Efficacy and safety of givosiran for acute hepatic porphyria: 24‐month interim analysis of the randomized phase 3 ENVISION study
Ventura, Paolo, Bonkovsky, Herbert L., Gouya, Laurent, Aguilera‐Peiró, Paula, Montgomery Bissell, D., Stein, Penelope E., Balwani, Manisha, Anderson, D. Karl E., Parker, Charles, Kuter, David J., Monroy, Susana, Oh, Jeeyoung, Ritchie, Bruce, Ko, John J., Hua, Zhaowei, Sweetser, Marianne T., Sardh, Eliane
Published in Liver international (01.01.2022)
Published in Liver international (01.01.2022)
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Solar capillaritis during hydrochlorothiazide treatment: A case report
Alamon‐Reig, Francesc, Luque‐Luna, Mar, Serra‐García, Laura, Martí‐Martí, Ignasi, Riera‐Monroig, Josep, Fuertes, Irene, Aguilera‐Peiró, Paula
Published in Photodermatology, photoimmunology & photomedicine (01.01.2023)
Published in Photodermatology, photoimmunology & photomedicine (01.01.2023)
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Twelve-year follow-up of bone marrow transplantation in congenital erythropoietic porphyria: lessons learned from a challenging case
Díaz-Calvillo, Pablo, Rodríguez-Pozo, Juan Ángel, Martínez-López, Antonio, Aguilera-Peiró, Paula, Díaz-de-Heredia, Cristina, Arias-Santiago, Salvador, Tercedor-Sánchez, Jesus
Published in Clinical and experimental dermatology (19.09.2023)
Published in Clinical and experimental dermatology (19.09.2023)
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Successful treatment of facial cutaneous leishmaniasis with photodynamic therapy
Alamon-Reig, Francesc, Martí-Martí, Ignasi, Loughlin, Constanza Riquelme-Mc, Garcia, Adriana, Carrera, Cristina, Aguilera-Peiró, Paula
Published in Indian journal of dermatology, venereology, and leprology (01.09.2022)
Published in Indian journal of dermatology, venereology, and leprology (01.09.2022)
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Intralesional Candida Antigen Immunotherapy for the Treatment of Recalcitrant and Multiple Warts in Children
Muñoz Garza, Fania Z., Roé Crespo, Esther, Torres Pradilla, Mauricio, Aguilera Peirò, Paula, Baltà Cruz, Susana, Hernández Ruiz, María Eugenia, Baselga Torres, Eulàlia
Published in Pediatric dermatology (01.11.2015)
Published in Pediatric dermatology (01.11.2015)
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Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria
Balwani, Manisha, Sardh, Eliane, Ventura, Paolo, Peiró, Paula Aguilera, Rees, David C, Stölzel, Ulrich, Bissell, D. Montgomery, Bonkovsky, Herbert L, Windyga, Jerzy, Anderson, Karl E, Parker, Charles, Silver, Samuel M, Keel, Siobán B, Wang, Jiaan-Der, Stein, Penelope E, Harper, Pauline, Vassiliou, Daphne, Wang, Bruce, Phillips, John, Ivanova, Aneta, Langendonk, Janneke G, Kauppinen, Raili, Minder, Elisabeth, Horie, Yutaka, Penz, Craig, Chen, Jihong, Liu, Shangbin, Ko, John J, Sweetser, Marianne T, Garg, Pushkal, Vaishnaw, Akshay, Kim, Jae B, Simon, Amy R, Gouya, Laurent
Published in The New England journal of medicine (11.06.2020)
Published in The New England journal of medicine (11.06.2020)
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Journal Article
S1170 Efficacy and Safety of Givosiran in Patients With Acute Hepatic Porphyria: 24-Month Interim Analysis of the Phase 3 ENVISION Randomized Clinical Trial
Bonkovsky, Herbert L., Ventura, Paolo, Gouya, Laurent, Peiró, Paula Aguilera, Bissell, D. Montgomery, Stein, Penelope E., Anderson, Karl E., Monroy, Susana, Kuter, David J., Oh, Jeeyoung, Ko, John J., Hua, Zhaowei, Sweetser, Marianne T., Sardh, Eliane
Published in The American journal of gastroenterology (01.10.2021)
Published in The American journal of gastroenterology (01.10.2021)
