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The AAV capsid can influence the epigenetic marking of rAAV delivered episomal genomes in a species dependent manner
Gonzalez-Sandoval, Adriana, Pekrun, Katja, Tsuji, Shinnosuke, Zhang, Feijie, Hung, King L., Chang, Howard Y., Kay, Mark A.
Published in Nature communications (28.04.2023)
Published in Nature communications (28.04.2023)
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Investigation of the safety and feasibility of AAV1/SERCA2a gene transfer in patients with chronic heart failure supported with a left ventricular assist device – the SERCA-LVAD TRIAL
Lyon, A. R., Babalis, D., Morley-Smith, A. C., Hedger, M., Suarez Barrientos, A., Foldes, G., Couch, L. S., Chowdhury, R. A., Tzortzis, K. N., Peters, N. S., Rog-Zielinska, E. A., Yang, H-Y, Welch, S., Bowles, C. T., Rahman Haley, S., Bell, A. R., Rice, A., Sasikaran, T., Johnson, N. A., Falaschetti, E., Parameshwar, J., Lewis, C., Tsui, S., Simon, A., Pepper, J., Rudy, J. J., Zsebo, K. M., Macleod, K. T., Terracciano, C. M., Hajjar, R. J., Banner, N., Harding, S. E.
Published in Gene therapy (01.12.2020)
Published in Gene therapy (01.12.2020)
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Bioengineering strategies for restoring vision
Cehajic-Kapetanovic, Jasmina, Singh, Mandeep S., Zrenner, Eberhart, MacLaren, Robert E.
Published in Nature biomedical engineering (01.04.2023)
Published in Nature biomedical engineering (01.04.2023)
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Sensitization of ON-bipolar cells with ambient light activatable multi-characteristic opsin rescues vision in mice
Batabyal, Subrata, Gajjeraman, Sivakumar, Pradhan, Sanjay, Bhattacharya, Sulagna, Wright, Weldon, Mohanty, Samarendra
Published in Gene therapy (01.04.2021)
Published in Gene therapy (01.04.2021)
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Optogenetic Peripheral Nerve Immunogenicity
Maimon, Benjamin E., Diaz, Maurizio, Revol, Emilie C. M., Schneider, Alexis M., Leaker, Ben, Varela, Claudia E., Srinivasan, Shriya, Weber, Matthew B., Herr, Hugh M.
Published in Scientific reports (19.09.2018)
Published in Scientific reports (19.09.2018)
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Late responses to adenoviral-mediated transfer of the aquaporin-1 gene for radiation-induced salivary hypofunction
Alevizos, I, Zheng, C, Cotrim, A P, Liu, S, McCullagh, L, Billings, M E, Goldsmith, C M, Tandon, M, Helmerhorst, E J, Catalán, M A, Danielides, S J, Perez, P, Nikolov, N P, Chiorini, J A, Melvin, J E, Oppenheim, F G, Illei, G G, Baum, B J
Published in Gene therapy (01.03.2017)
Published in Gene therapy (01.03.2017)
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Minicircle DNA Provides Enhanced and Prolonged Transgene Expression Following Airway Gene Transfer
Munye, Mustafa M., Tagalakis, Aristides D., Barnes, Josephine L., Brown, Rachel E., McAnulty, Robin J., Howe, Steven J., Hart, Stephen L.
Published in Scientific reports (15.03.2016)
Published in Scientific reports (15.03.2016)
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Targeted genome editing in human repopulating haematopoietic stem cells
Genovese, Pietro, Schiroli, Giulia, Escobar, Giulia, Di Tomaso, Tiziano, Firrito, Claudia, Calabria, Andrea, Moi, Davide, Mazzieri, Roberta, Bonini, Chiara, Holmes, Michael C., Gregory, Philip D., van der Burg, Mirjam, Gentner, Bernhard, Montini, Eugenio, Lombardo, Angelo, Naldini, Luigi
Published in Nature (London) (12.06.2014)
Published in Nature (London) (12.06.2014)
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Bat adeno-associated viruses as gene therapy vectors with the potential to evade human neutralizing antibodies
Li, Ya, Li, Jialu, Liu, Yunbo, Shi, Zhengli, Liu, Haizhou, Wei, Yuquan, Yang, Lin
Published in Gene therapy (01.06.2019)
Published in Gene therapy (01.06.2019)
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Adenovirus-mediated hAQP1 expression in irradiated mouse salivary glands causes recovery of saliva secretion by enhancing acinar cell volume decrease
Teos, L Y, Zheng, C-Y, Liu, X, Swaim, W D, Goldsmith, C M, Cotrim, A P, Baum, B J, Ambudkar, I S
Published in Gene therapy (01.07.2016)
Published in Gene therapy (01.07.2016)
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Indirect imaging of cardiac-specific transgene expression using a bidirectional two-step transcriptional amplification strategy
Chen, I Y, Gheysens, O, Ray, S, Wang, Q, Padmanabhan, P, Paulmurugan, R, Loening, A M, Rodriguez-Porcel, M, Willmann, J K, Sheikh, A Y, Nielsen, C H, Hoyt, G, Contag, C H, Robbins, R C, Biswal, S, Wu, J C, Gambhir, S S
Published in Gene therapy (01.07.2010)
Published in Gene therapy (01.07.2010)
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