Protein Engineering on Human Recombinant Follistatin: Enhancing Pharmacokinetic Characteristics for Therapeutic Application
Shen, Chuan, Iskenderian, Andrea, Lundberg, Dianna, He, Tao, Palmieri, Kathleen, Crooker, Robert, Deng, Qingwei, Traylor, Matthew, Gu, Sheng, Rong, Haojing, Ehmann, David, Pescatore, Brian, Strack-Logue, Bettina, Romashko, Alla, Baviello, George, Gill, John, Zhang, Bohong, Meiyappan, Muthuraman, Pan, Clark, Norton, Angela W
Published in The Journal of pharmacology and experimental therapeutics (01.08.2018)
Published in The Journal of pharmacology and experimental therapeutics (01.08.2018)
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Myostatin and activin blockade by engineered follistatin results in hypertrophy and improves dystrophic pathology in mdx mouse more than myostatin blockade alone
Iskenderian, Andrea, Liu, Nan, Deng, Qingwei, Huang, Yan, Shen, Chuan, Palmieri, Kathleen, Crooker, Robert, Lundberg, Dianna, Kastrapeli, Niksa, Pescatore, Brian, Romashko, Alla, Dumas, John, Comeau, Robert, Norton, Angela, Pan, Jing, Rong, Haojing, Derakhchan, Katayoun, Ehmann, David E
Published in Skeletal muscle (27.10.2018)
Published in Skeletal muscle (27.10.2018)
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Human Sulfatase 2 inhibits in vivo tumor growth of MDA-MB-231 human breast cancer xenografts
Peterson, Sarah M, Iskenderian, Andrea, Cook, Lynette, Romashko, Alla, Tobin, Kristen, Jones, Michael, Norton, Angela, Gómez-Yafal, Alicia, Heartlein, Michael W, Concino, Michael F, Liaw, Lucy, Martini, Paolo G V
Published in BMC cancer (13.08.2010)
Published in BMC cancer (13.08.2010)
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Cyclic dipeptides as building blocks for combinatorial libraries. Part 2: Synthesis of bifunctional diketopiperazines
Rodionov, Igor L, Rodionova, Ludmila N, Baidakova, Ludmila K, Romashko, Alla M, Balashova, Tamara A, Ivanov, Vadim T
Published in Tetrahedron (14.10.2002)
Published in Tetrahedron (14.10.2002)
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Structural characterization of the α-N-acetylglucosaminidase, a key enzyme in the pathogenesis of Sanfilippo syndrome B
Birrane, Gabriel, Dassier, Anne-Laure, Romashko, Alla, Lundberg, Dianna, Holmes, Kevin, Cottle, Thomas, Norton, Angela W., Zhang, Bohong, Concino, Michael F., Meiyappan, Muthuraman
Published in Journal of structural biology (01.03.2019)
Published in Journal of structural biology (01.03.2019)
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SRD005825 Acts as a Pharmacologic Chaperone of Opsin and Promotes Survival of Photoreceptors in an Animal Model of Autosomal Dominant Retinitis Pigmentosa
Ahmed, Chulbul M, Dwyer, Brian T, Romashko, All, Van Adestine, Stev, Park, Eun-He, Lou, Zhe, Welty, Devi, Josiah, Seren, Savinainen, Annel, Zhang, Bohon, Lewin, Alfred S
Published in Translational vision science & technology (01.11.2019)
Published in Translational vision science & technology (01.11.2019)
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Enzyme replacement therapy corrects Lysosomal Acid Lipase Deficiency (LALD) in a mouse model of Wolman disease/cholesteryl ester storage disease
Grabowski, Gregory, Du, Hong, Pescatore, Brian, Romashko, Alla, Meiyappan, Muthu, Martini, Paolo, Charnas, Lawrence, Gomez-Yafal, Alicia, Xu, You-Hai, Westmoreland, Oluwaseyi, Stanton, Lori
Published in Molecular genetics and metabolism (01.02.2011)
Published in Molecular genetics and metabolism (01.02.2011)
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TREATMENT OF SANFILIPPO SYNDROME TYPE B
PAN JING, BETTINA STRACK-LOGUE, DIANNA LUNDBERG, MUTHURAMAN MEIYAPPAN, ANGELA NORTON, RICHARD PFEIFER, ZHANG BOHONG, YAN HUANG, PAOLO MARTINI, MICHAEL F CONCINO, PERICLES CALIAS, MARY ALESSANDRINI, ANDREA ISKENDERIAN, KEVIN HOLMES, ALLA ROMASHKO
Year of Publication 26.05.2016
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Year of Publication 26.05.2016
Patent
TREATMENT OF SANFILIPPO SYNDROME TYPE B
Pfeifer, Richard, Pan, Jing, Martini, Paolo, Strack-Logue, Bettina, Iskenderian, Andrea, Zhang, Bohong, Holmes, Kevin, Alessandrini, Mary, Yan, Huang, Calias, Pericles, Meiyappan, Muthuraman, Lundberg, Dianna, Concino, Michael F, Romashko, Alla, Norton, Angela
Year of Publication 05.05.2022
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Year of Publication 05.05.2022
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Therapeutic fusion protein comprising an alpha-n-acetylglucosaminidase and a lysosomal targeting moiety
Pfeifer, Richard, Pan, Jing, Martini, Paolo, Strack-Logue, Bettina, Iskenderian, Andrea, Zhang, Bohong, Holmes, Kevin, Alessandrini, Mary, Yan, Huang, Calias, Pericles, Meiyappan, Muthuraman, Lundberg, Dianna, Concino, Michael F, Romashko, Alla, Norton, Angela
Year of Publication 20.07.2021
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Year of Publication 20.07.2021
Patent
Treatment of Sanfilippo Syndrome Type B
Norton Angela, Martini Paolo, Pfeifer Richard, Concino Michael F, Calias Pericles, Holmes Kevin, Meiyappan Muthuraman, Pan Jing, Zhang Bohong, Romashko Alla, Iskenderian Andrea, Lundberg Dianna, Strack-Logue Bettina, Yan Huang, Alessandrini Mary
Year of Publication 29.03.2018
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Year of Publication 29.03.2018
Patent