rAAV2 5 gene-targeting to rods:dose-dependent efficiency and complications associated with different promoters
BELTRAN, W. A, BOYE, S. L, BOYE, S. E, CHIODO, V. A, LEWIN, A. S, HAUSWIRTH, W. W, AGUIRRE, G. D
Published in Gene therapy (01.09.2010)
Published in Gene therapy (01.09.2010)
Get full text
Journal Article
Targeting gene expression to cones with human cone opsin promoters in recombinant AAV
Komáromy, A M, Alexander, J J, Cooper, A E, Chiodo, V A, Glushakova, L G, Acland, G M, Hauswirth, W W, Aguirre, G D
Published in Gene therapy (01.07.2008)
Published in Gene therapy (01.07.2008)
Get full text
Journal Article
A Linkage Map of the Canine Genome
Mellersh, Cathryn S., Langston, Amelia A., Acland, Gregory M., Fleming, Melissa A., Ray, Kunal, Wiegand, Neil A., Francisco, Leigh V., Gibbs, Mark, Aguirre, Gustavo D., Ostrander, Elaine A.
Published in Genomics (San Diego, Calif.) (15.12.1997)
Published in Genomics (San Diego, Calif.) (15.12.1997)
Get full text
Journal Article
A Marker Set for Construction of a Genetic Map of the Silver Fox (Vulpes vulpes)
Kukekova, A. V., Trut, L. N., Oskina, I. N., Kharlamova, A. V., Shikhevich, S. G., Kirkness, E. F., Aguirre, G. D., Acland, G. M.
Published in The Journal of heredity (01.05.2004)
Published in The Journal of heredity (01.05.2004)
Get full text
Journal Article
Inheritance, biochemical abnormalities, and clinical features of feline Mucolipidosis II: the first animal model of human I-cell disease
Mazrier, H, Van Hoeven, M, Wang, P, Knox, V.W, Aguirre, G.D, Holt, E, Wiemelt, S.P, Sleeper, M.M, Hubler, M, Haskins, M.E
Published in The Journal of heredity (01.09.2003)
Published in The Journal of heredity (01.09.2003)
Get full text
Journal Article
Gene therapy restores vision in a canine model of childhood blindness
Bennett, Jean, Acland, Gregory M, Aguirre, Gustavo D, Ray, Jharna, Zhang, Qi, Aleman, Tomas S, Cideciyan, Artur V, Pearce-Kelling, Susan E, Anand, Vibha, Zeng, Yong, Maguire, Albert M, Jacobson, Samuel G, Hauswirth, William W
Published in Nature genetics (01.05.2001)
Published in Nature genetics (01.05.2001)
Get full text
Journal Article
A Novel Retinal Degeneration Locus Identified by Linkage and Comparative Mapping of Canine Early Retinal Degeneration
Acland, Gregory M., Ray, Kunal, Mellersh, Cathryn S., Langston, Amelia A., Rine, Jasper, Ostrander, Elaine A., Aguirre, Gustavo D.
Published in Genomics (San Diego, Calif.) (15.07.1999)
Published in Genomics (San Diego, Calif.) (15.07.1999)
Get full text
Journal Article
Implications of retinal effects observed in chronic toxicity studies on the clinical development of a CNS-active drug candidate
Eichenbaum, G., Zhou, J., Kelley, M.F., Roosen, W., Costa-Giomi, P., Louden, C., Di Prospero, N.A., Pandina, G., Singh, J.B., Ford, L., Moyer, J.A., Nork, T.M., Ver Hoeve, J.N., Aguirre, G.D.
Published in Regulatory toxicology and pharmacology (01.07.2014)
Published in Regulatory toxicology and pharmacology (01.07.2014)
Get full text
Journal Article
Cloning of the Canine β-Glucuronidase cDNA, Mutation Identification in Canine MPS VII, and Retroviral Vector-Mediated Correction of MPS VII Cells
Ray, Jharna, Bouvet, Alain, DeSanto, Christopher, Fyfe, John C., Xu, Danbin, Wolfe, John H., Aguirre, Gustavo D., Patterson, Donald F., Haskins, Mark E., Henthorn, Paula S.
Published in Genomics (San Diego, Calif.) (01.03.1998)
Published in Genomics (San Diego, Calif.) (01.03.1998)
Get full text
Journal Article
Fine Mapping of Canine XLPRA Establishes Homology of the Human and Canine RP3 Intervals
Zhang, Qi, Acland, Gregory M, Zangerl, Barbara, Johnson, Jennifer L, Mao, Zuohua, Zeiss, Caroline J, Ostrander, Elaine A, Aguirre, Gustavo D
Published in Investigative ophthalmology & visual science (01.10.2001)
Get full text
Published in Investigative ophthalmology & visual science (01.10.2001)
Journal Article
Targeting gene expression to cones with human cone opsin promoters in recombinant AAV
Komaromy, A.M, Alexander, J.J, Cooper, A.E, Chiodo, V.A, Acland, G.M, Hauswirth, W.W, Aguirre, G.D
Published in Gene therapy (01.12.2011)
Published in Gene therapy (01.12.2011)
Get full text
Journal Article
Congenital stationary night blindness in the dog: common mutation in the RPE65 gene indicates founder effect
Aguirre, G D, Baldwin, V, Pearce-Kelling, S, Narfström, K, Ray, K, Acland, G M
Published in Molecular vision (30.10.1998)
Get full text
Published in Molecular vision (30.10.1998)
Journal Article