts, M., Schwenkreis, P., Sivakumar, K., van der Ploeg, A., Sitaraman, S., Barth, J., Lagast, H., Mozaffar, T.
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Schoser, B., Barohn, R., Byrne, B., Goker-Alpan, O., Kishnani, P., Ladha, S., Laforet, P., Mengel, E., Pena, L., Sacconi, S., Straub, V., Trivedi, J., Van Damme, P., van der Ploeg, A., Vissing, J., Young, P., Haack, K., Ivanina, I., Wang, Y., Dimachkie, M.
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Schoser, B., Barohn, R., Byrne, B., Goker-Alpan, O., Kishnani, P., Ladha, S., Laforet, P., Mengel, E., Pena, L., Sacconi, S., Straub, V., Trivedi, J., Van Damme, P., van der Ploeg, A., Vissing, J., Young, P., Haack, K., Ivanina, I., Wang, Y., Dimachkie, M.
Published in Neuromuscular disorders : NMD (01.10.2020)
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DePaolo, John, Goker-Alpan, Ozlem, Samaddar, Ted, Lopez, Grisel, Sidransky, Ellen
Published in Movement disorders (15.08.2009)
Published in Movement disorders (15.08.2009)
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NEW THERAPEUTIC APPROACHES AND THEIR READOUT: O.20Results from ATB200-02: first-in-human, open-label, phase 1/2 study of ATB200 co-administered with AT2221 for Pompe disease
Schoser, B., Bratkovic, D., Byrne, B., Clemens, P., Geberhiwot, T., Goker-Alpan, O., Kishnani, P., Ming, X., Mozaffar, T., Schwenkreis, P., Sivakumar, K., van der Ploeg, A., Wright, J., Johnson, F., Sitaraman, S., Barth, J., Sathe, S., Roberts, M.
Published in Neuromuscular disorders : NMD (01.10.2018)
Published in Neuromuscular disorders : NMD (01.10.2018)
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P.69NEO1 and NEO-EXT studies: exploratory efficacy of repeat avalglucosidase alfa dosing for up to 5 years in participants with late-onset Pompe disease (LOPD)
Schoser, B., Barohn, R., Byrne, B., Goker-Alpan, O., Kishnani, P., Ladha, S., Laforêt, P., Mengel, K., Pena, L., Sacconi, S., Straub, V., Trivedi, J., Van Damme, P., van der Ploeg, A., Vissing, J., Young, P., An Haack, K., Liu, K., Fraser, P., Dimachkie, M.
Published in Neuromuscular disorders : NMD (01.10.2019)
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P.025 Efficacy and safety results of the avalglucosidase alfa phase 3 COMET trial in participants with late-onset Pompe disease (LOPD)
Tarnopolsky, M, Attarian, S, Borges, J, Bouhour, F, Choi, Y, Clemens, P, Day, J, Díaz-Manera, J, Erdem-Ozdamar, S, Goker-Alpan, O, Illarioshkin, S, Kishnani, PS, Kostera-Pruszczyk, A, Kushlaf, H, Ladha, S, Mozaffar, T, Roberts, M, Straub, V, Toscano, A, van der Ploeg, AT, An Haack, K, Hug, C, Huynh-Ba, O, Johnson, J, Zhou, T, Dimachkie, MM, Schoser, B
Published in Canadian journal of neurological sciences (01.11.2021)
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'Educated' dendritic cells act as messengers from memory to naive T helper cells
Alpan, Oral, Bachelder, Eric, Isil, Eda, Arnheiter, Heinz, Matzinger, Polly
Published in Nature immunology (01.06.2004)
Published in Nature immunology (01.06.2004)
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Mehta, A, Kuter, DJ, Salek, SS, Belmatoug, N, Bembi, B, Bright, J, Dahl, SV, Deodato, F, Di Rocco, M, Goker-Alpan, O, Hughes, DA, Lukina, EA, Machaczka, M, Mengel, E, Nagral, A, Nakamura, K, Narita, A, Oliveri, B, Pastores, G, Perez-Lopez, J, Ramaswami, U, Schwartz, IV, Szer, J, Weinreb, NJ, Zimran, A
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Goker-Alpan, Ozlem, Longo, Nicola, McDonald, Marie, Shankar, Suma P, Schiffmann, Raphael, Chang, Peter, Shen, Yinghua, Pano, Arian
Published in Drug design, development and therapy (01.01.2016)
Published in Drug design, development and therapy (01.01.2016)
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T.P.24: Alglucosidase alfa reduces lysosomal glycogen in skeletal muscle biopsies of patients with late-onset Pompe disease (LOPD)
Thurberg, B.L., van der Ploeg, A., Kissel, J.T., Schoser, B., Pestronk, A., Barohn, R.J., Goker-Alpan, O., Mozaffar, T., Pena, L.D.M., Simmons, Z., Straub, V., Young, P., Bjartmar, C.
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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A 6-month, multicenter, open-label study of fixed dose naproxen/esomeprazole in adolescent patients with juvenile idiopathic arthritis
Lovell, Daniel J, Dare, Jason A, Francis-Sedlak, Megan, Ball, Julie, LaMoreaux, Brian D, Von Scheven, Emily, Reinhardt, Adam, Jerath, Rita, Alpan, Oral, Gupta, Ramesh, Goldsmith, Donald, Zeft, Andrew, Naddaf, Henry, Gottlieb, Beth, Jung, Lawrence, Holt, Robert J
Published in Pediatric Rheumatology (26.06.2018)
Published in Pediatric Rheumatology (26.06.2018)
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Evaluation of the efficacy and safety of three dosing regimens of agalsidase alfa enzyme replacement therapy in adults with Fabry disease
Goláň, Lubor, Goker-Alpan, Ozlem, Holida, Myrl, Kantola, Ikka, Klopotowski, Mariusz, Kuusisto, Johanna, Linhart, Aleš, Musial, Jacek, Nicholls, Kathleen, Gonzalez-Rodriguez, Derlis, Sharma, Reena, Vujkovac, Bojan, Chang, Peter, Wijatyk, Anna
Published in Drug design, development and therapy (2015)
Published in Drug design, development and therapy (2015)
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