P1543: MITAPIVAT DECREASES THE NEED FOR TRANSFUSIONS SECONDARY TO POORLY TOLERATED ANEMIA AND ACUTE EVENTS COMPARED TO PLACEBO IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY WHO ARE NOT REGULARLY TRANSFUSED
Al‐Samkari, H., Morales‐Arias, J., Xu, R., Beynon, V., Grace, R. F.
Published in HemaSphere (23.06.2022)
Published in HemaSphere (23.06.2022)
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Journal Article
P1522: LONG‐TERM EFFICACY AND SAFETY OF THE ORAL PYRUVATE KINASE ACTIVATOR MITAPIVAT IN ADULTS WITH NON–TRANSFUSION‐DEPENDENT ALPHA‐ OR BETA‐THALASSEMIA
Kuo, K. H. M., Layton, D. M., Lal, A., Al‐Samkari, H., Bhatia, J., Kosinski, P. A., Tong, B., Lynch, M., Uhlig, K., Vichinsky, E. P.
Published in HemaSphere (23.06.2022)
Published in HemaSphere (23.06.2022)
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P1735: IMPROVEMENTS IN PATIENT‐REPORTED OUTCOMES IN MITAPIVAT‐TREATED PATIENTS WITH PYRUVATE KINASE DEFICIENCY: A DESCRIPTIVE ANALYSIS FROM THE PHASE 3 ACTIVATE TRIAL
Kuo, K. H., Grace, R. F., Beers, E. J., Barcellini, W., Glenthøj, A., Holzhauer, S., Patel, P., Beynon, V., Li, J., Zagadailov, E., Al‐Samkari, H.
Published in HemaSphere (23.06.2022)
Published in HemaSphere (23.06.2022)
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P112: ENERGIZE AND ENERGIZE‐T: TWO PHASE 3, RANDOMIZED, DOUBLE‐BLIND, PLACEBO‐CONTROLLED STUDIES OF MITAPIVAT IN ADULTS WITH NON‐‐TRANSFUSION‐DEPENDENT OR TRANSFUSION‐DEPENDENT ALPHA‐ OR BETA‐THALASSEMIA
Kuo, K, Layton, D, Al‐Samkari, H, Kattamis, A, Sheth, S, Taher, A, Viprakasit, V, Chamberlain, C, Czapla, L, Gheuens, S, Lynch, M, Tong, B, Uhlig, K, Cappellini, M
Published in HemaSphere (01.01.2022)
Published in HemaSphere (01.01.2022)
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Journal Article
S116: LONG‐TERM EFFICACY AND SAFETY OF THE ORAL PYRUVATE KINASE ACTIVATOR MITAPIVAT IN ADULTS WITH NON—TRANSFUSION‐DEPENDENT ALPHA‐ OR BETA‐THALASSEMIA
Kuo, K, Layton, D, Lal, A, Al‐Samkari, H, Bhatia, J, Kosinski, P, Tong, B, Lynch, M, Uhlig, K, Vichinsky, E
Published in HemaSphere (01.01.2022)
Published in HemaSphere (01.01.2022)
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Journal Article
P1544: BONE MINERAL DENSITY REMAINS STABLE IN PYRUVATE KINASE DEFICIENCY PATIENTS RECEIVING LONG‐TERM TREATMENT WITH MITAPIVAT
Al‐Samkari, H., Grace, R. F., Glenthøj, A., Andres, O., Barcellini, W., Galactéros, F., Kuo, K. H. M., Layton, D. M., Morado Arias, M., Viprakasit, V., Dong, Y., Tai, F., Grekas, L., Khoja, K., Gheuens, S., McGee, B., Porter, J. B., Beers, E. J.
Published in HemaSphere (23.06.2022)
Published in HemaSphere (23.06.2022)
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Journal Article
P1548: LONG‐TERM TREATMENT WITH ORAL MITAPIVAT IS ASSOCIATED WITH NORMALIZATION OF HEMOGLOBIN LEVELS IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY
Barcellini, W., Grace, R. F., Al‐Samkari, H., Glenthøj, A., Rothman, J. A., Morado Arias, M., Layton, D. M., Andres, O., DiBacco, M., Hawkins, P., Judge, M. P., Tai, F., Morales‐Arias, J., Beynon, V., Beers, E. J.
