Mini-PCDH15 gene therapy rescues hearing in a mouse model of Usher syndrome type 1F
Ivanchenko, Maryna V., Hathaway, Daniel M., Klein, Alex J., Pan, Bifeng, Strelkova, Olga, De-la-Torre, Pedro, Wu, Xudong, Peters, Cole W., Mulhall, Eric M., Booth, Kevin T., Goldstein, Corey, Brower, Joseph, Sotomayor, Marcos, Indzhykulian, Artur A., Corey, David P.
Published in Nature communications (26.04.2023)
Published in Nature communications (26.04.2023)
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Journal Article
Gene Transfer with AAV9-PHP.B Rescues Hearing in a Mouse Model of Usher Syndrome 3A and Transduces Hair Cells in a Non-human Primate
György, Bence, Meijer, Elise J., Ivanchenko, Maryna V., Tenneson, Kelly, Emond, Frederick, Hanlon, Killian S., Indzhykulian, Artur A., Volak, Adrienn, Karavitaki, K. Domenica, Tamvakologos, Panos I., Vezina, Mark, Berezovskii, Vladimir K., Born, Richard T., O’Brien, Maureen, Lafond, Jean-François, Arsenijevic, Yvan, Kenna, Margaret A., Maguire, Casey A., Corey, David P.
Published in Molecular therapy. Methods & clinical development (14.06.2019)
Published in Molecular therapy. Methods & clinical development (14.06.2019)
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Journal Article
AAV-S: A versatile capsid variant for transduction of mouse and primate inner ear
Ivanchenko, Maryna V., Hanlon, Killian S., Hathaway, Daniel M., Klein, Alex J., Peters, Cole W., Li, Yaqiao, Tamvakologos, Panos I., Nammour, Josette, Maguire, Casey A., Corey, David P.
Published in Molecular therapy. Methods & clinical development (11.06.2021)
Published in Molecular therapy. Methods & clinical development (11.06.2021)
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Journal Article
Nrf2 overexpression rescues the RPE in mouse models of retinitis pigmentosa
Wu, David M, Ji, Xuke, Ivanchenko, Maryna V, Chung, Michelle, Piper, Mary, Rana, Parimal, Wang, Sean K, Xue, Yunlu, West, Emma, Zhao, Sophia R, Xu, Hongbin, Cicconet, Marcelo, Xiong, Wenjun, Cepko, Constance L
Published in JCI insight (25.01.2021)
Published in JCI insight (25.01.2021)
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Journal Article
Finding a window for gene therapy for hereditary deafness
Ivanchenko, Maryna V, Corey, David P
Published in Proceedings of the National Academy of Sciences - PNAS (26.09.2023)
Published in Proceedings of the National Academy of Sciences - PNAS (26.09.2023)
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Journal Article
Preclinical testing of AAV9-PHP.B for transgene expression in the non-human primate cochlea
Ivanchenko, Maryna V., Hanlon, Killian S., Devine, Maya K., Tenneson, Kelly, Emond, Frederick, Lafond, Jean-François, Kenna, Margaret A., Corey, David P., Maguire, Casey A.
Published in Hearing research (01.09.2020)
Published in Hearing research (01.09.2020)
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Journal Article
Rescue of hearing by adenine base editing in a humanized mouse model of Usher syndrome type 1F
Peters, Cole W., Hanlon, Killian S., Ivanchenko, Maryna V., Zinn, Eric, Linarte, Elizabeth F., Li, Yaqiao, Levy, Jonathan M., Liu, David R., Kleinstiver, Benjamin P., Indzhykulian, Artur A., Corey, David P.
Published in Molecular therapy (02.08.2023)
Published in Molecular therapy (02.08.2023)
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Journal Article
3D localization of PKHD1L1 in immunogold labeled outer hair cell stereocilia bundles using FIB‐ SEM (postnatal day 4)
Indzhykulian, Artur A., Ivanchenko, Maryna V., Cicconet, Marcelo, Hoor Al Jandal, Xudong Wu, Corey, David P.
Year of Publication 20.02.2020
Year of Publication 20.02.2020
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Screen captured demonstration of FIB-SEM data alignment and filtering using Dragonfly software package
Indzhykulian, Artur A., Ivanchenko, Maryna V., Cicconet, Marcelo, Hoor Al Jandal, Xudong Wu, Corey, David P.
Year of Publication 20.02.2020
Year of Publication 20.02.2020
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Screen captured demonstration of FIB-SEM data segmentation using Amira software package
Indzhykulian, Artur A., Ivanchenko, Maryna V., Cicconet, Marcelo, Hoor Al Jandal, Xudong Wu, Corey, David P.
Year of Publication 20.02.2020
Year of Publication 20.02.2020
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A 3D cumulative distribution map of anti‐PKHD1L1 immuno‐gold beads from six mouse outer hair cell stereocilia bundles (postnatal day 4)
Indzhykulian, Artur A., Ivanchenko, Maryna V., Cicconet, Marcelo, Hoor Al Jandal, Xudong Wu, Corey, David P.
Year of Publication 20.02.2020
Year of Publication 20.02.2020
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Elasticity and Thermal Stability are Key Determinants of Hearing Rescue by Mini-Protocadherin-15 Proteins
Pedro De-la-Torre, Wen, Haosheng, Brower, Joseph, Martínez-Pérez, Karina, Narui, Yoshie, Yeh, Frank, Hale, Evan, Ivanchenko, Maryna V, Corey, David P, Sotomayor, Marcos, Indzhykulian, Artur A
Published in bioRxiv (17.06.2024)
Published in bioRxiv (17.06.2024)
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Journal Article
AAV VECTORS ENCODING MINI-PCDH15 AND USES THEREOF
INDZHYKULIAN, Artur, PETERS, Cole, W.D, COREY, David, P, SOTOMAYOR, Marcos, IVANCHENKO, Maryna, V
Year of Publication 25.10.2023
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Year of Publication 25.10.2023
Patent
RECOMBINANT ADENO ASSOCIATED VIRUS ENCODING CLARIN-1 AND USES THEREOF
Maguire, Casey A, Corey, David P, Ivanchenko, Maryna V, Hanlon, Killian S
Year of Publication 21.04.2022
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Year of Publication 21.04.2022
Patent
Hexafluoro slows retinal degeneration and improves visual function in zebrafish models of Usher syndrome 1F
Phillips, Jennifer B, Siena Kulis, Buchner, Sarah H, Fox, Eric J, Wegner, Jeremy, Pierce, Judy, Ivanchenko, Maryna V, Corey, David P, Arbiser, Jack L, Westerfield, Monte
Published in bioRxiv (30.12.2023)
Published in bioRxiv (30.12.2023)
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Paper
RECOMBINANT ADENO ASSOCIATED VIRUS ENCODING CLARIN-1 AND USES THEREOF
IVANCHENKO, MARYNA V, MAGUIRE, CASEY A, COREY, DAVID P, HANLON, KILLIAN S
Year of Publication 14.03.2022
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Year of Publication 14.03.2022
Patent