Optimization and comparison of knockdown efficacy between polymerase II expressed shRNA and artificial miRNA targeting luciferase and Apolipoprotein B100
Maczuga, Piotr, Koornneef, Annemart, Borel, Florie, Petry, Harald, van Deventer, Sander, Ritsema, Tita, Konstantinova, Pavlina
Published in BMC biotechnology (24.07.2012)
Published in BMC biotechnology (24.07.2012)
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Journal Article
Mir-142-3p target sequences reduce transgene-directed immunogenicity following intramuscular adeno-associated virus 1 vector-mediated gene delivery
Majowicz, Anna, Maczuga, Piotr, Kwikkers, Karin L., van der Marel, Sander, van Logtenstein, Richard, Petry, Harald, van Deventer, Sander J., Konstantinova, Pavlina, Ferreira, Valerie
Published in The journal of gene medicine (01.06.2013)
Published in The journal of gene medicine (01.06.2013)
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Journal Article
Embedding siRNA sequences targeting Apolipoprotein B100 in shRNA and miRNA scaffolds results in differential processing and in vivo efficacy
Maczuga, Piotr, Lubelski, Jacek, van Logtenstein, Richard, Borel, Florie, Blits, Bas, Fakkert, Erwin, Costessi, Adalberto, Butler, Derek, van Deventer, Sander, Petry, Harald, Koornneef, Annemart, Konstantinova, Pavlina
Published in Molecular therapy (01.01.2013)
Published in Molecular therapy (01.01.2013)
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Journal Article
Subunit-specific Incorporation Efficiency and Kinetics in Mitochondrial Complex I Homeostasis
Dieteren, Cindy E.J., Koopman, Werner J.H., Swarts, Herman G., Peters, Janny G.P., Maczuga, Piotr, van Gemst, Jasper J., Masereeuw, Rosalinde, Smeitink, Jan A.M., Nijtmans, Leo G.J., Willems, Peter H.G.M.
Published in The Journal of biological chemistry (07.12.2012)
Published in The Journal of biological chemistry (07.12.2012)
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Journal Article