Published in HemaSphere (23.06.2022)
Published in HemaSphere (23.06.2022)
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Journal Article
P1545: DURABILITY OF HEMOGLOBIN RESPONSE AND REDUCTION IN TRANSFUSION BURDEN IS MAINTAINED OVER TIME IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY TREATED WITH MITAPIVAT IN A LONG‐TERM EXTENSION STUDY
Grace, R. F., Glenthøj, A., Barcellini, W., Verhovsek, M., Rothman, J. A., Morado Arias, M., Layton, D. M., Andres, O., Galactéros, F., Beers, E. J., Onodera, K., Viprakasit, V., Chonat, S., Porter, J. B., Judge, M. P., Kosinski, P. A., Hawkins, P., Gheuens, S., Xu, R., McGee, B., Beynon, V., Al‐Samkari, H.
Published in HemaSphere (23.06.2022)
Published in HemaSphere (23.06.2022)
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Journal Article
Perioperative thrombocytopenia: evidence, evaluation, and emerging therapies
Nagrebetsky, A., Al-Samkari, H., Davis, N.M., Kuter, D.J., Wiener-Kronish, J.P.
Published in British journal of anaesthesia : BJA (01.01.2019)
Published in British journal of anaesthesia : BJA (01.01.2019)
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Journal Article
Cancer and thrombosis: new insights to an old problem
Leiva, O., Newcomb, R., Connors, J.M., Al-Samkari, H.
Published in Journal de médecine vasculaire (01.11.2020)
Published in Journal de médecine vasculaire (01.11.2020)
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RESULTS FROM A PHASE 2 STUDY OF MITAPIVAT IN ADULTS WITH NON–TRANSFUSION-DEPENDENT ALPHA- OR BETA-THALASSEMIA
Kuo, KH, Layton, DM, Lal, A, Al-Samkari, H, Bhatia, J, Tong, B, Lynch, M, Uhlig, K, Vichinsky, EP
Published in Hematology, Transfusion and Cell Therapy (01.10.2021)
Published in Hematology, Transfusion and Cell Therapy (01.10.2021)
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Journal Article
ENERGIZE AND ENERGIZE-T: TWO PHASE 3, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED STUDIES OF MITAPIVAT IN ADULTS WITH NON–TRANSFUSION-DEPENDENT OR TRANSFUSION-DEPENDENT ALPHA- OR BETA-THALASSEMIA
Kuo, KH, Layton, DM, Al-Samkari, H, Kattamis, A, Sheth, S, Taher, A, Viprakasit, V, Chamberlain, CX, Czapla, L, Gheuens, S, Jiang, L, Lynch, M, Tong, B, Uhlig, K, Cappellini, MD
Published in Hematology, Transfusion and Cell Therapy (01.10.2021)
Published in Hematology, Transfusion and Cell Therapy (01.10.2021)
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Journal Article
1628TiP Romiplostim for chemotherapy-induced thrombocytopenia (CIT) in solid tumors: Two phase III, international, randomized controlled trials (RCT)
Al-Samkari, H., Geredeli, C., Arslan, C., Korantzis, I., Dogu, G.G., Nechaeva, M., Salgado Fernandez, M., Gonzalez Astorga, B., Yordanov, V.I., Ciuleanu, T-E., Bowers, C., Armas, A., Scotté, F., Camargo, J.F.C., Munoz Sanchez-Miguel, C.G., Bunn, P.A., Kuter, D., Soff, G.A.
Published in Annals of oncology (01.09.2022)
Published in Annals of oncology (01.09.2022)
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Journal Article
WS01.6 Antifibrinolytics therapy for treatment of hemoptysis in adults with cystic fibrosis; does it affect lung function?
Cardoni, L., Perkins, R., Shin, K., Al-Samkari, H., Pighetti, E., Rits, S., McMahon, L., Connors, J., Uluer, A.
Published in Journal of cystic fibrosis (01.06.2020)
Published in Journal of cystic fibrosis (01.06.2020)
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