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Journal Article
Inside Front Cover
Ventura, Paolo, Bonkovsky, Herbert L, Gouya, Laurent, Paula Aguilera‐Peiró, D Montgomery Bissell, Stein, Penelope E, Balwani, Manisha, Anderson, D Karl E, Parker, Charles, Kuter, David J, Monroy, Susana, Oh, Jeeyoung, Ritchie, Bruce, Ko, John J, Hua, Zhaowei, Sweetser, Marianne T, Sardh, Eliane
Published in Liver international (01.01.2022)
Published in Liver international (01.01.2022)
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Journal Article
Inside Front Cover
Ventura, Paolo, Bonkovsky, Herbert L., Gouya, Laurent, Aguilera‐Peiró, Paula, Montgomery Bissell, D., Stein, Penelope E., Balwani, Manisha, Anderson, D. Karl E., Parker, Charles, Kuter, David J., Monroy, Susana, Oh, Jeeyoung, Ritchie, Bruce, Ko, John J., Hua, Zhaowei, Sweetser, Marianne T., Sardh, Eliane
Published in Liver international (01.01.2022)
Published in Liver international (01.01.2022)
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Journal Article
S1154 Clinical Outcomes in Patients With Acute Hepatic Porphyria Treated With Givosiran Who Stopped Hemin Prophylaxis at Study Entry: A Post Hoc Analysis of Data From the Phase 3 ENVISION Study Through Month 12
Bonkovsky, Herbert L., Balwani, Manisha, Sardh, Eliane, Gouya, Laurent, Rees, David C., Stein, Penelope, Stölzel, Ulrich, Peiro, Paula Aguilera, Bissell, D. Montgomery, Keel, Sioban, Parker, Charles, Silver, Samuel, Windyga, Jerzy, D’Avola, Delia, Ross, Gayle, Stewart, Peter, Ritchie, Bruce, Oh, Jeeyoung, Harper, Pauline, Wang, Jiaan-Der, Langendonk, Janneke, Ivanova, Aneta, Horie, Yutaka, Anderson, Karl E., Minder, Elisabeth, Vassiliou, Daphne, Kubisch, Ilja, Guillen-Navarro, Encarna, Coman, David, Goto, Yoshie, Kuo, Hung-Chou, Hua, Zoe, Simon, Amy, Ko, John J., Ventura, Paolo
Published in The American journal of gastroenterology (01.10.2020)
Published in The American journal of gastroenterology (01.10.2020)
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Journal Article
S1169 Twelve-Month Interim Analysis of Efficacy and Safety of Givosiran, an Investigational RNAi Therapeutic for Acute Hepatic Porphyria, in the ENVISION Open Label Extension
Sardh, Eliane, Balwani, Manisha, Rees, David C., Stein, Penelope, Stölzel, Ulrich, Peiro, Paula Aguilera, Bissell, D. Montgomery, Bonkovsky, Herbert L., Keel, Sioban, Parker, Charles, Phillips, John D., Silver, Samuel, Windyga, Jerzy, D’Avola, Delia, Ross, Gayle, Stewart, Peter, Ritchie, Bruce, Harper, Pauline, Wang, Jiaan-Der, Langendonk, Janneke, Ivanova, Aneta, Horie, Yutaka, Anderson, Karl E., Ventura, Paolo, Cappellini, Maria D., Vassiliou, Daphne, Monroy, Susana, Petrides, Petro E., Adachi, Tomohide, Kuter, David, Scalera, Sushama, Penz, Craig, Liu, Shangbin, Ko, John J., Simon, Amy, Gouya, Laurent
Published in The American journal of gastroenterology (01.10.2020)
Published in The American journal of gastroenterology (01.10.2020)
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Journal Article
Lupus eritematoso neonatal
Aguilera Peiró, Paula, Vicente Villa, Asunción, Antonia González-Ensenyat, M
Published in Piel (2009)
Published in Piel (2009)
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Journal Article
Solar capillaritis during hydrochlorothiazide treatment: A case report
Alamon-Reig, Francesc, Luque-Luna, Mar, Serra-García, Laura, Martí-Martí, Ignasi, Riera-Monroig, Josep, Fuertes, Irene, Aguilera-Peiró, Paula
Published in Photodermatology, photoimmunology & photomedicine (01.01.2023)
Published in Photodermatology, photoimmunology & photomedicine (01.01.2023)
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